- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Steinert Myotonic Dystrophy
Total 1512 results
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GlaxoSmithKlineCompletedMuscular DystrophiesUnited States
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GlaxoSmithKlineTerminatedMuscular DystrophiesFrance, Bulgaria, Denmark, Germany, Belgium, Canada, Spain, Turkey, United Kingdom, Korea, Republic of, Brazil, Netherlands, Italy, Japan, Czech Republic, Chile, Israel, Hungary, Russian Federation, Australia, Poland, Norway, Argentina and more
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Washington University School of MedicineBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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BioMarin PharmaceuticalTerminated
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Skulpt, Inc.National Institute of Neurological Disorders and Stroke (NINDS)CompletedDuchenne Muscular DystrophyUnited States
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University Hospital, Basel, SwitzerlandCompletedDuchenne Muscular Dystrophy
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Catholic University of the Sacred HeartUniversity of Padova; Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta; Azienda Ospedaliera San Giovanni Battista and other collaboratorsUnknown
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Nationwide Children's HospitalCompletedDuchenne Muscular DystrophyUnited States
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Chaitanya Hospital, PuneUnknownMuscular Dystrophy | Duchenne Muscular DystrophyIndia
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Summit TherapeuticsCompletedDuchenne Muscular DystrophyUnited Kingdom
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Dart Therapeutics. LLCCompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalAsklepios Biopharmaceutical, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Xiamen Ophthalmology Center Affiliated to Xiamen...Active, not recruitingBietti's Crystalline DystrophyChina
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Eye Hospital Pristina KosovoEnrolling by invitationMacular Corneal DystrophyKosovo
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Hôpital CochinAssociation Monégasque contre les MyopathiesUnknownDuchenne Muscular Dystrophy | Duchenne Muscular Dystrophy-Associated Dilated CardiomyopathyFrance
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Stanford UniversityUniversity of Pennsylvania; University of California, Davis; Oregon Health and... and other collaboratorsRecruitingFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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Michael D. Straiko, MDLions VisionGift Research; Eye Bank Association of AmericaRecruitingFuchs Endothelial DystrophyUnited States
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Trefoil Therapeutics, Inc.CompletedFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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Avidity Biosciences, Inc.RecruitingDuchenne Muscular Dystrophy | Exon 44United States
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesNo longer availableCongenital Muscular Dystrophy Due to Lamin A/C MutationUnited States
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PTC TherapeuticsTerminatedLimb-Girdle Muscular DystrophyUnited States, Norway, Canada, Sweden, Russian Federation, Denmark, France, Germany
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NS Pharma, Inc.Approved for marketingMuscular Dystrophy, Duchenne | DMD
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Hacettepe UniversityCompletedPerformance | Duchenne Muscular Dystrophy | FlexibilityTurkey
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Hacettepe UniversityCompletedPerformance | Duchenne Muscular Dystrophy | FlexibilityTurkey
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Cooperative International Neuromuscular Research...aTyr Pharma, Inc.; Muscular Dystrophy Canada; FSHD Global Research Foundation; FSH...CompletedFacioscapulohumeral Muscular DystrophyUnited States, Canada, Australia, Sweden, United Kingdom
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Rigshospitalet, DenmarkCompletedLimb-girdle Muscular DystrophyDenmark
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Universitaire Ziekenhuizen KU LeuvenFund for Scientific Research, Flanders, Belgium; Funds for Research in Ophthalmology... and other collaboratorsCompletedFuchs' Endothelial DystrophyBelgium
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Seoul National University HospitalRecruitingMuscular Dystrophy, Duchenne | Upper Extremity | Orthotic DevicesKorea, Republic of
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Benitec Biopharma, Inc.RecruitingOculopharyngeal Muscular DystrophyUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruitingDuchenne Muscular DystrophyFrance
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University of MalagaCompletedMuscular Dystrophy, Duchenne and Becker TypesSpain
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Sarepta Therapeutics, Inc.Active, not recruiting
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University of FloridaCompleted
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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National Center for Research Resources (NCRR)National Institute of Neurological Disorders and Stroke (NINDS); University...CompletedDuchenne Muscular Dystrophy
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Başak Çağla ArslanHacettepe UniversityRecruitingDuchenne Muscular Dystrophy | Occupational Therapy | GamificationTurkey
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Assiut UniversityNot yet recruitingLimb-girdle Muscular Dystrophy
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.Worldwide Clinical TrialsCompletedBecker Muscular Dystrophy | Healthy VolunteerUnited States
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Dokuz Eylul UniversityCompletedDuchenne Muscular Dystrophy | Upper Extremity ProblemTurkey
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Hacettepe UniversityCompletedPerformance | Duchenne Muscular Dystrophy | Gait | EnergyTurkey
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Rigshospitalet, DenmarkCompleted
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Istituto Ortopedico RizzoliCompletedBethlem Myopathy | Ullrich Congenital Muscular DystrophyItaly
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Santhera PharmaceuticalsCompletedMuscular Dystrophy, Duchenne | Ambulatory CareUnited States, Spain, Austria, Belgium, France, Germany, Italy, Netherlands, Sweden, Switzerland
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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University of RochesterLivionex IncCompletedCorneal Dystrophy, Band-ShapedUnited States
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University Hospital, RouenCompleted
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingDuchenne Muscular Dystrophy | Natural History | Motor Function; RetardationItaly
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Asociación para Evitar la Ceguera en MéxicoEmmecellRecruitingEndothelial Dysfunction | Corneal Edema | Fuchs' Endothelial Dystrophy | Fuchs Dystrophy | Corneal Endothelial Dystrophy | Bullous Keratopathy | Pseudophakic Bullous Keratopathy | Corneal Edema PseudophakicMexico