- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Thalassemia in United Kingdom
Total 166 results
-
Emory UniversityPatient-Centered Outcomes Research InstituteCompletedSickle Cell Disease | Sickle Cell Anemia | Hemoglobin SC | Hemoglobin SS | Hemoglobin Beta ThalassemiaUnited States
-
Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Italy, Germany, Saudi Arabia
-
National Heart, Lung, and Blood Institute (NHLBI)Not yet recruitingSickle Cell Disease | Sickle Cell Disorders | Hb-SS Disease | Hemoglobin S | Disease Sickle Cell Anemia | Hemoglobin Beta Thalassemia DiseaseUnited States
-
DisperSol Technologies, LLCCompletedThalassemia MajorThailand, United States
-
HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedThalassemiaUnited States, Canada
-
Dana-Farber Cancer InstituteTehran University of Medical SciencesCompletedThalassemia MajorUnited States, Iran, Islamic Republic of
-
National Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Anemia, Sickle Cell | Beta-Thalassemia | Hematopoietic Stem Cell TransplantationUnited States, Canada
-
UCSF Benioff Children's Hospital OaklandNovartis PharmaceuticalsCompletedTHALASSEMIA MAJORUnited States
-
Novartis PharmaceuticalsCompletedAnemia | HemosiderosisUnited States, Germany, Belgium, United Kingdom, Italy, Canada, France
-
ShireTerminatedBeta-Thalassemia | Transfusional Iron OverloadUnited States, Lebanon, Canada, Italy, Turkey
-
FerroKin BioSciences, Inc.CompletedBeta-thalassemia | Transfusional Iron OverloadUnited States, Australia, Thailand
-
National Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Anemia | Beta ThalassemiaUnited States
-
Columbia UniversityActive, not recruitingSickle Cell Disease | Beta ThalassemiaUnited States
-
National Institute of Allergy and Infectious Diseases...TerminatedAnemia, Sickle Cell | Hemoglobinopathies | Thalassemia | Hemoglobin SC Disease | Thalassemia MajorUnited States
-
Timothy OlsonActive, not recruitingSickle Cell Disease | Thalassemia MajorUnited States
-
National Institute of Allergy and Infectious Diseases...RecruitingMalaria | Sickle Cell Disease | Alpha and Beta Thalassemia | Human PhysiologyUnited States
-
Agios Pharmaceuticals, Inc.Active, not recruitingThalassemiaUnited States, Canada, United Kingdom
-
Memorial Sloan Kettering Cancer CenterRecruitingSickle Cell Disease | Thalassemia | Thalassemia, BetaUnited States
-
Novartis PharmaceuticalsCompletedNon-transfusion Dependent ThalassemiaGreece, Taiwan, Italy, United Kingdom, Lebanon, Turkey, Malaysia, Thailand, United States
-
Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
-
Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
-
Paul SzabolcsRecruitingSickle Cell Anemia | Diamond-blackfan Anemia | Beta-thalassemia MajorUnited States
-
National Heart, Lung, and Blood Institute (NHLBI)National Institutes of Health Clinical Center (CC); National Cancer Institute...RecruitingStem Cell Transplantation | Sickle Cell Disease | Thalassemia | Graft vs Host DiseaseUnited States
-
Sangamo TherapeuticsEnrolling by invitationBlood and Lymphatic DiseasesUnited States
-
CelgeneRecruitingBeta-thalassemia | Myelodysplastic Syndromes (MDS) | Myeloproliferative Neoplasm(MPN)-Associated MyelofibrosisUnited States, Japan, United Kingdom, Turkey, Greece, France, Australia, Belgium, Bulgaria, Canada, Germany, Israel, Italy, Malaysia, Spain, Sweden, Taiwan, Thailand, Tunisia, Lebanon, China, Netherlands
-
Fairview University Medical CenterCompletedNeutropenia | Sickle Cell Anemia | Red-Cell Aplasia, Pure | Thalassemia MajorUnited States
-
Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
-
Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
-
Catherine BollardChildren's National Research InstituteActive, not recruitingThalassemia | Sickle Cell-thalassemia DiseaseUnited States
-
HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); Thalassemia Clinical Research...CompletedHematologic Diseases | Iron Overload | Hypertension, Pulmonary | Osteoporosis | Thalassemia | Beta-Thalassemia | Anemia, Cooley'sUnited States, Canada
-
Terumo BCTbioUnited States Department of Defense; U.S. Army Medical Research and Development... and other collaboratorsTerminatedTransfusion Dependent ThalassemiaUnited States, Israel, Italy, Turkey
-
Boston Children's HospitalNovartisCompletedSickle Cell Disease | Thalassemia Major | Transfusion-dependent HemachromatosisUnited States
-
CelgeneAcceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway...CompletedThalassemiaUnited States, Greece, Italy, Lebanon, Thailand, United Kingdom
-
University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Anemia | Sickle Cell-Beta0-ThalassemiaUnited States
-
Vanderbilt University Medical CenterWashington University School of Medicine; University of Alabama at BirminghamRecruitingStroke | Sickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Thalassemia | Sickle Cell-Beta0-ThalassemiaUnited States
-
University of Texas Southwestern Medical CenterWithdrawn
-
Invenux, LLCState University of New York - Downstate Medical CenterActive, not recruitingSickle Cell Disease | Sickle-Beta Zero ThalassemiaUnited States
-
Washington University School of MedicineHealthCore-NERI; Pediatric Blood and Marrow Transplant ConsortiumCompletedSevere ThalassemiaUnited States
-
Gamida Cell ltdCompletedSickle Cell Disease & ThalassemiaUnited States
-
Columbia UniversityCompletedMyelodysplastic Syndromes | Sickle Cell Disease | Aplastic Anemia | Transfusional Iron Overload | Thalassemia MajorUnited States
-
Novo Nordisk A/SRecruitingHealthy Volunteers Sickle Cell Disease, ThalassemiaUnited States
-
HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); Thalassemia Clinical Research...CompletedThalassemiaUnited States, Canada, United Kingdom
-
Julia FinkelCompletedSCD With Severe Phenotype (HbSS, HbSβ0 Thalassemia, HbSOARab)United States
-
Imara, Inc.CompletedSickle Cell DiseaseUnited States, United Kingdom
-
HaEmek Medical Center, IsraelUnknownSickle Cell Anemia | Sickle Cell β+ or β0 ThalassemiaUnited States, Israel
-
Mitchell CairoRecruitingHodgkin Lymphoma | Sickle Cell Disease | Acute Leukemia | Beta-Thalassemia | Non-hodgkin Lymphoma | Severe Aplastic Anemia | Diamond Blackfan Anemia | Amegakaryocytic Thrombocytopenia | KostmannUnited States
-
New York Medical CollegeCompletedLymphoma | Leukemia | Sickle Cell Disease | Histiocytosis | Immunodeficiencies | Inborn Errors of Metabolism | Bone Marrow Failure | Beta ThalassemiaUnited States
-
Imara, Inc.Quintiles, Inc.CompletedSickle Cell Disease | Sickle Beta 0 Thalassemia | Sickle-Cell; Hb-SCUnited States
-
Emmaus Medical, Inc.CompletedSickle Cell Anemia | Sickle ß0-ThalassemiaUnited States
-
Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Fanconi Syndrome | Anemia, Aplastic | Beta-thalassemia | Anemia, Diamond-BlackfanUnited States