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Clinical Trials on Stargardt-Like Macular Dystrophy in United Kingdom
Total 503 results
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Stanford UniversityBiogenActive, not recruitingMyotonic Dystrophy 1United States
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University of PennsylvaniaNational Eye Institute (NEI)RecruitingAge-related Macular Degeneration | Stargardts | Retinitis Pigmentosa | Choroideremia | Geographic AtrophyUnited States
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Liverpool University Hospitals NHS Foundation TrustNot yet recruiting
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Wake Forest University Health SciencesNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMyotonic Dystrophy Type 2United States
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Foundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Choroideremia | Usher Syndrome | Batten Disease | Leber Congenital Amaurosis | Goldmann-Favre Syndrome | Kearns-Sayre Syndrome | Retinal Disease | Bardet-Biedl Syndrome | Stargardt Disease | Cone Dystrophy | Retinoschisis | Achromatopsia | Gyrate Atrophy | Eye Diseases Hereditary | Bassen-Kornzweig... and other conditionsUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); University... and other collaboratorsCompletedMyotonic Dystrophy Type 1United States
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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Ionis Pharmaceuticals, Inc.CompletedMyotonic Dystrophy Type 1United States
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Insmed IncorporatedMuscular Dystrophy AssociationCompleted
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Gillette Children's Specialty HealthcareUniversity of MinnesotaCompletedSpinal Muscular Dystrophy | Neuromuscular DisabilityUnited States
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Sheffield Hallam UniversitySheffield Teaching Hospitals NHS Foundation TrustCompletedQuality of Life | Systemic Sclerosis | Raynaud's PhenomenonUnited Kingdom
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University of WinchesterUniversity of Southampton; University of North Carolina, Chapel Hill; AlterG; University... and other collaboratorsCompletedStroke | Quality of Life | Vascular Stiffness | Gait, HemiplegicUnited Kingdom
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
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Boston Children's HospitalMuscular Dystrophy AssociationRecruitingCentronuclear Myopathy | Myotubular Myopathy | Nemaline Myopathy | Central Core Disease | Congenital Fiber Type Disproportion | Multiminicore Disease | Rigid Spine Muscular Dystrophy | Undefined Congenital MyopathyUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedCardiomyopathy, Hypertrophic | Muscular Dystrophy, OculopharyngealUnited States
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedCharcot-Marie-Tooth Disease | Facioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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ML Bio Solutions, Inc.Active, not recruiting
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University of LeedsNot yet recruitingAcute Coronary SyndromeUnited Kingdom
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GlaxoSmithKlineCompleted
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FDA Office of Orphan Products DevelopmentCompletedMuscular DystrophiesUnited States
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Edgewise Therapeutics, Inc.CompletedMuscular DystrophiesUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Terminated
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MD Stem CellsUnknownGlaucoma | Macular Degeneration | Retinal Disease | Hereditary Retinal Dystrophy | Optic Nerve DiseaseUnited States
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Wake Forest University Health SciencesCompleted
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Katherine MathewsNational Institute of Neurological Disorders and Stroke (NINDS)Recruiting
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Edgewise Therapeutics, Inc.CompletedNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Healthy VolunteerUnited States
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Cambridge University Hospitals NHS Foundation TrustUnknownStroke | Osteoarthritis | Back Pain | Sciatica | Fibromyalgia | Complex Regional Pain Syndromes | Traumatic Brain InjuryUnited Kingdom
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Duke UniversityCompleted
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Hull University Teaching Hospitals NHS TrustNational Institute for Health Research, United Kingdom; University of York; South... and other collaboratorsCompletedCoronary Artery Disease | Quality of LifeUnited Kingdom
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Children's National Research InstituteActive, not recruitingGenetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Dystrophies | Cardiac FibrosisUnited States
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Eunice Kennedy Shriver National Institute of Child...National Institutes of Health Clinical Center (CC); National Institute of Neurological... and other collaboratorsActive, not recruitingGenetic DisorderUnited States
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Columbia UniversityActive, not recruitingAge-related Macular Degeneration | Retinitis Pigmentosa | Vitelliform Macular Dystrophy | Choroidal Ischemia | Central Serous RetinopathyUnited States
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IpsenCompletedSpasticity, MuscleUnited Kingdom
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National Institute of Neurological Disorders and...RecruitingMuscular Dystrophy | Peripheral Neuropathy | Normal Physiology | Motor Neuron DisorderUnited States
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Haukeland University HospitalGolden Jubilee National HospitalRecruitingQuality of Life | Angina Pectoris | Chronic Total Occlusion of Coronary Artery | PROMNorway, United States, United Kingdom
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Massachusetts General HospitalBeth Israel Deaconess Medical Center; Brigham and Women's Hospital; University...Recruiting
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Healeon Medical IncWithdrawnFibromyalgia | RSD (Reflex Sympathetic Dystrophy) | CRPS - Complex Regional Pain Syndrome Type IUnited States, Honduras
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University of ChicagoRecruitingMuscular Dystrophy | Arrhythmia | CardiomyopathyUnited States
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Queen Mary University of LondonCompletedQuality of Life | Critical Illness | Chronic Kidney Diseases | Acute Kidney Injury | Muscle Loss | Major TraumaUnited Kingdom
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Baylor College of MedicineUnknownHeart Failure | Muscular Dystrophy | Dilated CardiomyopathyUnited States
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Johns Hopkins UniversityNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationHypertrophic Cardiomyopathy (HCM) | Long QT Syndrome (LQTS) | Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT) | Inherited Cardiac Arrythmias | Brugada Syndrome (BrS) | Early Repolarization Syndrome (ERS) | Arrhythmogenic Cardiomyopathy (AC, ARVD/C) | Dilated Cardiomyopathy (DCM) | Muscular... and other conditionsUnited States
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Massachusetts Eye and Ear InfirmaryWithdrawnAge Related Macular DegenerationUnited States
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BayerCompletedMacular EdemaSpain, Canada, Switzerland, Portugal, Austria, Poland, Slovakia, United Kingdom, France, Czechia, Germany, Hungary, Italy, Lithuania
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National Cancer Institute (NCI)CompletedSkin Diseases | Virus Diseases | Healthy | Retinal Degeneration | Muscular DystrophyUnited States
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BiositeCompletedStroke | Stroke Mimic(Conditions Presenting With Stroke-like Conditions)United States, Canada, Germany, Switzerland, United Kingdom
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William Beaumont HospitalsWithdrawnDeep Vein Thrombosis | Vascular Access Complication | Central Line Complication | Superficial Vein Thrombosis | Central Line-Associated InfectionUnited States
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University of PittsburghCompletedMuscular Dystrophy | ALS | Spinal Cord Injury | Tetraplegia | Brachial Plexus Injury | Brainstem StrokeUnited States
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University of New MexicoCompletedRetinitis Pigmentosa | Age Related Macular Degeneration | Congenital Stationary Night Blindness | ColorblindnessUnited States
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National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Muscular Dystrophy | Peripheral Nervous System Disease | Muscular DiseaseUnited States, Mali
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Khondrion BVJulius Clinical; ProPharma Group; CertaraCompletedMitochondrial Diseases | Mitochondrial DNA tRNALeu(UUR) m.3243A<G Mutation | Maternally Inherited Diabetes and Deafness (MIDD) | Mitochondrial Encephalomyopathy, Lactic Acidosis and Stroke Like Episodes (MELAS) | Chronic Progressive External Ophthalmoplegia (CPEO)Netherlands, Denmark, United Kingdom, Germany