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Clinical Trials on SHOX Gene With Short Stature in United Kingdom
Total 88 results
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M.D. Anderson Cancer CenterSyndax PharmaceuticalsNot yet recruitingLeukemia | HOX GeneUnited States
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BioMarin PharmaceuticalRecruitingIdiopathic Short StatureUnited States
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Nemours Children's ClinicNovartis; Pfizer; AstraZeneca; Genentech, Inc.; Thrasher Research FundCompletedIdiopathic Short StatureUnited States, Chile
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Novo Nordisk A/SRecruitingIdiopathic Short StatureUnited States
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Children's Hospital Medical Center, CincinnatiCompleted
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PfizerCompletedIdiopathic Short StatureUnited States
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Nemours Children's ClinicNovo Nordisk A/SActive, not recruitingGrowth Hormone Deficiency | Idiopathic Short StatureUnited States
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Manchester University NHS Foundation TrustCompletedGrowth Hormone Treatment | Short StatureUnited Kingdom
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Tripler Army Medical CenterCompletedFailure to Thrive | Idiopathic Short StatureUnited States
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University of California, Los AngelesTerminatedGrowth Hormone Deficiency | Small for Gestational Age | Idiopathic Short StatureUnited States
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PfizerCompletedGrowth Hormone Deficiency | Idiopathic Short StatureUnited States
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Queen Mary University of LondonRecruitingGrowth Disorders | Short StatureUnited Kingdom
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Novo Nordisk A/SActive, not recruitingShort Stature Children Born Small for Gestational Age (SGA)France, Russian Federation, United States, India, Spain, Estonia, Japan, Italy, Algeria, Austria, Hungary, Ireland, Israel, Latvia, Poland, Serbia, Thailand, Ukraine
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Hoffmann-La RocheNo longer availableCancers With NTRK, ROS1, or ALK Gene FusionsUnited States
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Taiho Oncology, Inc.TerminatedAdvanced or Metastatic Solid Tumors Irrespective of Gene Alterations | Advanced or Metastatic Solid Tumors With Germline PTEN Inactivating MutationsUnited States, United Kingdom, Austria, France
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Children's Hospital Medical Center, CincinnatiCompleted
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Arog Pharmaceuticals, Inc.Centre Leon Berard; Fox Chase Cancer CenterUnknownGIST With D842V Mutated PDGFRA GeneUnited States, France, Spain, Italy, Germany, Norway, Poland
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Stanford UniversityCompleted
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Maimonides Medical CenterWithdrawnShort StatureUnited States
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Novo Nordisk A/SCompletedHealthy | Prader-Willi Syndrome | Genetic Disorder | Growth Disorder | Idiopathic Short StatureUnited States
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Ohio State UniversityNationwide Children's HospitalCompletedGrowth Hormone Deficiency | Panhypopituitarism | Short StatureUnited States
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Eunice Kennedy Shriver National Institute of Child...National Institutes of Health (NIH)TerminatedShort Stature | Growth Disorder | Syndromic Growth Disorder | Tall StatureUnited States
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Novartis PharmaceuticalsCompletedEstrogen Receptor Positive Breast Cancer | Advanced Solid Tumors With an Alteration of the PIK3CA GeneUnited States, Netherlands, Spain, Germany, United Kingdom
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IpsenTerminatedrhGH and rhIGF-1 Combination Therapy in Children With Short Stature Associated With IGF-1 DeficiencyInsulin-like Growth Factor-1 DeficiencyUnited States
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Eli Lilly and CompanyCompletedGrowth DisorderUnited States
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Novo Nordisk A/SCompletedGrowth Hormone Disorder | Growth Hormone Deficiency in Children | Growth Disorder | Idiopathic Short StatureUnited States
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Arkansas Children's Hospital Research InstituteActive, not recruitingGrowth Failure | Nutritional StuntingUnited States
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Novartis PharmaceuticalsCompletedSolid Tumor With p53 Wild Type StatusFrance, Germany, Singapore, Switzerland, United States
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Thomas Jefferson UniversityFederico II UniversityRecruitingPreterm Birth | Twin Pregnancy With Antenatal Problem | Short CervixUnited States, Egypt, Italy, Spain
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Stanford UniversityTerminatedToileting in Adults With Impaired Functional Status | Caregiver Burden for Those Who Care for Adults With Impaired Functional Status | UTI in Adults With Impaired Functional StatusUnited States
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Massachusetts General HospitalTerminatedTurner Syndrome | Idiopathic Short StatureUnited States
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Andrew DauberActive, not recruiting
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Eunice Kennedy Shriver National Institute of Child...TerminatedObesity | Growth Hormone Deficiency | Short StatureUnited States
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Eunice Kennedy Shriver National Institute of Child...CompletedOsteogenesis Imperfecta | Short StatureUnited States
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IpsenCompletedGrowth Disorders | Insulin-Like Growth Factor-1 DeficiencyUnited States
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Maximilian Stahl, MDSyndax PharmaceuticalsNot yet recruitingAcute Myeloid Leukemia | Leukemia | AML | AML, Adult | AML With Gene MutationsUnited States
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University of Texas Southwestern Medical CenterUCB PharmaCompletedMemory Loss Associated With Corticosteroid Use | Manic State Associated With Corticosteroid UseUnited States
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Washington University School of MedicineCompletedPatients With Post Orthotopic Heart Transplantation StatusUnited States
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Ikena OncologyRecruitingSolid Tumor | Solid Tumors, Adult | Malignant Pleural Mesothelioma (MPM) | Epithelioid Hemangioendothelioma (EHE) | NF2 Deficient Mesothelioma | Other NF2 Deficient Solid Tumors and Solid Tumors With YAP1/TAZ Fusion Genes | NF2 Deficiency | YAP1 or TAZ Gene FusionsUnited States, United Kingdom
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Mayo ClinicNational Cancer Institute (NCI)TerminatedSecondary Acute Myeloid Leukemia | Untreated Adult Acute Myeloid Leukemia | Acute Myeloid Leukemia With FLT3/ITD Mutation | Acute Myeloid Leukemia With Gene Mutations | FLT3 Tyrosine Kinase Domain Point MutationUnited States
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Nemours Children's ClinicNovo Nordisk A/S; Children's Hospital Los AngelesCompletedPituitary Dwarfism | Idiopathic Short StatureUnited States
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University of Massachusetts, WorcesterCompletedThe IGFBP-3 Stimulation Test: A New Tool for the Diagnosis of Growth Hormone Deficiency in Children.Growth Hormone Deficiency | Short StatureUnited States
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Eunice Kennedy Shriver National Institute of Child...CompletedDwarfism, Pituitary | Short Stature | Constitutional Delay of Growth and DevelopmentUnited States
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Eli Lilly and CompanyNo longer availableChronic Atypical Neutrophilic Dermatosis With Lipodystrophy and Elevated Temperature (CANDLE) | Juvenile Dermatomyositis (JDM) | Stimulator of Interferon Genes (STING)-Associated Vasculopathy With Onset During Infancy (SAVI) | Aicardi-Goutières Syndrome (AGS)United States, United Kingdom
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National Cancer Institute (NCI)CompletedTherapy-Related Acute Myeloid Leukemia | Acute Myeloid Leukemia With FLT3/ITD Mutation | FLT3 Gene Mutation | Acute Promyelocytic Leukemia With PML-RARA | Acute Myeloid Leukemia With Inv(16)(p13.1q22) or t(16;16)(p13.1;q22); CBFB-MYH11 | Acute Myeloid Leukemia With t(8;21); (q22; q22.1); RUNX1-RUNX1T1United States
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Ultragenyx Pharmaceutical IncNewcastle UniversityCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Nonaka Disease | Quadriceps Sparing Myopathy (QSM) | Distal Myopathy With Rimmed Vacuoles (DMRV)United States, Bulgaria, Canada, France, United Kingdom
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National Cancer Institute (NCI)Active, not recruitingChronic Lymphocytic Leukemia | Small Lymphocytic Lymphoma | Stage 0 Chronic Lymphocytic Leukemia | Stage I Chronic Lymphocytic Leukemia | Stage II Chronic Lymphocytic Leukemia | Ann Arbor Stage I Small Lymphocytic Lymphoma | Ann Arbor Stage II Small Lymphocytic Lymphoma | Chronic Lymphocytic Leukemia... and other conditionsUnited States
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BiogenRecruitingAmyotrophic Lateral Sclerosis Associated With a SOD1 Gene MutationUnited States, Canada, Spain, Australia, Germany, Italy, Japan, Korea, Republic of, United Kingdom, Belgium, Brazil, France, Poland, Sweden
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Vanderbilt University Medical CenterRecruitingIdiopathic Pulmonary Arterial Hypertension | Heritable Pulmonary Arterial Hypertension | Unaffected Mutation Carriers: Healthy Participants With a Known BMPR2 Gene Mutation and Normal Pulmonary Pressure and RV Function on Echo | Healthy Individuals With no Cardiopulmonary DiseaseUnited States
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Avita MedicalCompletedCellulitis | Surgical Wound | Skin Cancer | Infection | Crush Injuries | Degloving Injuries | Gun Shot Wound | Necrotizing Fasciitis | Laceration of Skin | Full-thickness Skin DefectsUnited States