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Clinical Trials on Transthyretin Gene Mutations
Total 1304 results
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HaoxuanZhangRecruitingGene Product Sequence Variation | Lumbar Degenerative DiseasesChina
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Arog Pharmaceuticals, Inc.Centre Leon Berard; Fox Chase Cancer CenterUnknownGIST With D842V Mutated PDGFRA GeneUnited States, France, Spain, Italy, Germany, Norway, Poland
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Betta Pharmaceuticals Co., Ltd.UnknownLung Cancer | ROS1 Gene RearrangementChina
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Universitaire Ziekenhuizen KU LeuvenCompletedFamily Study HbA2 Leuven Mutation.Belgium
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Boehringer IngelheimActive, not recruitingSolid Tumors, KRAS MutationSpain, United Kingdom, United States, Belgium
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Shanghai Jiatan Pharmatech Co., LtdCompletedPIK3CA Mutation-Related TumorsChina
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Akcea TherapeuticsRecruitingPregnancy | Hereditary Transthyretin-mediated Amyloidosis With PolyneropathyUnited States
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AstraZenecaRecruiting
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PfizerRecruitingTransthyretin Amyloid CardiomyopathyIndia
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Brigham and Women's HospitalNot yet recruitingTransthyretin Amyloid CardiopathyUnited States
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Columbia UniversityCompletedTransthyretin Amyloid CardiomyopathyUnited States
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, Brazil, Bulgaria, France, Italy, Japan, Mexico, Netherlands, Taiwan, United Kingdom, Belgium, Czechia, Denmark, New Zealand, Sweden, Korea, Republic of, Argentina, Chile, Hong Kong, Portugal
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Poland, Argentina, Australia, Belgium, France, Germany, Japan, Netherlands, Portugal, Spain, Sweden, United Kingdom, Canada, Czechia, Denmark, Hungary, Ireland, Norway, Korea, Republic of, Austria, Croatia, Israel, Latvia, Lithuan... and more
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Alexion Pharmaceuticals, Inc.RecruitingTransthyretin Amyloid CardiomyopathyUnited States, Spain, United Kingdom, Norway, Israel, Korea, Republic of, Belgium, France, Germany, Italy, Japan, China, Australia, Argentina, Austria, Taiwan, Switzerland, Canada, Sweden, Poland, Denmark, Turkey, Brazil, Netherlands, G... and more
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Neurimmune AGCompletedAmyloid Transthyretin CardiomyopathyGermany, France, Netherlands, Spain
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Blueprint Medicines CorporationActive, not recruitingNeoplasms | Neoplasms by Histologic Type | Lung Diseases | Neoplasms by Site | Adenocarcinoma | Carcinoma | Carcinoma, Non-Small-Cell Lung | Respiratory Tract Neoplasms | Carcinoma, Bronchogenic | Bronchial Neoplasms | Metastatic Lung Cancer | Antineoplastic Agents | Brain Metastases | Lung Neoplasm Malignant | EGFR... and other conditionsUnited States, Canada, Korea, Republic of, Japan, Taiwan
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AZ-VUBUnknownCancers Harbouring an EGFR Mutation, (Excluding Non-squamous Non- Small Cell Lung Cancer, a Registered Indication), a HER2 Mutation or a HER3 MutationBelgium
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PfizerCompletedTransthyretin Familial Amyloid PolyneuropathyJapan
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Sidney Kimmel Comprehensive Cancer Center at Johns...Merck Sharp & Dohme LLCActive, not recruitingHigh Tumor Mutation Burden | High TMB (Tumor Mutation Burden) | MSS (Microsatellite Stable)United States
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Illumina, Inc.CompletedDetection and Genotyping of Factor V and Factor II Point Mutations
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Sohag UniversityCompletedIrisin Gene Polymorphism in Type II Diabetic PatientsEgypt
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Iambic Therapeutics, IncRecruiting
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Affiliated Hospital to Academy of Military Medical...RecruitingEndoscopy | Mitochondrial DNA MutationChina
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The University of Hong KongUnknownAML | FLT3-ITD MutationHong Kong
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Nanfang Hospital of Southern Medical UniversityRecruitingDifferent Gene Between Different TKIs EffectionChina
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PfizerRecruiting
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N.N. Petrov National Medical Research Center of...RecruitingMelanoma | Lung Cancer | Pancreas Cancer | Refractory Cancer | Colorectal Cancer Recurrent | RAS Mutation | Ras (Kras or Nras) Gene MutationRussian Federation
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Kura Oncology, Inc.RecruitingAcute Myeloid Leukemia | Acute Myeloid Leukemia, in Relapse | Myeloid Sarcoma | Acute Myeloid Leukemia Recurrent | Mixed Phenotype Acute Leukemia | Mixed Lineage Acute Leukemia | Refractory AML | NPM1 Mutation | Mixed Lineage Leukemia Gene Mutation | AML With Mutated NPM1 | KMT2ArUnited States
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Alexion Pharmaceuticals, Inc.Eidos Therapeutics, a BridgeBio companyActive, not recruitingSymptomatic Transthyretin Amyloid CardiomyopathyJapan
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Eidos Therapeutics, a BridgeBio companyActive, not recruitingAmyloid Cardiomyopathy, Transthyretin-RelatedUnited States, Spain, Australia, Canada, Italy, Netherlands, Ireland, New Zealand, Belgium, Israel, Greece, Korea, Republic of, Czechia, Brazil, Denmark, Portugal, United Kingdom
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Aarhus University Hospital SkejbyActive, not recruitingHeart Failure | Transthyretin Amyloid CardiomyopathyDenmark
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Okayama UniversityMerck Sharp & Dohme LLCRecruitingBreast Cancer | Breast Neoplasms | Triple Negative Breast Cancer | Triple Negative Breast Neoplasms | BRCA1 Mutation | BRCA2 Mutation | BRCA Mutation | BRCA-Associated Breast CarcinomaJapan
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Enliven TherapeuticsRecruitingHER2-positive Metastatic Breast Cancer | HER2 Gene Mutation | HER2 Mutant Non-small Cell Lung Cancer | HER2 AmplificationUnited States, Spain, Korea, Republic of, Taiwan, Italy, Australia, France
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI); Genentech, Inc.RecruitingAcute Myeloid Leukemia | Therapy-Related Acute Myeloid Leukemia | Hematologic and Lymphocytic Disorder | Acute Myeloid Leukemia in Remission | FLT3 Gene Mutation | Minimal Residual Disease PersistenceUnited States
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Centre Leon BerardCompletedGastrointestinal Stromal Tumors | Resected Gastrointestinal Stromal Tumors | Non-metastatic | High Risk of Recurrence | KIT Gene MutationFrance
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Betta Pharmaceuticals Co., Ltd.UnknownNon Small Cell Lung Cancer Stage IIIB | EGFR Gene Mutation | Non Small Cell Lung Cancer Stage IIIAChina
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University Health Network, TorontoPfizerRecruitingNon-squamous Non-small-cell Lung Cancer | Stage IV Non-small Cell Lung Cancer | ROS1 Gene Rearrangement | MET Activating Mutation | MET AmplificationCanada
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Arcus Biosciences, Inc.Gilead SciencesActive, not recruitingNon Small Cell Lung Cancer | Nonsquamous Nonsmall Cell Neoplasm of Lung | Non Small Cell Lung Cancer Metastatic | Sensitizing EGFR Gene MutationUnited States, Korea, Republic of, Singapore, Taiwan
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Oncoethix GmbHCompletedTriple Negative Breast Cancer | Pancreatic Ductal Adenocarcinoma | Castrate-resistant Prostate Cancer | CRPC | NUT Midline Carcinoma | Non-small Cell Lung Cancer With Rearranged ALK Gene/Fusion Protein or KRAS Mutation
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Rutgers, The State University of New JerseyNational Cancer Institute (NCI)TerminatedAcute Lymphoblastic Leukemia | Mantle Cell Lymphoma | Non-Hodgkin Lymphoma | Myelodysplastic Syndrome | Plasma Cell Myeloma | Recurrent Diffuse Large B-Cell Lymphoma | Refractory Diffuse Large B-Cell Lymphoma | Minimal Residual Disease | Therapy-Related Acute Myeloid Leukemia | Therapy-Related Myelodysplastic... and other conditionsUnited States
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General Oncology, Inc.Myriad Genetics, Inc.RecruitingPancreatic Cancer | Pancreatic Ductal Adenocarcinoma | Pancreatic Cancer Stage IV | Breast Cancer Stage IV | BRCA1 Mutation | BRCA2 Mutation | Pancreatic Acinar Cell Carcinoma | Metastatic Pancreatic Cancer | Breast Cancer Metastatic | HER2-negative Breast Cancer | Metastatic Pancreatic Ductal Adenocarcinoma and other conditionsUnited States
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ABM Therapeutics CorporationRecruitingAdvanced Solid Tumor | RAS Mutation | NF1 Mutation | RAF MutationUnited States
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AstraZenecaCompletedHER2-ve Metastatic Breast Cancer | Germline BRCA1/2 Mutations | Somatic BRCA1/2 MutationsItaly, Spain, Poland, Taiwan, Canada, France, Germany, Korea, Republic of, Hungary, Japan, Russian Federation, Turkey, United Kingdom, United States, Bulgaria
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Inonu UniversityAnadolu UniversityActive, not recruitingInfections | Immune Response | Liver Transplant; Complications | Gene AmplificationTurkey
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University Hospital Inselspital, BerneUniversity of Zurich; University Hospital MuensterCompletedPolymorphism, Genetic | Libido | Receptors, Androgen | Androgen EffectSwitzerland
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PfizerRecruitingATTR-CM (Transthyretin Amyloid Cardiomyopathy)Korea, Republic of
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Novo Nordisk A/SActive, not recruitingTransthyretin Amyloid Cardiomyopathy (ATTR CM)United States, Netherlands, Spain, Portugal, Canada, Czechia, France, Germany, Italy, Japan
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Aarhus University HospitalUnknown
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Mahidol UniversityPfizerNot yet recruiting
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Shandong UniversityCompletedGastric Intestinal Metaplasia | Gene Expression Profiling | DuodenumChina