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Clinical Trials on Transfusion Dependent Alpha- or Beta- Thalassemia
Total 312 results
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Northwell HealthCompletedSickle Cell Disease | Beta Thalassemia-MajorUnited States
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Cairo UniversityUnknownBeta Thalassemia Major AnemiaEgypt
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CelgeneCompletedBeta-ThalassemiaGreece, Italy, Lebanon, Thailand, Turkey
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Marwa Hassan Abdelhamed HassanAssiut UniversityNot yet recruitingEvaluate Bone Denisty Changes in Children With Beta Thalassemia Major
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsEnrolling by invitationHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Canada, Italy, United Kingdom, Germany
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Novartis PharmaceuticalsWithdrawnThalassemia (Transfusion Delendent)
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Italy, Germany, Saudi Arabia
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National Institute of Allergy and Infectious Diseases...Recruiting
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Deborah RundCompleted
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CelgeneCompletedMyelodysplastic Syndromes | Beta-thalassemiaAustria
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NovartisCompletedIron Overload | Beta-thalassemiaUnited States
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)TerminatedHeart Diseases | Cardiovascular Diseases | Beta-ThalassemiaUnited States
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Kenneth Ataga, MDAugusta UniversityCompletedSickle Cell Anemia | Sickle - Beta Thalassemia
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Sideris PharmaceuticalsTerminatedIron Overload | Beta-ThalassemiaUnited States, Canada, Lebanon, Thailand, Turkey
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Novartis PharmaceuticalsCompletedBeta-ThalassemiaUnited States
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Bioray LaboratoriesXiangya Hospital of Central South University; First Affiliated Hospital of... and other collaboratorsEnrolling by invitation
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Imara, Inc.Terminatedβ ThalassemiaIsrael, France, Malaysia, Turkey, Denmark, Georgia, Greece, Italy, Lebanon, Morocco, Netherlands, Tunisia, United Kingdom
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Acceleron Pharma Inc. (a wholly owned subsidiary...CompletedB-ThalassemiaItaly, Greece
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Institute of Hematology & Blood Diseases Hospital...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingThalassemia Major | Thalassemia, BetaChina
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Children's Hospital KarachiCompleted
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La Jolla Pharmaceutical CompanyTerminatedBeta-ThalassemiaAustralia, Thailand, United States, Greece, Italy, Lebanon, Turkey, United Kingdom
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Cairo UniversityCompletedQuality of Life | Fatigue | Cognitive Change | Beta-ThalassemiaEgypt
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Abfero Pharmaceuticals, IncWithdrawnIron Overload | Beta-ThalassemiaThailand, Lebanon, Turkey, Canada
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CorrectSequence Therapeutics Co., LtdRecruitingBeta-Thalassemia MajorChina
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First Affiliated Hospital of Guangxi Medical UniversityUnknown
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Hamad Medical CorporationTerminatedOsteoporosis | Thalassemia Majors (Beta-Thalassemia Major)Qatar
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Bioray LaboratoriesXiangya Hospital of Central South University; Sun Yat-Sen Memorial Hospital... and other collaboratorsNot yet recruiting
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Nanfang Hospital of Southern Medical UniversityShenzhen Second People's Hospital; Shenzhen Children's Hospital; ZhuHai Hospital and other collaboratorsRecruitingBeta ThalassemiaChina
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Federico II UniversityCompleted
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HemaQuest Pharmaceuticals Inc.Completed
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Tanta UniversityCompletedBeta Thalassemia MajorEgypt
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Novartis PharmaceuticalsCompletedTransfusional Iron Overload in β-thalassemiaUnited States, Greece, Argentina, Germany, Belgium, Italy, United Kingdom, France, Tunisia, Canada, Turkey, Brazil
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Novartis PharmaceuticalsCompletedTransfusional Iron Overload | β-thalassemiaItaly
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Chiesi Canada CorpCompletedIron Overload | Beta Thalassemia Major AnemiaEgypt, Indonesia
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Genzyme, a Sanofi CompanyCompletedBeta-ThalassemiaUnited States
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Children's Hospital of PhiladelphiaAnn & Robert H Lurie Children's Hospital of Chicago; The Cooley's Anemia Foundation...CompletedThalassemia Major With Severe Transfusional Iron OverloadUnited States
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Children's Hospital KarachiCompleted
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Tanta UniversityCompletedBeta ThalassemiaEgypt
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Bioray LaboratoriesXiangya Hospital of Central South University; The 923rd Hospital of Joint Logistics...Recruiting
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Nanfang Hospital of Southern Medical UniversityShenzhen Second People's Hospital; Shenzhen Children's Hospital; ZhuHai Hospital and other collaboratorsRecruiting
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Nanfang Hospital of Southern Medical University303rd Hospital of the People's Liberation Army; Liuzhou Municipal Maternity... and other collaboratorsRecruiting
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HaEmek Medical Center, IsraelCompleted
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Deborah RundCompleted
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Mahidol UniversityChaingMai UniversityCompleted
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National Institute of Diabetes and Digestive and...Completed
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Azienda Ospedaliera V. CervelloCompletedBeta-Thalassemia | Thalassemia MajorItaly
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Case Western Reserve UniversityNational Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Iron Overload | Hemoglobinopathies | Thalassemia | Beta-Thalassemia | Anemia (Iron-Loading)
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Kevin H.M. Kuo, MD, MSc, FRCPCUnknownIron Overload | Beta-ThalassemiaCanada
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Hillel Yaffe Medical CenterUnknownSickle Cell Anemia | Beta-Thalassemia | Microalbuminuria