- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Steroid Metabolism, Inborn Errors
Total 4328 results
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Manchester University NHS Foundation TrustRecruitingAdrenal Hyperplasia, CongenitalUnited Kingdom
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Ain Shams UniversityRecruiting
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Federico II UniversityRecruitingCongenital Adrenal HyperplasiaItaly
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University of Texas Southwestern Medical CenterNational Institutes of Health Clinical Center (CC); University of Michigan; Children... and other collaboratorsNot yet recruitingCongenital Adrenal HyperplasiaUnited States
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Millendo Therapeutics, Inc.CompletedCongenital Adrenal HyperplasiaUnited States
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Hospices Civils de LyonCompletedCongenital Adrenal HyperplasiaFrance
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Kasr El Aini HospitalUnknownCongenital Adrenal HyperplasiaEgypt
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Hospices Civils de LyonUnknown
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CHU de ReimsUnknownGeneral Glucocorticoid ResistanceFrance
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Neurocrine BiosciencesWithdrawnCongenital Adrenal HyperplasiaUnited States
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Radboud University Medical CenterCompletedCongenital Adrenal HyperplasiaNetherlands
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National Center for Research Resources (NCRR)CompletedCongenital Adrenal HyperplasiaUnited States
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Eva Morava-KoziczChildren's Hospital of Philadelphia; Seattle Children's HospitalNot yet recruiting
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Diurnal LimitedSimbec ResearchCompletedCongenital Adrenal Hyperplasia | Adrenal Insufficiency
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Assistance Publique - Hôpitaux de ParisCompletedCongenital Adrenal HyperplasiaFrance
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University Hospital, CaenUnknown
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Office of Rare Diseases (ORD)UnknownAdrenal Hyperplasia, CongenitalUnited States, Brazil, France
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AlexionEnrolling by invitationHypophosphatasia (HPP)France, Poland, United Kingdom, Germany, Spain, Saudi Arabia, United States, Canada, Russian Federation, Australia, Italy
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Alexion PharmaceuticalsApproved for marketingHypophosphatasiaUnited States, France
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Origin BiosciencesCompletedMolybdenum Cofactor DeficiencyUnited States, Australia, United Kingdom, Germany, Netherlands, Turkey
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, Spain, Australia, United Kingdom, Italy, France, Canada, Germany, Japan, Russian Federation, Saudi Arabia, Turkey
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University of PittsburghCompleted
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LogicBio Therapeutics, IncAlexion Pharmaceuticals, Inc.Active, not recruitingMethylmalonic AcidemiaUnited States
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Hvidovre University HospitalOdense University HospitalActive, not recruitingHypophosphatasia (HPP)Denmark
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedAmino Acid Metabolism, Inborn ErrorsFrance, United Kingdom, Italy, Belgium, Germany, Switzerland
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University of FloridaCompleted
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Eunice Kennedy Shriver National Institute of Child...Completed
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Nutricia ResearchCompletedInborn Errors of Metabolism | Urea Cycle DisorderUnited States
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Diurnal LimitedCompletedCongenital Adrenal HyperplasiaUnited States
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Assiut UniversityUnknownCongenital Adrenal Hyperplasia
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Eunice Kennedy Shriver National Institute of Child...CompletedHealthy | Congenital Adrenal HyperplasiaUnited States
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Diurnal LimitedSimbec ResearchCompletedCongenital Adrenal Hyperplasia | Adrenal Insufficiency
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Baylor College of MedicineCompletedAdrenal Hyperplasia, CongenitalUnited States
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Spain, Netherlands, France, United Kingdom, Australia, Canada, Italy
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Canada, United Kingdom
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AlexionWithdrawn
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CENTOGENE GmbH RostockWithdrawnDefective MineralizationGermany, Sri Lanka, India
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, Canada
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, United Arab Emirates, United Kingdom
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Alexion PharmaceuticalsCompleted
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University of FloridaDiabetes SentryTerminatedClinical Evaluation of a Non-Invasive Hypoglycemia Detector in a Glycogen Storage Disease PopulationGlycogen Storage DiseaseUnited States
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Eunice Kennedy Shriver National Institute of Child...Completed
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Istanbul UniversityBiruni UniversityNot yet recruitingLipid Storage DiseaseTurkey
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National Institutes of Health Clinical Center (CC)Active, not recruiting
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Nantes University HospitalActive, not recruitingHYPOCHOL : A Genetically-based Strategy to Identify New Targets in Cholesterol Metabolism (HYPOCHOL)HypobetalipoproteinemiaFrance
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Rennes University HospitalCompleted
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University of Campinas, BrazilCompletedHypoalphalipoproteinemiaBrazil
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Sanquin Research & Blood Bank DivisionsRadboud University Medical Center; Maastricht University Medical Center; Atrium...Completed
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University...Recruiting
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University of British ColumbiaCanadian Institutes of Health Research (CIHR); Saudi Arabian Cultural Bureau...Unknown