- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Refractive Errors in United Kingdom
Total 2276 results
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National Center for Research Resources (NCRR)Icahn School of Medicine at Mount SinaiCompletedMetabolism, Inborn Errors | Leukodystrophy, Globoid Cell | Tay-Sachs Disease | Porphyria, ErythropoieticUnited States
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ShireApproved for marketingGaucher Disease, Type 1United States
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Pacific Parkinson's Research CentreUniversity of British Columbia; Oregon Health and Science University; University... and other collaboratorsRecruitingParkinson Disease | Gaucher Disease | GBA Gene MutationUnited States, Canada
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TakedaCompletedGout | Moderate Renal ImpairmentUnited States
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TakedaTakeda Development Center Americas, Inc.Active, not recruitingHunter SyndromeUnited States, Germany, Malaysia, Philippines, Thailand, Dominican Republic, Serbia, Vietnam
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Neurocrine BiosciencesCompletedCAH - Congenital Adrenal HyperplasiaUnited States
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University of RochesterNational Institute on Aging (NIA)CompletedDepression | Cognitive Impairment | Medication Administered in ErrorUnited States
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Emalex Biosciences Inc.Psyadon PharmaTerminatedLesch-Nyhan Disease | Self-injurious BehaviorSpain, United States
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Genzyme, a Sanofi CompanyRecruitingGlycogen Storage Disease Type II | Pompe DiseaseHungary, Croatia, Serbia, United States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Chile, China, Colombia, Denmark, France, Germany, Greece, Hong Kong, India, Indonesia, Israel, Italy, Japan, Jordan, Korea, Republic of, Kuwait and more
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SanofiRecruitingFabry DiseaseChina, Finland, Germany, Norway, United Kingdom, United States, Denmark, Austria, Greece, Romania, Argentina, Brazil, Canada, Japan, Mexico, Poland, Italy, France, Turkey, Australia, Switzerland
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Amicus TherapeuticsApproved for marketingPhysician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry DiseaseFabry DiseaseUnited States, Australia
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Amicus TherapeuticsCompletedFabry DiseaseUnited States
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Talaris Therapeutics Inc.Duke UniversityNo longer availableMetachromatic LeukodystrophyUnited States
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis II (MPS II)United States, France, United Kingdom, Germany, Sweden, Spain, Brazil, Canada, Italy, Romania
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Homology Medicines, IncWithdrawnMucopolysaccharidosis IIUnited States, Canada
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Genzyme, a Sanofi CompanyCompleted
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingWeight Loss | Advanced Malignant Solid Neoplasm | Recurrent Malignant Solid Neoplasm | Metastatic Malignant Solid Neoplasm | Cancer Fatigue | C-Reactive Protein MeasurementUnited States
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National Institutes of Health Clinical Center (CC)RecruitingCongenital Adrenal HyperplasiaUnited States
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Eunice Kennedy Shriver National Institute of Child...CompletedCongenital Adrenal Hyperplasia (CAH)United States
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Amicus TherapeuticsEngage Health Inc.CompletedFabry DiseaseUnited States
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Cyprium Therapeutics, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedMenkes Disease | Occipital Horn Syndrome | Unexplained Copper DeficiencyUnited States
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Baylor Research InstituteNational Institute of Neurological Disorders and Stroke (NINDS)Completed
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ActelionCompleted
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Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Taiwan, Japan, Australia, Canada
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Amicus TherapeuticsCompletedFabry DiseaseJapan, Taiwan, Turkey, United States, Brazil
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Genzyme, a Sanofi CompanyTerminatedPompe DiseaseUnited States
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ShireCompleted
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Mayo ClinicCompleted
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Adrenas Therapeutics IncRecruitingCongenital Adrenal HyperplasiaUnited States
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Genzyme, a Sanofi CompanyCompletedCerebroside Lipidosis Syndrome | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease Type I | Clucocerebrosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States
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Horizon Pharma USA, Inc.CompletedCystinosisFrance, United States, Netherlands
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Neurocrine BiosciencesCompletedCAH - Congenital Adrenal HyperplasiaUnited States
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Neurocrine BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Spain, Belgium, Austria, Bulgaria, Canada, Czechia, France, Germany, Greece, Israel, Italy, Netherlands, Poland, Portugal, Serbia, Sweden, United Kingdom
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National MPS SocietyMediResource Inc.TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidoses | Mucopolysaccharidosis VI | Mucopolysaccharidosis IVUnited States
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Olatec Therapeutics LLCRecruitingArthritis | Joint Pain | Gout | Gout Flare | Gouty Arthritis | Acute Gout Flare | Gout AttackUnited States, Spain, France
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Brazil
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PfizerNo longer availableGaucher DiseaseUnited States, Israel
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Spruce BiosciencesCompletedCongenital Adrenal Hyperplasia | CAH - Congenital Adrenal HyperplasiaUnited States
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Amicus TherapeuticsCompleted
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University of California, San FranciscoRecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolman Disease | Pompe Disease Infantile-Onset | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopathic Gaucher DiseaseUnited States
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University of WashingtonNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsUnknown
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Masonic Cancer Center, University of MinnesotaCompletedNiemann-Pick Disease | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | GM1 Gangliosidosis | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Tay Sachs Disease | Sandhoff DiseaseUnited States
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SanofiRecruitingGaucher's Disease Type IIIUnited States, Germany, Hungary, France, China, Japan, Canada, Argentina, Italy, Turkey
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Brigham and Women's HospitalUnknownMedication Administered in Error | Adverse Drug EventsUnited States
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Maya GuglinTerminatedHeart Failure With Reactive Pulmonary HypertensionUnited States
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AVROBIOTerminatedFabry DiseaseUnited States, Australia, Brazil
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Masonic Cancer Center, University of MinnesotaTerminatedSphingolipidoses | Niemann-Pick Disease, Type C | Krabbe Disease | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Hurler's Syndrome | Maroteaux-Lamy Syndrome | Wolman's Disease | Niemann-Pick Disease Type BUnited States
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National Human Genome Research Institute (NHGRI)CompletedCancer | Myelofibrosis | Pulmonary Fibrosis | Gaucher Disease | Hermansky-Pudlak Syndrome (HPS)United States