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Clinical Trials on Spinocerebellar Ataxia 1
Total 6035 results
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Hospital Universitário Professor Edgard SantosCompletedImmune System Diseases | Physical Disability | Tropical Spastic Paraparesis | HTLV-1 | PentoxifyllineBrazil
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National Cancer Institute (NCI)TerminatedRecurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Small Lymphocytic LymphomaUnited States
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AstraZenecaNot yet recruitingNeurofibromatosis 1 | Neurofibroma, Plexiform
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Massachusetts General HospitalJohns Hopkins UniversityNot yet recruitingNeurofibromatosis 1 | Neurofibromas, CutaneousUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruitingInterstitial Lung and Liver Disease | Infantile Liver Failure Syndrome 1 | Neurologic, Endocrine and Pancreatic Disease, Multisystem, Infantile-Onset 2 | Rajab Interstitial Lung Disease With Brain Calcifications 2France
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Tasly GeneNet Pharmaceuticals Co., LtdRecruitingCharcot-Marie-Tooth Type 1AChina
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyRecruitingPrimary Hyperoxaluria Type 3 | Primary Hyperoxaluria Type 2 | Primary Hyperoxaluria Type 1 | Primary HyperoxaluriaUnited States, Canada, Lebanon, Turkey, United Kingdom, Germany, Italy, Japan, Poland, Spain, United Arab Emirates
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University of Wisconsin, MilwaukeeNF Midwest; NF NortheastRecruitingSocial Skills | Neurofibromatosis 1United States
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National Institute of Neurological Disorders and...Recruiting
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AstraZenecaDaiichi Sankyo Co., Ltd.RecruitingPart 1: Bladder, Biliary Tract, Cervical, Endometrial, Ovarian, Pancreatic Cancer, Rare Tumors, Any Tumor Type Excluding Breast, Gastric, Colorectal Cancer | Part 2: HER2 Expressing/Amplified Solid Tumors Excluding Breast, Gastric, Colorectal CancerCanada, Korea, Republic of, Taiwan, United States, Italy, United Kingdom, Thailand, Russian Federation, India, Belgium, Australia, Poland, Spain, Japan, Brazil, Czechia, Netherlands
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Australian and New Zealand Urogenital and Prostate...RecruitingRenal Cell Carcinoma | Sarcomatoid Renal Cell Carcinoma | Papillary Renal Cell Carcinoma Type 1 | Papillary Renal Cell Carcinoma Type 2 | Chromophobe Renal Cell Carcinoma | Xp11.2 Translocation-Related Renal Cell CarcinomaAustralia
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsRecruitingGaucher Disease Type 1United States
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University of MinnesotaNational Institute of Allergy and Infectious Diseases (NIAID); National Institutes...RecruitingInfluenza | Novel Respiratory Virus-1 Middle Eastern Respiratory Syndrome Coronavirus (MERS-CoV) | Novel Respiratory Virus-2 Severe Acute Respiratory Syndrome Coronavirus (SARS-CoV)United States, Australia, Spain, Denmark, Greece, Argentina, United Kingdom, Belgium, Chile, Germany, Peru, Thailand
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Genzyme, a Sanofi CompanyActive, not recruitingGaucher Disease Type 1 | Gaucher Disease Type 3Germany, United States, Japan, United Kingdom
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University Health Network, TorontoTakara Bio Inc.Active, not recruitingMelanoma | Esophageal Cancer | Ovarian Cancer | Lung Cancer | Bladder Cancer | Liver Cancer | Synovial Sarcoma | NY-ESO-1 Expressing Solid Tumors in HLA-A2 Positive PatientsCanada
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NFlection Therapeutics, Inc.CompletedNeurofibromatosis 1 | Cutaneous NeurofibromaUnited States
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Yale UniversityThe Hospital for Sick Children; United States Department of Defense; Connecticut...CompletedChronic Pain | Neurofibromatosis 1United States
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NFlection Therapeutics, Inc.CompletedNeurofibromatosis 1 | Cutaneous NeurofibromaUnited States
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Jonsson Comprehensive Cancer CenterNovartis PharmaceuticalsWithdrawnRefractory Plasma Cell Myeloma | Recurrent Plasma Cell Myeloma | HLA-A*0201 Positive Cells Present | NY-ESO-1 Positive Tumor Cells PresentUnited States
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National Cancer Institute (NCI)CompletedNeurofibromatosis 1United States
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Baylor Research InstituteTexas Scottish Rite Hospital for ChildrenWithdrawnGaucher Disease Type 1 | Gaucher Disease Type 3United States
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Fundação Educacional Serra dos ÓrgãosCompletedNeurofibromatosis 1 | Cutaneous NeurofibromaBrazil
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Kent RobertsonCompletedNeurofibromatosis | NeurofibromasUnited States
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Indiana UniversityCompleted
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Hospices Civils de LyonRecruitingPatients With PH1 Treated With Lumasiran in FranceFrance
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Johns Hopkins UniversityNeurofibromatosis Therapeutic Acceleration ProgramRecruitingCutaneous Neurofibroma | NF1 | MonotherapyUnited States
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Medical University of LodzMedical University of Silesia; Medical University of Gdansk; Institute of Medical... and other collaboratorsNot yet recruitingDiabetes Mellitus, Type 1 | Attention Deficit Disorder With Hyperactivity
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University of StavangerStavanger Municipality, NorwayRecruitingFrailty | Healthy Aging | Alcohol Use, Unspecified | Mental Health Issue | Social Functioning | Vision and Hearing Loss | Cognitive Function, Social 1Norway
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.Not yet recruitingType I NeurofibromatosisChina
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National Cancer Institute (NCI)RecruitingMesothelioma | Familial Cancer | BRCA1-Associated Protein-1 (BAP1) Mutations | Tumor Predisposition Syndrome (TPDS)United States
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Massachusetts General HospitalUnited States Department of DefenseRecruiting
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VA Eastern Colorado Health Care SystemRecruitingHIV Infections | HIV/AIDS | Human Immunodeficiency Virus | HIV-1-infectionUnited States
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Nationwide Children's HospitalSuspendedCharcot-Marie-Tooth Neuropathy Type 1AUnited States
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Region SkaneNovartisActive, not recruitingChild | Neurofibromatosis 1 | Neurofibroma, PlexiformSweden
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Cellatoz Therapeutics, IncActive, not recruitingCharcot Marie Tooth Disease, Type 1Korea, Republic of
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National Cancer Institute (NCI)Completed
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Novartis Gene TherapiesActive, not recruitingSpinal Muscular Atrophy 1United States
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Virginia Commonwealth UniversityCompletedNeurofibromatosis 1 | Neurocognitive Deficit | Mental Health ImpairmentUnited States
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University of Wisconsin, MilwaukeeNF MidwestActive, not recruitingSocial Skills | Neurofibromatosis 1United States
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Prof. Dr. Fridoon Jawad AhmadUniversity of Lahore; Bahria International HospitalUnknownNeurokinin 1 Receptor, Substance P, Respiratory Illness, Inflammation, Covid-19, CoronavirusPakistan
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National Cancer Institute (NCI)CompletedNeurofibromatosis 1 | Neurofibroma, PlexiformUnited States
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Assistance Publique - Hôpitaux de ParisAssociation Française contre les Myopathies (AFM), ParisUnknownRespiratory Insufficiency | Myopathy | Muscular WeaknessFrance
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Assistance Publique - Hôpitaux de ParisCompletedPrimary; Complex | Pigmented Nodular Adrenocortical Disease, Primary, 1 | Periorificial Lentiginosis | Cardiac MyxomaFrance
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National Cancer Institute (NCI)TerminatedNodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Lymphoblastic Lymphoma | Recurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Mantle Cell Lymphoma | Recurrent Marginal Zone... and other conditionsUnited States
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Children's Hospital Medical Center, CincinnatiRecruitingNeurofibromatosis 1 | Noonan Syndrome | Legius Syndrome | Cardiofaciocutaneous Syndrome | Costello Syndrome | SYNGAP1-Related Intellectual Disability | DLG4 | RAS Mutation | Noonan Syndrome With Multiple Lentigines | Noonan Neurofibromatosis Syndrome | Smith-Kingsmore Syndrome | MTOR Gene Mutation | GATOR-1 Gene... and other conditionsUnited States
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Cairo UniversityNot yet recruitingMolar Incisor Hypomineralization
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Massachusetts General HospitalPatient-Centered Outcomes Research InstituteNot yet recruitingNeurofibromatosis 1United States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMuscular Dystrophy | Myotonic Dystrophy Type 2 | Myotonic Dystrophy Type 1 | Myotonic Dystrophy | Facioscapulohumeral Muscular Dystrophy | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Myotonic Muscular DystrophyUnited States
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Robert LowskyNational Cancer Institute (NCI); Janssen, LP; The Leukemia and Lymphoma Society; Rising Tide FoundationCompletedMantle Cell Lymphoma | Marginal Zone Lymphoma | Recurrent Follicular Lymphoma | Refractory Follicular Lymphoma | Grade 1 Follicular Lymphoma | Grade 2 Follicular Lymphoma | Grade 3a Follicular LymphomaUnited States
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Ain Shams UniversityCompleted