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Clinical Trials on Rare Neoplastic Syndrome in United States
Total 68125 results
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M.D. Anderson Cancer CenterActive, not recruitingMultiple Endocrine Neoplasia SyndromesUnited States
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Children's Mercy Hospital Kansas CityKatherine Berry Richardson FoundationCompleted
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University of CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Rare Diseases Clinical Research...CompletedBirt-Hogg-Dube SyndromeUnited States
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National Cancer Institute (NCI)CompletedHamartoma Syndrome, Multiple | Cowden's DiseaseUnited States
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Uma BorateRecruitingTherapy-Related Myelodysplastic Syndrome | Secondary Myelodysplastic SyndromeUnited States
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University of South FloridaBoston Children's HospitalCompletedPTEN Gene MutationUnited States
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John Carroll UniversityUniversity Hospital Southampton NHS Foundation TrustActive, not recruitingPTEN Hamartoma Tumor SyndromeUnited States, United Kingdom
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Stanford UniversityNot yet recruitingPTEN Gene Mutation | PTEN Hamartoma Tumor Syndrome | PTEN Hamartoma SyndromeUnited States
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Scripps HealthJ. Craig Venter InstituteCompletedLi-Fraumeni Syndrome | Hereditary Cancer Syndromes | TP53 Gene Germline Mutation CarrierUnited States
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Abramson Cancer Center of the University of PennsylvaniaChildren's Hospital of PhiladelphiaRecruiting
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National Cancer Institute (NCI)CompletedLi-Fraumeni SyndromeUnited States
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Washington University School of MedicineTaiho Oncology, Inc.RecruitingMyelodysplastic SyndromesUnited States
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National Cancer Institute (NCI)RecruitingNeoplasms | Li-Fraumeni Syndrome | Tp53 MutationsUnited States
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National Cancer Institute (NCI)RecruitingKidney Cancer | Bladder Cancer | Renal Cancer | Malignant Neoplasms | Hereditary Neoplastic SyndromesUnited States
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National Institute of Diabetes and Digestive and...Completed
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University of FloridaCelgene CorporationTerminatedMyelodysplastic Syndromes | Leukemia, MyeloidUnited States
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Dana-Farber Cancer InstituteNational Cancer Institute (NCI); Baylor College of Medicine; City of Hope Medical...RecruitingTP53 Gene Mutation | Li-Fraumeni Syndrome | Hereditary Cancer Syndrome | Mosaicism | Clonal HematopoiesisUnited States
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National Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | LeukemiaUnited States
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Jersey Shore University Medical CenterRutgers University; Rutgers Cancer Institute of New JerseyCompletedPancreatic Cancer | Parathyroid Disease | Thymic Cancer | MEN1 SyndromeUnited States
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National Cancer Institute (NCI)CompletedBreast Neoplasm | Hereditary Neoplastic SyndromeUnited States
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National Institute of Neurological Disorders and...CompletedMuscle Rigidity | Spasm | Stiff Man SyndromeUnited States
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Weill Medical College of Cornell UniversityRecruitingGynecologic Cancer | Hereditary Cancer SyndromeUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RecruitingLi-Fraumeni SyndromeUnited States
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M.D. Anderson Cancer CenterCompletedMultiple Endocrine NeoplasiaUnited States
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedPTEN Gene Mutation | PTEN Hamartoma Tumor SyndromeUnited States
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Myriad Genetic Laboratories, Inc.Myriad Genetics, Inc.CompletedHereditary CancerUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)TerminatedMeningioma | Neuroendocrine Neoplasm | Multiple Endocrine Neoplasia Type 1 | Von Hippel-Lindau Syndrome | Metastatic Well Differentiated Neuroendocrine Neoplasm | Somatostatin Positive Neoplastic Cells PresentUnited States
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InheRET, IncUniversity of MichiganEnrolling by invitationHereditary Cancer-Predisposing SyndromeUnited States
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Dana-Farber Cancer InstituteBrigham and Women's HospitalCompletedRefractory Acute Myeloid Leukemia | Myelodysplastic Syndrome RAEB-I or RAEB-II | Refractory CML Myeloid Blast CrisisUnited States
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M.D. Anderson Cancer CenterGenzyme, a Sanofi CompanyCompletedAcute Myeloid Leukemia | Chronic Myeloid Leukemia | Myelodysplastic SyndromeUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedMitochondrial Disorders | Li-Fraumeni Syndrome | Carriers of p53 MutationUnited States
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Dana-Farber Cancer InstituteActive, not recruiting
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H. Lee Moffitt Cancer Center and Research InstituteActive, not recruitingMyelodysplastic Syndromes | Secondary Acute Myeloid LeukemiaUnited States
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University of ChicagoNational Cancer Institute (NCI)CompletedAcute Myeloid Leukemia | Secondary Acute Myeloid Leukemia | Myelodysplastic Syndrome | Secondary Myelodysplastic Syndrome | de Novo Myelodysplastic SyndromeUnited States
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Fred Hutchinson Cancer CenterJazz PharmaceuticalsTerminatedAcute Myeloid Leukemia | Myelodysplastic Syndrome With Excess Blasts-2 | Myeloid NeoplasmUnited States
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UCSF Benioff Children's Hospital OaklandNational Cancer Institute (NCI)CompletedNeoplastic SyndromeUnited States
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Mayo ClinicRecruitingHematologic Neoplasms | Myeloid Malignancy | Cytopenia | Bone Marrow Failure Syndrome | Clonal Cytopenia of Undetermined Significance | Clonal Hematopoiesis of Indeterminate Potential | Low Risk Myelodysplastic Syndrome | Inherited Bone Marrow Failure Syndrome | Clonal Expansion | Hereditary Neoplastic... and other conditionsUnited States
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University of RochesterRecruitingAcute Myeloid Leukemia | Myelodysplastic SyndromeUnited States
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Institute of Cancer Research, United KingdomCancer Research UK; National Institute for Health Research, United KingdomCompletedLi-Fraumeni SyndromeUnited Kingdom
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City of Hope Medical CenterCompletedRecurrent Adult Acute Myeloid Leukemia | Secondary Acute Myeloid Leukemia | Untreated Adult Acute Myeloid Leukemia | Previously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | Adult Acute Myeloid Leukemia | de Novo Myelodysplastic SyndromesUnited States
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University of UtahNovartisTerminatedPeutz-Jeghers SyndromeUnited States
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NYU Langone HealthWithdrawnEpilepsy | Tuberous Sclerosis | Dravet Syndrome | Focal Seizures | Lennox-Gastaut SyndromeUnited States
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Novartis PharmaceuticalsCompletedBreast Cancer | Solid Tumors | Cowden SyndromeUnited States, Spain, Canada
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Kaiser PermanenteDana-Farber Cancer Institute; Columbia University; Emory University; University... and other collaboratorsActive, not recruiting
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National Cancer Institute (NCI)CompletedMultiple Endocrine Neoplasia Type 2A | Multiple Endocrine Neoplasia Type 2B | Medullary Thyroid CarcinomaUnited States
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University of Illinois at ChicagoWithdrawnDysplastic Nevus SyndromeUnited States
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National Cancer Institute (NCI)RecruitingNeurofibromatosis 1 | Noonan Syndrome | Legius Syndrome | Cardiofaciocutaneous Syndrome | Costello SyndromeUnited States
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NYU Langone HealthCompleted
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National Cancer Institute (NCI)CompletedMultiple Endocrine Neoplasia Type 2 | Medullary Thyroid CarcinomaUnited States