- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on SCID
Total 1202 results
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Vitaflo International, LtdCompleted
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Vitaflo International, LtdJohannes Gutenberg University Mainz; Kreiskliniken ReutlingenCompleted
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Klaus ParhoferTerminated
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Nutricia UK LtdCompletedPKU | TyrosinemiasUnited Kingdom
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BioMarin PharmaceuticalCompletedPhenylketonuriaItaly, Spain, United Kingdom, Germany
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Rubius TherapeuticsTerminated
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Ludwig-Maximilians - University of MunichEuropean UnionCompletedPhenylketonuriaGermany, Italy, Spain, United Kingdom
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Florence Nightingale Hospital, IstanbulCompletedRotator Cuff Tears | Rotator Cuff Rupture | Tranexamic Acid | Shoulder Arthroscopy | Visual ClarityTurkey
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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SynlogicCompletedHealthy | PhenylketonuriaUnited States
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedIrritable Bowel Syndrome With Diarrhea | Bile Acid Malabsorption | Chronic DiarrheaUnited States
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Assiut UniversityUnknown
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Boston Children's HospitalBrigham and Women's HospitalCompletedPhenylketonuriaUnited States
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Washington University School of MedicineUniversity of Missouri-Columbia; BioMarin PharmaceuticalCompleted
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University Medical Center GroningenUMC Utrecht; University of Oxford; Academisch Medisch Centrum - Universiteit... and other collaboratorsCompletedVLCAD Deficiency | Fatty Acid Oxidation DefectsNetherlands
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Universiti Sains MalaysiaCompletedObesity | Gastroesophageal Reflux Disease | Acid RefluxMalaysia
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalCompletedPhenylketonuriaUnited States
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University of Missouri-ColumbiaBioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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BioMarin PharmaceuticalCompleted
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Alexion PharmaceuticalsTerminatedLysosomal Acid Lipase DeficiencyUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States, Canada
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Emory UniversityAtlanta Clinical and Translational Science InstituteCompleted
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The University of Texas Health Science Center,...BioMarin PharmaceuticalTerminatedPhenylketonuria | HyperphenylalaninemiaUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Brigham and Women's HospitalCompletedPhenylketonuriaUnited States
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The University of Texas Health Science Center,...BioMarin PharmaceuticalCompleted
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Emory UniversityTerminated
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Merck KGaA, Darmstadt, GermanyCompleted
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BioMarin PharmaceuticalCompleted
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Shoji YanoBioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
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BioMarin PharmaceuticalApproved for marketing
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BioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
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University GhentInstitut de Recherche en Sciences de la Sante, Burkina Faso; Addis Ababa University and other collaboratorsRecruitingDepressive Symptoms | Vitamin B 12 Deficiency | Folate Deficiency | Cognitive Development | Anemia, MegaloblasticEthiopia
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BioMarin PharmaceuticalActive, not recruitingPhenylketonuria (PKU)United States, Germany
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Akdeniz UniversityCeren KahramanCompletedDiabetic Ketoacidosis | Brain Edema | Metabolic AcidosisTurkey
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metaX Institut fuer Diatetik GmbHBirmingham Children's HospitalCompletedPhenylketonurias | Hyperphenylalaninaemia | Tetrahydrobiopterin DeficiencyUnited Kingdom
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Hydrocephalus and Neuroscience InstituteCompletedFolic Acid Deficiency | Neural Tube Defects | Spina Bifida | Anencephaly-Spina BifidaUnited States
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University of AarhusCompletedDiabetes Mellitus, Type 2 | Heart Failure With Preserved Ejection Fraction | KetonemiaDenmark
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Homology Medicines, IncEnrolling by invitationPhenylketonuria | PAH DeficiencyUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States
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University of British ColumbiaRare Disease Foundation, Vancouver, CanadaCompleted
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University of Colorado, DenverNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)WithdrawnType I DiabetesUnited States
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Brendan LeeCompleted
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Cukurova UniversityCompleted
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University of GlasgowUnknownPhenylketonuria (PKU)United Kingdom
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University Hospital, ToursInstitut National de la Santé Et de la Recherche Médicale, FranceCompletedPKU | HyperphenylalaninemiaFrance
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Dr. Linda RandolphBioMarin PharmaceuticalTerminated
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Instituto Nacional de Cardiologia Ignacio ChavezNational Council of Science and Technology, MexicoCompletedSystolic and Diastolic Blood Pressure Levels | Uric Acid Levels | Metabolic Syndrome Parameters | Hepatic EnzymesMexico