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Clinical Trials on Pyruvate Metabolism, Inborn Errors in Canada
Total 484 results
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McGill University Health Centre/Research Institute...March of DimesCompleted
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Children's Hospital of Eastern OntarioCompleted
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Ultragenyx Pharmaceutical IncCompletedGSD1Netherlands, United States, Canada, Spain
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PTC TherapeuticsCompletedMitochondrial Diseases | Drug Resistant Epilepsy | Leigh Disease | Leigh Syndrome | Mitochondrial Encephalopathy (MELAS) | Pontocerebellar Hypoplasia Type 6 (PCH6) | Alpers Disease | Alpers SyndromeUnited States, Spain, United Kingdom, Canada, France, Italy, Poland, Sweden, Japan
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PfizerCompletedHypercholesterolemia, FamilialCanada, United States, South Africa
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NeuroBo Pharmaceuticals Inc.CompletedHypercholesteremiaUnited States, Canada, Israel
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TakedaTerminatedHypercholesterolemiaFrance, United Kingdom, United States, Israel, Poland, Canada
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Canada
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University of British ColumbiaMedical University of Graz; Hospital de Clinicas de Porto AlegreUnknownMorquio B Disease | GM1 Gangliosidosis Type IIICanada
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Protagonist Therapeutics, Inc.CompletedHereditary HemochromatosisUnited States, Canada
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The Hospital for Sick ChildrenActelionCompletedGangliosidoses GM2Canada
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The Hospital for Sick ChildrenCompletedGangliosidoses, GM2 | Tay-Sachs Disease | Sandhoff DiseaseCanada
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Taiwan, United Kingdom, Australia, Canada, Germany, Spain
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Aegerion Pharmaceuticals, Inc.CompletedFamilial HypercholesterolemiaUnited States, Canada, Italy, South Africa
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolemiaSlovenia, Taiwan, Russian Federation, Canada, Netherlands, Brazil, Denmark, Mexico, Spain, Turkey
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseCanada, Russian Federation, Tunisia
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University of WashingtonCompleted
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaAustralia, United States, Japan, Germany, Turkey, Italy, India, France, United Kingdom, Argentina, Canada
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Canada, United Arab Emirates, United Kingdom
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Dr. Anupam SehgalTaysha Gene Therapies, Inc.; GlycoNetActive, not recruitingInfantile GM2 Gangliosidosis (Disorder)Canada
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, Spain, Australia, United Kingdom, Italy, France, Canada, Germany, Japan, Russian Federation, Saudi Arabia, Turkey
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Cerenis Therapeutics, SACompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Netherlands, United Kingdom
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Chylomicronemia Syndrome | Lipoprotein Lipase Deficiency | Hyperlipoproteinemia Type 1Canada
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AstraZenecaCompletedFamilial HypercholesterolaemiaUnited States, Netherlands, Norway, Canada, Belgium
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Cortria CorporationMontreal Heart InstituteCompletedHypertriglyceridemia | Mixed HyperlipidemiaCanada
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Arrowhead PharmaceuticalsActive, not recruitingHomozygous Familial HypercholesterolemiaAustralia, Canada, United States, South Africa
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AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Taiwan, Belgium, Denmark, Israel
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AstraZenecaCompletedFamilial HypercholesterolemiaUnited States, Spain, Netherlands, Norway, Canada
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Novartis PharmaceuticalsCompletedIron Overload | Hereditary HemochromatosisUnited States, Germany, Italy, Australia, Canada, France
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Aegerion Pharmaceuticals, Inc.FDA Office of Orphan Products DevelopmentCompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, South Africa
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Cytonet GmbH & Co. KGTerminatedUrea Cycle DisordersUnited States, Canada
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, France, United Kingdom, Canada, Netherlands, Russian Federation, Turkey, Australia
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Cerenis Therapeutics, SATerminatedFamilial HypoalphalipoproteinemiaFrance, United States, Belgium, Canada, Israel, Italy, Netherlands
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaItaly, Spain, Israel, Korea, Republic of, Belgium, Germany, United States, China, France, Taiwan, Austria, Japan, India, Australia, Argentina, Poland, Turkey, Brazil, Canada, Thailand, United Kingdom, Slovakia, Czechia
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaIsrael, Korea, Republic of, Taiwan, Sweden, Germany, Italy, Turkey, China, Poland, United States, France, Australia, Thailand, United Kingdom, Mexico, Vietnam, Argentina, Belgium, Brazil, Canada, Spain
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Spain, Netherlands, France, United Kingdom, Australia, Canada, Italy
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Canada, United Kingdom
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AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Israel, Netherlands, Taiwan, Belgium, Denmark
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Novartis PharmaceuticalsCompletedHereditary HemochromatosisBelgium, France, Russian Federation, Romania, Slovakia, Spain, Switzerland
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McGill University Health Centre/Research Institute...CompletedGenetic Diseases, Inborn | Coronary Arteriosclerosis | HypoalphalipoproteinemiasCanada
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M.A.G.I.C. Clinic LTDHanalytics Solutions Inc.RecruitingMitochondrial Diseases | Fabry Disease | Metabolic Disease | Gaucher Disease | Pompe DiseaseCanada
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolaemiaNorway, Russian Federation, Sweden, South Africa, Czechia, United States, Canada, France, Netherlands, Spain
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AVROBIOTerminatedType 1 Gaucher DiseaseUnited States, Canada
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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ModernaTX, Inc.RecruitingMethylmalonic AcidemiaUnited States, Spain, Canada, Netherlands, France, Australia, United Kingdom
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HomozygousGreece, Lebanon, Turkey, France, Canada, Malaysia, Netherlands, United States
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Université de MontréalGenzyme, a Sanofi CompanyCompleted
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ModernaTX, Inc.RecruitingGlycogen Storage DiseaseUnited States, Canada
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Ultragenyx Pharmaceutical IncTerminatedWilson Disease | Ornithine Transcarbamylase Deficiency | Glycogen Storage Disease Type IASpain, United Kingdom, Canada, United States, Brazil