- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Sphingomyelin Lipidosis
Total 571 results
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Chiesi Farmaceutici S.p.A.Chiesi USA, Inc.AvailableFabry DiseaseUnited States
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Massachusetts General HospitalCompleted
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Idorsia Pharmaceuticals Ltd.CompletedFabry DiseaseUnited States, Spain, Belgium, Australia, Austria, Canada, Germany, Ireland, Italy, Netherlands, Norway, Poland, Switzerland, United Kingdom
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ShireCompleted
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ShireCompletedFabry DiseaseUnited States, Slovenia, Australia, Finland, Poland, Czechia, United Kingdom
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University Hospital MuensterAmicus TherapeuticsCompleted
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseFrance, Poland, United States, Russian Federation, United Kingdom
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Amicus TherapeuticsCompletedFabry DiseaseCanada, Belgium, United States, Australia, Netherlands
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Idorsia Pharmaceuticals Ltd.Completed
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University Hospital, RouenUnknownAnderson-Fabry DiseaseFrance
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Zymenex A/SCompletedInfantile Globoid Cell LeukodystrophyUnited States
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Greenovation Biotech GmbHFGK Clinical Research GmbHCompleted
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Université de MontréalGenzyme, a Sanofi CompanyCompleted
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Chang Gung Memorial HospitalSanofiUnknown
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, Poland, Netherlands, Canada, Argentina, United Kingdom, Norway, Brazil, Czech Republic
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Genzyme, a Sanofi CompanyCompleted
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseCzech Republic, Estonia, Poland, Slovakia
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, France, Poland, United Kingdom
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Genzyme, a Sanofi CompanyCompleted
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Amicus TherapeuticsCompleted
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University of ZurichCompleted
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Amicus TherapeuticsCompleted
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, France, Netherlands, Puerto Rico, United Kingdom
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National Institute of Neurological Disorders and...CompletedFabry DiseaseUnited States
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National Institute of Neurological Disorders and...Completed
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National Institute of Neurological Disorders and...CompletedHealthy | Fabry DiseaseUnited States
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Children's Hospital of Fudan UniversityNot yet recruiting
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Westfälische Wilhelms-Universität MünsterChiesi GmbHRecruiting
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ISU Abxis Co., Ltd.RecruitingFabry DiseaseKorea, Republic of
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SanofiRecruiting
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SanofiRecruitingFabry's DiseaseUnited States
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Bio Sidus SARecruiting
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University of California, San FranciscoRecruitingSphingolipidoses | Enzyme DeficiencyUnited States
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Hospital Clinico Universitario de SantiagoAlvaro Hermida (Co-IP); Susana Belen Bravo; Maria Teresa Cardoso; Cristobal Colon... and other collaboratorsRecruiting
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Amicus TherapeuticsRecruiting
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Amicus Therapeutics France SASCompletedFabry Disease | Anderson Fabry DiseaseFrance
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University Health Network, TorontoOzmosis Research Inc.Completed
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4D Molecular TherapeuticsActive, not recruiting
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Bio Sidus SACompleted
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TakedaCompleted
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AVROBIOTerminatedFabry DiseaseUnited States, Australia, Brazil
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National and Kapodistrian University of AthensCompletedFabry DiseaseGreece
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Genzyme, a Sanofi CompanyCompleted
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ProtalixChiesi Farmaceutici S.p.A.CompletedFabry DiseaseUnited States, Denmark, Belgium, United Kingdom, Norway, Italy, Czechia
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ProtalixChiesi Farmaceutici S.p.A.CompletedFabry DiseaseUnited States, Spain, United Kingdom, Paraguay
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Chiesi Farmaceutici S.p.A.Iqvia Pty Ltd; ProtalixCompletedFabry DiseaseUnited States, Belgium, Denmark, Italy, United Kingdom
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HaEmek Medical Center, IsraelTerminatedLiver Fibrosis | Gaucher Disease | Spleen; FibrosisIsrael