- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Pyruvate Metabolism, Inborn Errors
Total 4323 results
-
Rennes University HospitalCompleted
-
Madrigal Pharmaceuticals, Inc.CompletedHeterozygous Familial HypercholesterolemiaDenmark
-
Central South UniversityCompletedHomozygous Familial HypercholesterolemiaChina
-
CymaBay Therapeutics, Inc.CompletedHomozygous Familial HypercholesterolemiaCanada, France, Netherlands, Norway
-
Merck Sharp & Dohme LLCTerminatedHyperlipoproteinemia Type II | Homozygous Familial Hypercholesterolemia
-
Japan Tobacco Inc.CompletedType II HyperlipidaemiaNetherlands
-
University of California, San DiegoCompleted
-
University Medical Center GroningenUniversity of Oxford; University of the Faroe Islands; Stichting Stofwisselkracht and other collaboratorsCompleted
-
Rigshospitalet, DenmarkCompleted
-
Lumos DiagnosticsAptatek BiosciencesRecruiting
-
SanofiRecruiting
-
Children's Hospital of Fudan UniversityHedu Biotechnology (Shanghai) Co., LTDRecruiting
-
University Hospital, GrenobleRecruitingMetabolic Diseases | PhenylketonuriaFrance
-
APR Applied Pharma Research s.a.Recruiting
-
University Children's Hospital, ZurichUniversity Children's Hospital Basel; UChildrenVienna; Insel Gruppe AG, University...RecruitingPhenylketonuriasSwitzerland
-
University Hospital, LilleNot yet recruiting
-
Emory UniversityBioMarin PharmaceuticalRecruitingPhenylketonuriasUnited States
-
Vitaflo International, LtdCompleted
-
Vitaflo International, LtdJohannes Gutenberg University Mainz; Kreiskliniken ReutlingenCompleted
-
Klaus ParhoferTerminated
-
Nutricia UK LtdCompletedPKU | TyrosinemiasUnited Kingdom
-
BioMarin PharmaceuticalCompletedPhenylketonuriaItaly, Spain, United Kingdom, Germany
-
Rubius TherapeuticsTerminated
-
Ludwig-Maximilians - University of MunichEuropean UnionCompletedPhenylketonuriaGermany, Italy, Spain, United Kingdom
-
BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
-
SynlogicCompletedHealthy | PhenylketonuriaUnited States
-
Assiut UniversityUnknown
-
Boston Children's HospitalBrigham and Women's HospitalCompletedPhenylketonuriaUnited States
-
Washington University School of MedicineUniversity of Missouri-Columbia; BioMarin PharmaceuticalCompleted
-
Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalCompletedPhenylketonuriaUnited States
-
University of Missouri-ColumbiaBioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
-
BioMarin PharmaceuticalCompleted
-
BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States, Canada
-
Emory UniversityAtlanta Clinical and Translational Science InstituteCompleted
-
The University of Texas Health Science Center,...BioMarin PharmaceuticalTerminatedPhenylketonuria | HyperphenylalaninemiaUnited States
-
Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalCompletedPhenylketonuriaUnited States
-
The University of Texas Health Science Center,...BioMarin PharmaceuticalCompleted
-
Emory UniversityTerminated
-
Merck KGaA, Darmstadt, GermanyCompleted
-
BioMarin PharmaceuticalCompleted
-
Shoji YanoBioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
-
BioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
-
BioMarin PharmaceuticalApproved for marketing
-
BioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
-
HemoShear TherapeuticsTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States, Saudi Arabia, Australia
-
Nicoline LøkkenCompleted
-
King Abdullah International Medical Research CenterCompletedPropionic Acidemia | Methylmalonic AcidemiaSaudi Arabia
-
Mendel TuchmanUniversity of Colorado, Denver; Children's Hospital of Philadelphia; University... and other collaboratorsTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States
-
PTC TherapeuticsRecruitingPhenylketonuriaUnited States