- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Steroid Metabolism, Inborn Errors
Total 4328 results
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Assistance Publique - Hôpitaux de ParisCompletedInborn Errors of MetabolismFrance
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CENTOGENE GmbH RostockRecruitingInborn Errors of MetabolismPakistan
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University of LausanneCompletedInborn Errors of MetabolismSwitzerland
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CENTOGENE GmbH RostockCompletedInborn Errors of Metabolism | BiomarkerEgypt, Sri Lanka, Albania, Romania, Georgia, India, Lithuania, Pakistan
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University Children's Hospital, ZurichRecruitingInborn Errors of Metabolism | TransitionSwitzerland, Austria
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Universitätsklinikum Hamburg-EppendorfRecruitingBatten Disease | Neuronal Ceroid Lipofuscinosis | CLN1 Disease | CLN2 Disease | CLN3 Disease | CLN4 Disease | CLN5 Disease | CLN6 Disease | CLN7 Disease | CLN8 Disease | CLN10 Disease | CLN11 Disease | CLN12 Disease | CLN13 Disease | CLN14 DiseaseGermany
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Universitaire Ziekenhuizen KU LeuvenUnknownLipid Metabolism, Inborn ErrorsBelgium
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Shanghai Jiao Tong University School of MedicineNot yet recruitingCongenital Adrenal HyperplasiaChina
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Diurnal LimitedNational Institutes of Health (NIH)WithdrawnCongenital Adrenal HyperplasiaUnited States
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Region StockholmEnrolling by invitationCongenital Adrenal HyperplasiaSweden
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Boston Children's HospitalCompletedAdrenal Hyperplasia, CongenitalUnited States
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Diurnal LimitedCompletedCongenital Adrenal HyperplasiaUnited States
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Haukeland University HospitalUnknownAdrenal Hyperplasia, CongenitalNorway
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Maria I. NewNational Center for Research Resources (NCRR); Office of Rare Diseases (ORD)Completed21-hydroxylase DeficiencyUnited States, Brazil
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Johnson & Johnson Pharmaceutical Research & Development...Completed21-hydroxylase DeficiencyUnited States
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National Human Genome Research Institute (NHGRI)RecruitingInborn Errors of Metabolism | Methylmalonic Acidemia | Organic AcidemiaUnited States
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Duke UniversitySuspendedLysosomal Storage Diseases | Genetic Disease | Inborn Errors of Metabolism | Glycogen Storage Disease | Storage DiseaseUnited States
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Vitaflo International, LtdCompleted
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Dr. Schär AG / SPACompletedPhenylketonurias | Inborn Errors of Metabolism | Metabolic Disease | PKUUnited Kingdom
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Aga Khan University Hospital, PakistanCompletedInborn Errors of MetabolismPakistan
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaUnited States, Japan, Italy, Germany, Turkey, India, Australia, United Kingdom, Argentina, France, Canada
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Alexion Pharmaceuticals, Inc.Not yet recruiting
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AlexionRecruiting
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Children's Mercy Hospital Kansas CityRecruiting
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Sheffield Teaching Hospitals NHS Foundation TrustNational Institute for Health Research, United Kingdom; Alexion Pharmaceuticals...Completed
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of SheffieldActive, not recruiting
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Duke UniversityRecruitingHypophosphatasiaUnited States
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Ultragenyx Pharmaceutical IncNovartis; Mereo BioPharmaCompleted
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Dr. Lothar SeefriedAlexion PharmaceuticalsCompleted
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CENTOGENE GmbH RostockAlexion PharmaceuticalsCompleted
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, Germany
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Translational Research Center for Medical Innovation...Osaka University Graduate School of MedicineCompleted
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CENTOGENE GmbH RostockWithdrawnLipoprotein Lipase Deficiency | Inborn Error of Lipid Metabolism | Corneal ArcusGermany, India, Sri Lanka
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Millendo Therapeutics US, Inc.TerminatedCongenital Adrenal HyperplasiaSpain, Israel, France, Brazil, Czechia
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Penn State UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...Completed
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Office of Rare Diseases (ORD)UnknownAdrenal Hyperplasia, CongenitalUnited States
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustCompletedPhenylketonuria | Inborn Errors of MetabolismUnited Kingdom
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Dr. Schär AG / SPACompletedPhenylketonurias | Inborn Errors of Metabolism | Metabolic Disease | PKUUnited Kingdom
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Alexion Pharmaceuticals, Inc.Not yet recruitingHypophosphatasiaUnited States, Taiwan, Thailand, Vietnam, United Kingdom, Korea, Republic of, Israel, Italy, Australia, Turkey, France, Poland, Germany, Spain, Belgium, China, Canada, Brazil, Argentina, Mexico
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaItaly, Spain, Israel, Korea, Republic of, Belgium, Germany, United States, China, France, Taiwan, Austria, Japan, India, Australia, Argentina, Poland, Turkey, Brazil, Thailand, United Kingdom, Canada, Slovakia, Czechia
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Vitaflo International, LtdUniversity College London Hospitals; University Medical Center Groningen; University... and other collaboratorsCompletedGlycogen Storage DiseaseUnited States, United Kingdom, France, Netherlands
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Alexion Pharmaceuticals, Inc.Completed
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AM-PharmaCompleted
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Sheffield Teaching Hospitals NHS Foundation TrustCompleted
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Wuerzburg University HospitalCompleted
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Monash University MalaysiaRecruiting
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National Human Genome Research Institute (NHGRI)CompletedPregnancy | Inborn Errors of Metabolism | AcidemiasUnited States