- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Rett Syndrome in New Zealand
Total 4011 results
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National Cancer Institute (NCI)RecruitingChronic Myelomonocytic Leukemia | Myelodysplastic Syndrome | Myelodysplastic Syndrome With Excess Blasts | Myeloproliferative NeoplasmUnited States, Canada
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Geron CorporationActive, not recruitingMyelodysplastic SyndromesUnited States, Canada, Belgium, Spain, Czechia, Korea, Republic of, United Kingdom, Netherlands, Israel, Germany, Russian Federation, Switzerland, Italy, France, Turkey, Poland, Ukraine
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Zogenix, Inc.Zogenix International Limited, Inc., a subsidiary of Zogenix, Inc.Active, not recruitingDravet Syndrome | Epileptic Encephalopathy | Lennox Gastaut SyndromeUnited States, Australia, Belgium, Canada, Denmark, France, Germany, Italy, Mexico, Netherlands, Poland, Spain, Sweden, United Kingdom
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Rutgers, The State University of New JerseyNational Cancer Institute (NCI)CompletedMelanoma | Health Status Unknown | Dysplastic Nevus | No Evidence of DiseaseUnited States
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TakedaCompletedDravet Syndrome (DS)China, Canada, France, Hungary, Poland, United States, Spain, Greece, Australia, Brazil, Serbia, Germany, Italy, Japan, Latvia, Netherlands, Ukraine, Russian Federation
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University of Illinois at ChicagoWayne State University; Boston Children's Hospital; Duke University; University... and other collaboratorsRecruitingSturge-Weber SyndromeUnited States
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VectivBio AGCompletedShort Bowel SyndromeUnited States, France, United Kingdom, Israel, Korea, Republic of, Germany, Japan, Taiwan, Sweden, Belgium, Spain, Czechia, Hungary, Norway, Italy, Argentina, Denmark, Poland
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Memorial Sloan Kettering Cancer CenterActive, not recruitingMyelodysplastic Syndromes (MDS) | Acute Myeloid Leukemia (AML) | Acute Lymphoid Leukemia (ALL)United States
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State University of New York - Upstate Medical...CompletedAnterior Knee Pain SyndromeUnited States
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MedtronicNeuroCompletedChronic Refractory Pain Associated With Failed Back Surgery Syndrome, Epidural Fibrosis, Peripheral Causalgia, Complex Regional Pain SyndromeUnited States
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Yale UniversityBristol-Myers Squibb; Merck Sharp & Dohme LLCCompletedHIV Infections | Human Immunodeficiency Virus | AIDS | Acquired Immune Deficiency SyndromeUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingAcute Myeloid Leukemia | Down Syndrome | Myelodysplastic Syndrome | Myeloproliferative Neoplasm | Myeloid Leukemia Associated With Down SyndromeUnited States, Canada, Saudi Arabia, Puerto Rico, Australia, New Zealand
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Grünenthal GmbHCompleted
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Rutgers, The State University of New JerseyNational Heart, Lung, and Blood Institute (NHLBI)RecruitingMetabolic Syndrome | Vascular Stiffness | Insulin SensitivityUnited States
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Jazz PharmaceuticalsCompletedEpilepsy | Lennox Gastaut SyndromeUnited States, Spain, France, United Kingdom
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Foghorn Therapeutics Inc.RecruitingRefractory Acute Myeloid Leukemia | Refractory Chronic Myelomonocytic Leukemia | Relapsed Acute Myeloid Leukemia | Relapsed Myelodysplastic Syndromes | Refractory Myelodysplastic Syndromes | Advanced Hematologic Malignancy | Relapsed Chronic Myelomonocytic LeukemiaUnited States
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Icahn School of Medicine at Mount SinaiTerminatedSleep Apnea Syndromes | Obesity | Endoscopy | Gastric Bypass | BariatricsUnited States
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Celgene CorporationCompletedHIV Infections | HIV Wasting SyndromeUnited States
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Masonic Cancer Center, University of MinnesotaIncyte CorporationCompletedAcute Myeloid Leukemia | Myelodysplastic Syndromes | Myeloid and Monocytic LeukemiaUnited States
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NovartisCompletedFamilial Cold Autoinflammatory Syndrome | Cryopyrin-Associated Periodic Syndromes | Neonatal Onset Multisystem Inflammatory Disease | Muckle Wells SyndromeUnited States, Germany, Italy, Spain, United Kingdom, Turkey, France, Belgium, India
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Cairo UniversityActive, not recruitingCarpal Tunnel Syndrome | Hand BurnEgypt
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BayerActive, not recruitingAcute Respiratory Distress Syndrome (ARDS) | Post Intensive Care Syndrome (PICS)United States
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Genzyme, a Sanofi CompanyCompletedMyelodysplastic Syndromes | Secondary Acute Myeloid Leukemia (AML)United States
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Kyowa Kirin, Inc.TerminatedMyelodysplastic Syndromes | Acute Lymphoblastic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous LeukemiaUnited States
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Zynerba Pharmaceuticals, Inc.Enrolling by invitationFragile X SyndromeUnited States, United Kingdom, New Zealand, Australia
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New York CFS AssociationUnknownChronic Fatigue SyndromeUnited States
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National Cancer Institute (NCI)Active, not recruitingAcute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Acute Erythroid Leukemia | Acute Megakaryoblastic Leukemia | Myelodysplastic Syndrome | Myelodysplastic Syndrome With Excess Blasts | Refractory Anemia | Myelodysplastic Syndrome With Ring SideroblastsUnited States
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Novartis PharmaceuticalsTerminatedThrombocytopaeniaUnited States, Belgium, Australia, Canada, Hong Kong, Austria, Brazil, Czechia, Israel, Russian Federation, Spain, Sweden, Thailand, Denmark, France, Germany, Ireland, Italy, Korea, Republic of, Peru, Switzerland, Taiwan, Turkey, Hungary and more
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University of PennsylvaniaNational Heart, Lung, and Blood Institute (NHLBI); University Medical Center... and other collaboratorsEnrolling by invitationAcute Respiratory Distress Syndrome in ChildrenUnited States, Netherlands, Israel, Thailand, New Zealand, United Kingdom, Australia, Brazil, Canada, China, India, Italy, Malaysia, United Arab Emirates, Spain
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Montefiore Medical CenterForest LaboratoriesCompletedAutism Spectrum Disorder | Asperger Syndrome | Aspergers SyndromeUnited States
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Novartis PharmaceuticalsCompletedPrimary Sjögren's SyndromeUnited States, Hungary, Germany, Switzerland, United Kingdom
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Tonix Pharmaceuticals, Inc.CompletedNervous System Diseases | Musculoskeletal Diseases | Rheumatic Diseases | Muscular Diseases | Neuromuscular Diseases | Fibromyalgia | Myofascial Pain SyndromesUnited States
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Alexander KolevzonCompleted
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National Institute of Allergy and Infectious Diseases...Biogen; Autoimmunity Centers of ExcellenceTerminatedPrimary Sjögren's SyndromeUnited States
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Ono Pharma USA IncCompletedIrritable Bowel Syndrome (IBS)United States
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National Cancer Institute (NCI)CompletedRecurrent Mycosis Fungoides and Sezary Syndrome | Refractory Mycosis Fungoides and Sezary Syndrome | Stage IB Mycosis Fungoides and Sezary Syndrome AJCC v7 | Stage IIA Mycosis Fungoides and Sezary Syndrome AJCC v7 | Stage IIB Mycosis Fungoides and Sezary Syndrome AJCC v7 | Stage IIIA Mycosis... and other conditionsUnited States
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State University of New York - Upstate Medical...Terminated
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases... and other collaboratorsTerminatedAndersen-Tawil SyndromeUnited States
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SanofiCompletedAcute Myelogenous LeukemiaUnited States
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ShireNycomedCompletedShort Bowel SyndromeUnited States, Spain, France, Canada, Netherlands, Denmark, Germany, Italy, Poland, United Kingdom
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Institute of Liver and Biliary Sciences, IndiaUnknownLiver Diseases | Intra-Abdominal Hypertension | Cirrhosis, Liver | Organ Dysfunction SyndromeIndia
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Brain Trauma FoundationUnited States Department of DefenseCompleted
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Alliance for Clinical Trials in OncologyNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Myelodysplastic/Myeloproliferative NeoplasmsUnited States
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Celgene CorporationTerminatedComplex Regional Pain Syndrome, Type IUnited States
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Memorial Sloan Kettering Cancer CenterCompletedLeukemia | Non-Hodgkin's Lymphoma | Myelodysplastic Syndrome | Allogeneic Marrow TransplantUnited States
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State University of New York at BuffaloCompletedTemporomandibular Joint Dysfunction SyndromeUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Myelodysplastic/Myeloproliferative NeoplasmsUnited States, Canada, Australia, Puerto Rico
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National Center for Research Resources (NCRR)CompletedRetinitis Pigmentosa | Usher Syndrome | Congenital Hearing ImpairmentUnited States
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Aldeyra Therapeutics, Inc.CompletedSjogren-Larsson SyndromeUnited States
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Twin Star Medical, Inc.United States Department of DefenseUnknownCompartment SyndromeUnited States