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Clinical Trials on Pyruvate Metabolism, Inborn Errors in France
Total 727 results
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, France, United Kingdom, Canada, Netherlands, Russian Federation, Turkey, Australia
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Centre Hospitalier Universitaire de NiceCompleted
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Cerenis Therapeutics, SATerminatedFamilial HypoalphalipoproteinemiaFrance, United States, Belgium, Canada, Israel, Italy, Netherlands
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OxTheraFP7-SME-2013 Research for the benefit of SMEs programCompletedPrimary HyperoxaluriaFrance, Germany, United Kingdom
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Hospital St. Joseph, Marseille, FranceCompleted
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaIsrael, Korea, Republic of, Taiwan, Sweden, Germany, Italy, Turkey, China, Poland, United States, France, Australia, Thailand, United Kingdom, Mexico, Vietnam, Argentina, Belgium, Brazil, Canada, Spain
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LYSOGENECompletedMucopolysaccharidosis IIIAGermany, Brazil, United Kingdom, France, Netherlands
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PfizerTerminatedHyperlipoproteinemia Type IIICanada, United States
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Spain, Netherlands, France, United Kingdom, Australia, Canada, Italy
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Assistance Publique - Hôpitaux de ParisInstitut National de la Santé Et de la Recherche Médicale, France; Association...Unknown
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Dicerna Pharmaceuticals, Inc.CompletedPrimary HyperoxaluriaUnited States, France, Germany, Netherlands, United Kingdom
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Groupe Hospitalier Diaconesses Croix Saint-SimonTerminated
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Abeona Therapeutics, IncTerminatedMucopolysaccharidosis III-BUnited States, Germany, France
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolaemiaNorway, Russian Federation, Sweden, South Africa, Czechia, United States, Canada, France, Netherlands, Spain
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe Disease Infantile-OnsetUnited States, France, South Africa
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Central Hospital, Nancy, FranceRecruitingPompe's Disease Juvenile OnsetFrance
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Institut National de la Santé Et de la Recherche...Recruiting
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaItaly, Spain, Israel, Korea, Republic of, Belgium, Germany, United States, China, France, Taiwan, Austria, Japan, India, Australia, Argentina, Poland, Turkey, Brazil, Canada, Thailand, United Kingdom, Slovakia, Czechia
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Genzyme, a Sanofi CompanyActive, not recruitingGlycogen Storage Disease Type IIFrance
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Lille Catholic UniversityUniversity of Birmingham; Variant Bio, Inc.; University of San Diego; Ministry...Completed
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GOIZETBioMarin PharmaceuticalRecruiting
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Fondation Ophtalmologique Adolphe de RothschildRecruiting
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Fondation Ophtalmologique Adolphe de RothschildRecruiting
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Fondation Ophtalmologique Adolphe de RothschildCompletedWilson DiseaseFrance
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ModernaTX, Inc.RecruitingMethylmalonic AcidemiaUnited States, Spain, Canada, Netherlands, France, Australia, United Kingdom
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University Hospital, RouenUniversity Hospital, CaenRecruitingLysosomal Storage Diseases | Neonatal ScreeningFrance
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Centre Hospitalier Universitaire de NiceUnknownArthritis | Osteoarthritis | Rheumatoid Arthritis | Gouty Arthritis | ChondrocalcinosisFrance
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolaemiaCzechia, France, Denmark, Netherlands, Austria, Mexico, Spain, United States, Argentina, Brazil, Bulgaria, Canada, Finland, Hungary, Italy, Lebanon, Norway, Poland, Russian Federation, Slovenia, South Africa, Sweden, Taiwan, Turkey
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La Jolla Pharmaceutical CompanyPRA Health SciencesCompletedHereditary HemochromatosisUnited States, Australia, France, United Kingdom
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Assistance Publique - Hôpitaux de ParisRecruiting
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HomozygousGreece, Lebanon, Turkey, France, Canada, Malaysia, Netherlands, United States
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University Hospital, RouenUnknownAnderson-Fabry DiseaseFrance
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PfizerCompletedHypertriglyceridemia | Hyperlipoproteinemia Type IVUnited States, Canada
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Ultragenyx Pharmaceutical IncCompletedGlycogen Storage Disease Type IIIUnited States
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Assistance Publique - Hôpitaux de ParisUnknown
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Ultragenyx Pharmaceutical IncTerminatedGlycogen Storage Disease Type IIIUnited States, Spain, Italy
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Hospices Civils de LyonCompletedIdiopathic Hypercalciuria | Primary Hyperoxaluria Type 1France
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University Hospital, BordeauxUnknown
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Institut National de la Santé Et de la Recherche...Assistance Publique - Hôpitaux de Paris; European Leukodystrophy AssociationActive, not recruitingMetachromatic LeukodystrophyFrance
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Hospices Civils de LyonNot yet recruitingWilson DiseaseFrance
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Bicetre HospitalUnknownRare Diseases | X-linked HypophosphatemiaFrance
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Assistance Publique - Hôpitaux de ParisEuropean Leukodystrophy AssociationCompletedLate Infantile Metachromatic LeukodystrophyFrance
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OxTheraCompletedPrimary HyperoxaluriaFrance, United Kingdom, Spain, Belgium, United States, Germany, Tunisia
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Homology Medicines, IncTerminated
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University Hospital, LimogesCompletedHemochromatosis | Glomerulonephritis, Membranous | Neonatal Diseases and AbnormalitiesFrance
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States, Turkey, Canada, France, Germany, Italy, United Kingdom
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Assistance Publique - Hôpitaux de ParisCompletedMovement Disorders | Wilson Disease | Repetitive Transcranial Magnetic StimulationFrance
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PfizerCompletedHyperlipidemia | Hypercholesterolemia, FamilialUnited States, Canada, South Africa, Czech Republic, Italy, Finland, Netherlands, France
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University Hospital, CaenUnknownCardiomyopathiesFrance
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Recordati Rare DiseasesRecruitingPropionic Acidemia | Methylmalonic AcidemiaFrance, Spain, Italy, United Kingdom, Norway, Germany, Sweden