- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Tissue Metabolism
Total 105354 results
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Vitaflo International, LtdRecruitingPhenylketonurias | PKU | Maple Syrup Urine Disease | Homocystinuria | Glutaric Acidemia I | Hereditary TyrosinemiaUnited Kingdom
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Bambino Gesù Hospital and Research InstituteCatholic University of the Sacred HeartCompletedGenetic Disease | Retinopathy | Methylmalonic Aciduria and Homocystinuria,Cblc TypeItaly
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Centre Hospitalier Universitaire de la RéunionCompleted
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Centre Hospitalier Universitaire de la RéunionRecruitingLipodystrophy | Dunnigan SyndromeRéunion
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Kinderkrankenhaus auf der BultSanofiCompletedType 1 Diabetes | Lipoatrophy
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University of Texas Southwestern Medical CenterTakeda; National Institutes of Health (NIH); Amylin Pharmaceuticals, LLC.CompletedDiabetes | Insulin Resistance | Hypertriglyceridemia | Hepatic SteatosisUnited States
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National Institute of Allergy and Infectious Diseases...CompletedMetabolic Diseases | HIV Infections | Nutrition Disorders | LipodystrophyUnited States
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National Institute of Allergy and Infectious Diseases...CompletedMetabolic Diseases | HIV Infections | Nutrition Disorders | LipodystrophyUnited States
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National Institute of Allergy and Infectious Diseases...CompletedHIV Infections | Lipodystrophy | HIV SeronegativityUnited States
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ShireCompletedSanfilippo Syndrome Type BUnited States, United Kingdom, Germany
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis IVA (Morquio A Syndrome)Australia
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Alexion PharmaceuticalsCompletedMPS IIIB (Sanfilippo Syndrome)Spain, Netherlands, United Kingdom, United States, Brazil
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Children's Hospitals and Clinics of MinnesotaBioMarin Pharmaceutical; Gillette Children's Specialty Healthcare; Greenwood...CompletedMucopolysaccharidosis VI | Mucopolysaccharidosis IV AUnited States
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Emory UniversityBioMarin PharmaceuticalTerminatedMucopolysaccharidosis Type IVAUnited States
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BioMarin PharmaceuticalApproved for marketingMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, Puerto Rico
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler Syndrome | Hurler-Scheie SyndromeJapan
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University of Alabama at BirminghamKaiser Permanente; University of NebraskaCompleted
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59th Medical WingUnited States Air ForceCompleted
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Ardea Biosciences, Inc.CompletedCombination Treatment Study in Subjects With Tophaceous Gout With Lesinurad and Febuxostat (CRYSTAL)Tophaceous GoutPoland, United States, Canada, Australia, New Zealand, Switzerland
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Tongji HospitalCompleted
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Savient PharmaceuticalsCompleted
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Universita di VeronaUnknownPsoriasis | Metabolic SyndromeItaly
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City of Hope Medical CenterNational Cancer Institute (NCI)Active, not recruitingBreast Carcinoma | CalcificationUnited States
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M.D. Anderson Cancer CenterRecruitingBreast CarcinomaUnited States
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University Hospital, Strasbourg, FranceUnknownFamilial Lipomatosis | Very Rare Dermatologic DiseasesFrance
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George Washington UniversityCompletedCardiovascular Diseases | Psoriasis | DyslipidemiaUnited States
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University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)RecruitingLipid Metabolism DisorderUnited States
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Université de SherbrookeHospices Civils de LyonCompleted
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Merck Sharp & Dohme LLCCompletedLipid Metabolism Disorder
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Abhimanyu GargCompletedFamilial Partial LipodystrophyUnited States
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SanofiRecruitingOsteochondrodysplasiaAustralia, Spain, Korea, Republic of, China, Italy
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Phoenix NestAparito Ltd.; Vaincres Les Maladies Lysosomales; Association Sanfilippo SudNot yet recruitingSanfilippo Syndrome Type CUnited States, France
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Phoenix NestNational Institute of Neurological Disorders and Stroke (NINDS)Enrolling by invitationSanfilippo Syndrome Type DUnited States
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agnes chenUniversity of California, Los Angeles; National Institute of Neurological Disorders... and other collaboratorsTerminatedMucopolysaccharidosis I | Cognitive DeclineUnited States
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Swedish Orphan BiovitrumCompletedSanfilippo Syndrome Type A (MPS IIIA)United States, Turkey
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Swedish Orphan BiovitrumCompletedSanfilippo Syndrome Type A (MPS IIIA)United States, Germany, Turkey
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ShireTerminatedSanfilippo SyndromeNetherlands, United Kingdom
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Oregon Health and Science UniversityUniversity of Utah; BioMarin PharmaceuticalCompleted
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Masonic Cancer Center, University of MinnesotaTerminatedHurler Syndrome | Mucopolysaccharidosis Type IH | MPS IUnited States
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler Syndrome | Hurler-Scheie SyndromeNetherlands, France, Germany, United Kingdom
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ShireCompletedSanfilippo Syndrome Type AUnited States
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Masonic Cancer Center, University of MinnesotaCompleted
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Nadia Ali, PhDBioMarin PharmaceuticalCompletedMucopolysaccharidosis IV | Morquio DiseaseUnited States
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Cliniques universitaires Saint-Luc- Université...RecruitingRare Diseases | Inborn Errors of MetabolismBelgium
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RenJi HospitalWestlake TherapeuticsNot yet recruiting
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Novartis PharmaceuticalsCompletedGoutUnited States, Colombia, Russian Federation, Taiwan, Argentina, Turkey, Germany, Singapore, Spain, Hungary, Guatemala, Poland, South Africa, Slovakia, Portugal, Belgium, Czechia, United Kingdom
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Regeneron PharmaceuticalsCompletedIntercritical GoutUnited States, Canada