- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on SCID
Total 1201 results
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University Hospital, BordeauxRecruiting
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Fondation Ophtalmologique Adolphe de RothschildCompletedAlbinism, OcularFrance
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BioMarin PharmaceuticalCompletedTetrahydrobiopterin Deficiencies | Hyperphenylalaninemia, Non-PhenylketonuricGermany, United States
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Dr. Schär AG / SPACompletedPhenylketonurias | Inborn Errors of Metabolism | Metabolic Disease | PKUUnited Kingdom
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University of UlsanUlsan University HospitalCompletedTuberculosis | Tuberculosis, Pulmonary | Multi-drug Resistant Tuberculosis | Bronchoscopy | Transmission | Cavity | Acid Fast Bacilli Infection | InsolationKorea, Republic of
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Duke UniversityFogarty International Center of the National Institute of Health; FulbrightCompletedAcidosis | Stillbirth | Birth Asphyxia | Fetal DistressTanzania
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Baylor College of MedicineCompletedCitrullinemiaUnited States
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Eunice Kennedy Shriver National Institute of Child...Completed
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VA Office of Research and DevelopmentKessler Institute for RehabilitationActive, not recruitingSpinal Cord Injury (=3 Years) | Sublesional Bone Loss Secondary to SCIUnited States
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Mayo ClinicRecruitingSpontaneous Coronary Artery Dissection | SCADUnited States
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Mayo ClinicEnrolling by invitationSpontaneous Coronary Artery Dissection | SCADUnited States
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Fondation Ophtalmologique Adolphe de RothschildCompletedAlbinism | Fovea PlanaFrance
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Brendan LeeEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedAmino Acid Metabolism, Inborn Errors | Urea Cycle Disorders | Argininosuccinic AciduriaUnited States
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University of GlasgowCompletedPhenylketonuria (PKU)United Kingdom
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Children's Hospital Medical Center, CincinnatiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedWolman Disease | Cholesterol Ester Storage Disease | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2United States
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University of WashingtonCompleted
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Bayside HealthNational Health and Medical Research Council, Australia; Monash University; Cystic...UnknownCystic FibrosisAustralia
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National Center for Research Resources (NCRR)University of MichiganCompletedTyrosinemia, Type I
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Children's Hospital of PhiladelphiaCompletedMaple Syrup Urine DiseaseUnited States
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University Hospital, MontpellierActive, not recruitingAcute Kidney Injury | Metabolic AcidosisFrance
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S.LAB (SOLOWAYS)Center of New Medical Technologies; Triangel ScientificCompletedHyperlipoproteinemias | HyperhomocysteinemiaRussian Federation
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Aeglea BiotherapeuticsTerminatedArginase I Deficiency | HyperargininemiaCanada
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
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University Hospital, ToursInstitut National de la Santé Et de la Recherche Médicale, FranceCompletedPKU | HyperphenylalaninemiaFrance
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University of LausanneCompleted
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Children's National Research InstitutePatient-Centered Outcomes Research Institute; Eunice Kennedy Shriver National... and other collaboratorsCompleted
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Promethera TherapeuticsCompletedUrea Cycle DisordersBelgium, Spain, France, Poland
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Kaleido BiosciencesCompletedUrea Cycle DisordersSwitzerland
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National Human Genome Research Institute (NHGRI)CompletedOculocutaneous AlbinismUnited States
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia
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University of Colorado, DenverCompletedHomocystinuriaUnited States
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National Institute of Neurological Disorders and...CompletedSuccinic Semialdehyde | Dehydrogenase Deficiency | DiseasesUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...UnknownPiebaldism | Segmental VitiligoNetherlands
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McGill University Health Centre/Research Institute...March of DimesCompleted
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Chang Gung Memorial HospitalRecruitingNon-Phenylketonuric HyperphenylalaninemiaTaiwan
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Travere Therapeutics, Inc.Enrolling by invitation
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Faculty Hospital Kralovske VinohradyCompletedObstructive Sleep Apnea | Continuous Positive Airway Pressure | Fatty Acid MetabolismCzechia
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Netherlands Institute for Pigment DisordersAvita MedicalCompletedPiebaldism | Segmental VitiligoNetherlands
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Luca RonfaniUniversity of TriesteCompletedUrea Cycle Disorders, Inborn | Other Metabolic DiseasesItaly
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States
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Cytonet GmbH & Co. KGTerminatedUrea Cycle DisordersUnited States, Canada
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University of West LondonCompletedVitamin B12 DeficiencyUnited Kingdom
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National Eye Institute (NEI)CompletedAlbinism | Albinism, Oculocutaneous | Albinism, OcularUnited States
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Travere Therapeutics, Inc.Active, not recruiting
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Horizon Therapeutics, LLCCompletedUrea Cycle DisorderUnited States, Spain, Italy, Switzerland
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SynlogicCompletedHomocystinuriaUnited States
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CENTOGENE GmbH RostockWithdrawnMetabolic Disorders | Tyrosinosis | Hepatorenal Tyrosinemia | Fumarylacetoacetase Deficiency | Fah DeficiencyGermany, Sri Lanka, India
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University of Wisconsin, MadisonTerminated
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD) | LAL-DeficiencyFrance, United States, United Kingdom, Czechia