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Clinical Trials on Spinal Muscular Atrophy With Respiratory Distress 1
Total 922 results
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Assistance Publique - Hôpitaux de ParisCompleted
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Nido Biosciences, Inc.RecruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseKorea, Republic of, Denmark, Italy, United Kingdom
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National Institute of Neurological Disorders and...CompletedSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
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Bar-Chama, Natan, M.D.RecruitingFertility IssuesUnited States
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Centre Hospitalier Universitaire, AmiensRecruitingSpinal Muscular Atrophy | Non Invasive Ventilation | Respiratory Bacterial InfectionFrance
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University Hospital, Basel, SwitzerlandCompletedLumbar Spinal Stenosis (LSS)Switzerland
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AnnJi Pharmaceutical Co., Ltd.Active, not recruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
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Karen Brorup Heje PedersenCompletedHealthy Subjects | Spinal and Bulbar Muscular AtrophyDenmark
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Synchron Medical, Inc.Active, not recruitingParalysis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Neurologic Disorder | Spinal Muscular Atrophy | Cervical Spinal Cord Injury | Stroke, Lacunar | Paralysis; Stroke | Stroke Brainstem | Tetraplegic; Paralysis | Quadriplegia/TetraplegiaUnited States
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National Center for Research Resources (NCRR)Ohio State UniversityCompletedAmyotrophic Lateral Sclerosis | Spinal Muscular Atrophy | Spinobulbar Muscular Atrophy
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Universidad Autonoma de MadridKing's College London; Centro Superior de Estudios Universitarios LasalleCompletedMuscle Atrophy | Intervertebral Disc Compression | Spine InjurySpain, United Kingdom
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Ain Shams UniversityUnknownMuscular Dystrophy | Polyneuropathies | Spinal Muscular Atrophy | Muscle Diseases | Myasthenic SyndromesEgypt
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Synchron Medical, Inc.WithdrawnParalysis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Neurologic Disorder | Spinal Muscular Atrophy | Spinal Cord Injury | Stroke, Lacunar | Upper Limb Injury | Paralysis; Stroke | Stroke, BrainstemAustralia
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National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy | Kennedys DiseaseUnited States
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MarsiBionicsHospital General Universitario Gregorio Marañon; Hospital Infantil Universitario... and other collaboratorsRecruitingCerebral Palsy | Acquired Brain Injury | Spinal Muscular AtrophySpain
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National Taiwan University HospitalUnknownColon Cancer | Spinal Muscular Atrophy | Neonatal HyperbilirubinemiaTaiwan
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BiogenRecruitingObservational, Postmarketing Surveillance Study of Spinraza Injection (Nusinersen Sodium) (STANDARD)Muscular Atrophy, SpinalKorea, Republic of
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Fondazione Policlinico Universitario Agostino Gemelli...CompletedMuscular Atrophy, Spinal | UltrasoundItaly
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalUnited States
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Hoffmann-La RocheCompleted
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Clinique Romande de ReadaptationSwiss Paraplegic Centre NottwilUnknownSpinal Cord Injuries | Muscle AtrophySwitzerland
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Fondazione Policlinico Universitario Agostino Gemelli...University of Messina; Istituto Giannina Gaslini; University of Milan; Ospedale...Recruiting
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Hoffmann-La RochePTC TherapeuticsCompletedMuscular Atrophy, SpinalUnited States
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The Children's Hospital of Zhejiang University...Withdrawn
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Seoul National University HospitalNational Research Foundation of KoreaNot yet recruitingSarcopenia | Spinal Disease
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Ramathibodi HospitalAstraZenecaCompletedSpinobulbar Muscular Atrophy | Kennedy's DiseaseThailand
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National Institute of Neurological Disorders and...CompletedMotor Neuron DiseaseUnited States
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Cystinose StiftungLabor Becker & Kollegen, Munich, Germany; Screening Labor Hannover; Genetikum... and other collaboratorsCompletedSpinal Muscular Atrophy | Cystinosis | Cystinosis, NephropathicGermany
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BiogenRecruitingMuscular Atrophy, SpinalUnited States
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BiogenCompletedMuscular Atrophy, SpinalChina
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Indiana University School of MedicineCure SMACompleted
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University Hospital FreiburgNovo Nordisk A/SCompleted
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BiogenRecruitingHealthy Volunteer | Muscular Atrophy, SpinalKorea, Republic of, Germany, Belgium, Netherlands, Italy, Poland, Canada, France, United Kingdom, Israel
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Duke UniversityCenters for Disease Control and Prevention; National ALS Registry; Agency for...CompletedMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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Milton S. Hershey Medical CenterBioSensicsNot yet recruitingAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy
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Asan Medical CenterActive, not recruitingSarcopenia | Lumbar Spinal Stenosis | Neurogenic ClaudicationKorea, Republic of
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University of Sao Paulo General HospitalAgência Brasileira de Desenvolvimento Industrial (Brazilian Agency For Industrial...Not yet recruitingBrain Injuries | Spinal Cord Injuries | Muscle AtrophyBrazil
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Duke UniversityCReATe Consortium (funded by NIH/NCATS/NINDS)CompletedAmyotrophic Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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Massachusetts General HospitalNorthwestern University; University of Florida; University of Minnesota; Henry... and other collaboratorsRecruitingALS | Kennedy Disease | MND (Motor Neurone DIsease) | PLS | PMA - Progressive Muscular Atrophy | PBP - Progressive Bulbar PalsyUnited States, Italy
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University of OklahomaCompletedCerebral Palsy | Spinal Muscular Atrophy | Arthrogryposis | Other Central Nervous System or Musculoskeletal DisordersUnited States
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University of AlbertaMcGill University; University of Toronto; Laval University; Simon Fraser UniversityRecruitingAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Degeneration | Progressive Muscular AtrophyCanada
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University of MiamiFloridaRecruitingInsulin Resistance | Spinal Cord Injuries | Tetraplegia | Muscle Loss | Paraplegia | Atrophy, MuscularUnited States
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Avidity Biosciences, Inc.RecruitingPhase 1/2 Study of AOC 1020 in Adults With Facioscapulohumeral Muscular Dystrophy (FSHD) (FORTITUDE)Muscular Dystrophies | Muscular Dystrophy, Facioscapulohumeral | FSHD | Facio-Scapulo-Humeral Dystrophy | FMD | Facioscapulohumeral Muscular Dystrophy 1 | FSHD2 | FSHD1 | FMD2 | Fascioscapulohumeral Muscular Dystrophy | Fascioscapulohumeral Muscular Dystrophy Type 1 | Fascioscapulohumeral Muscular Dystrophy... and other conditionsUnited States, United Kingdom, Canada
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Duke UniversityUCB PharmaCompletedMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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Carl Zeiss Meditec, Inc.DataMed Devices Inc.CompletedAdvanced Dry AMD With Geographic AtrophyUnited States
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LMU KlinikumRecruitingPompe Disease (Late-onset) | FSHD | Spinal Muscular Atrophy Type 3 | Inclusion Body MyositisGermany
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Stem Cells ArabiaUnknownMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy | Progressive Bulbar Palsies
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The Hong Kong Polytechnic UniversityResearch Grants Council, Hong KongRecruitingMuscular Atrophy | Child With Cancer | Child With Cerebral Palsy | Child With Medical ComplexityHong Kong
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Ohio State UniversityCompletedSpinal Cord Injuries | Metabolic Disease | Skeletal Muscle AtrophyUnited States
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Ningbo Medical Center Lihuili HospitalCompletedHemodialysis Patients With SarcopeniaChina