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Clinical Trials on Renal Tubular Transport, Inborn Errors
Total 3030 results
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Augusta UniversityTerminatedDietary Fructose IntoleranceUnited States
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University of LausanneUniversity of LiegeCompletedHereditary Fructose IntoleranceBelgium
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Inherited Bone Marrow Failure SyndromeUnited States
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University of North Carolina, Chapel HillNational Institutes of Health (NIH); National Center for Research Resources... and other collaboratorsCompletedCystic Fibrosis | Primary Ciliary Dyskinesia | Kartagener Syndrome | PseudohypoaldosteronismUnited States, Canada
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University Hospital FreiburgCompletedMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Pearson Marrow-pancreas Syndrome | Shwachman-diamond SyndromeSpain, Germany, Switzerland, Austria, Netherlands, Italy, Czech Republic, Belgium, Denmark, Ireland
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedLeukemia | Thrombocytopenia | Fanconi Anemia | Congenital Amegakaryocytic Thrombocytopenia | Severe Congenital Neutropenia | Diamond-blackfan AnemiaUnited States
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Sohag UniversityNot yet recruitingInborn Errors of ImmunityEgypt
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National Center for Global Health and Medicine,...UnknownHIV Infection | Renal Function Disorder | Renal Tubular Disorder
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CENTOGENE GmbH RostockWithdrawnLipoprotein Lipase Deficiency | Inborn Error of Lipid Metabolism | Corneal ArcusGermany, India, Sri Lanka
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyRecruitingEnd Stage Renal Disease | Primary Hyperoxaluria Type 2 | Primary Hyperoxaluria Type 1Germany, Spain, United States, United Kingdom, Italy, United Arab Emirates, Lebanon, Morocco, France, Romania
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CENTOGENE GmbH RostockCompletedInborn Errors of Metabolism | BiomarkerEgypt, Sri Lanka, Albania, Romania, Georgia, India, Lithuania, Pakistan
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Eva Morava-KoziczChildren's Hospital of Philadelphia; Seattle Children's HospitalNot yet recruiting
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CENTOGENE GmbH RostockRecruitingInborn Errors of MetabolismPakistan
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University of LausanneCompletedInborn Errors of MetabolismSwitzerland
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Duke UniversitySuspendedLysosomal Storage Diseases | Genetic Disease | Inborn Errors of Metabolism | Glycogen Storage Disease | Storage DiseaseUnited States
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First Affiliated Hospital, Sun Yat-Sen UniversitySecond Affiliated Hospital of Guangzhou Medical UniversityUnknownKidney Transplantation | Acute Kidney Tubular NecrosisChina
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University of LausanneRecruiting
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Assistance Publique - Hôpitaux de ParisCompletedInborn Errors of MetabolismFrance
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National Human Genome Research Institute (NHGRI)RecruitingInborn Errors of Metabolism | Methylmalonic Acidemia | Organic AcidemiaUnited States
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University of LausanneCompletedGlucose Metabolism Disorders | Fructose Metabolism, Inborn Errors | Hereditary Fructose Intolerance
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Genzyme, a Sanofi CompanyCRL/MedinetTerminatedFabry Disease | Chronic Kidney Disease, Stage IV (Severe)United States
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University Children's Hospital, ZurichRecruitingInborn Errors of Metabolism | TransitionSwitzerland, Austria
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OHSU Knight Cancer InstituteNational Heart, Lung, and Blood Institute (NHLBI)CompletedChronic Myeloproliferative Disorders | Fanconi Anemia | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative NeoplasmsUnited States
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BioCryst PharmaceuticalsCompletedRenal Insufficiency | Arthritis | Hyperuricemia | Gout | Joint DiseaseUnited States
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Shenzhen Ausa Pharmed Co.,LtdNanfang Hospital of Southern Medical UniversityWithdrawn
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaAustralia, United States, Japan, Germany, Turkey, Italy, India, France, United Kingdom, Argentina, Canada
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Alexion Pharmaceuticals, Inc.Not yet recruiting
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AlexionRecruiting
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Children's Mercy Hospital Kansas CityRecruiting
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Sheffield Teaching Hospitals NHS Foundation TrustNational Institute for Health Research, United Kingdom; Alexion Pharmaceuticals...Completed
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of SheffieldActive, not recruiting
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Aga Khan University Hospital, PakistanCompletedInborn Errors of MetabolismPakistan
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
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Boston Children's HospitalRecruitingGenetic Disease | Chopra-Amiel-Gordon Syndrome | CAGS | ANKRD17United States
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First Affiliated Hospital, Sun Yat-Sen UniversitySecond Affiliated Hospital of Guangzhou Medical UniversityUnknownKidney Transplantation | Acute Kidney Tubular NecrosisChina
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaItaly, Spain, Israel, Korea, Republic of, Belgium, Germany, United States, China, France, Taiwan, Austria, Japan, India, Australia, Argentina, Poland, Turkey, Brazil, Canada, Thailand, United Kingdom, Slovakia, Czechia
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaIsrael, Korea, Republic of, Taiwan, Sweden, Germany, Italy, Turkey, China, Poland, United States, France, Australia, Thailand, United Kingdom, Mexico, Vietnam, Argentina, Belgium, Brazil, Canada, Spain
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Vitaflo International, LtdUniversity College London Hospitals; University Medical Center Groningen; University... and other collaboratorsCompletedGlycogen Storage DiseaseUnited States, United Kingdom, France, Netherlands
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Alexion Pharmaceuticals, Inc.Completed
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AM-PharmaCompleted
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Sheffield Teaching Hospitals NHS Foundation TrustCompleted
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Wuerzburg University HospitalCompleted
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Universitaire Ziekenhuizen KU LeuvenUnknownLipid Metabolism, Inborn ErrorsBelgium
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Duke UniversityRecruitingHypophosphatasiaUnited States
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Ultragenyx Pharmaceutical IncNovartis; Mereo BioPharmaCompleted
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Dr. Lothar SeefriedAlexion PharmaceuticalsCompleted
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CENTOGENE GmbH RostockAlexion PharmaceuticalsCompleted
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, Germany