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Clinical Trials on Transthyretin Gene Mutations
Total 1304 results
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedHigh-Frequency Microsatellite Instability | Mismatch Repair Gene Mutation | Mutation-Negative Lynch Syndrome | Mutation-Positive Lynch SyndromeUnited States
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Columbia UniversityAttralus, Inc.RecruitingTransthyretin AmyloidosisUnited States
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Yale UniversityAlnylam Pharmaceuticals IncNot yet recruitingTransthyretin AmyloidosisUnited States
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University Hospital, CaenPfizerRecruitingAmyloidosis TransthyretinFrance
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Alnylam PharmaceuticalsCompletedA Study of the Safety, Tolerability and Pharmacokinetics of ALN-TTR02 in Japanese Healthy VolunteersTransthyretin (TTR)-Mediated AmyloidosisUnited Kingdom
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingObesity | Overweight | Ductal Breast Carcinoma In Situ | Deleterious BRCA1 Gene Mutation | Deleterious BRCA2 Gene Mutation | Premalignant LesionUnited States
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Harvard School of Public Health (HSPH)CompletedGene and Diet Interaction
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Technological Centre of Nutrition and Health, SpainCompletedGene Expression | Cardiovascular FunctionSpain
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Weill Medical College of Cornell UniversityBasser Research Center for BRCARecruiting
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University of PennsylvaniaRecruiting
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Azienda Ospedaliera Universitaria Policlinico Paolo...Unknown
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Yonsei UniversityMerck KGaA, Darmstadt, GermanyActive, not recruitingPD-L1 Positive Mutation Tumor | EBV Positive Mutation Tumor | MSI-H Mutation Tumor | POLE/POLD1 Mutation TumorKorea, Republic of
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PfizerFrench College of General Hospital Pneumologists (CPHG)CompletedNSCLC | Crizotinib | ALK Gene Rearrangement or ROS1 Gene RearrangementFrance
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Hunan Province Tumor HospitalRecruitingCarcinoma, Non-Small Cell Lung | EGFR Gene MutationChina
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National Institute of Environmental Health Sciences...Completed
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Memorial Sloan Kettering Cancer CenterMemorial Health University Medical CenterCompleted
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Alnylam PharmaceuticalsRecruitingTransthyretin-Mediated AmyloidosisUnited Kingdom
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Fudan UniversityNot yet recruitingLung Cancer | Minimal Residual Disease | EGFR Gene Mutation
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Stanford UniversityNot yet recruitingPTEN Gene Mutation | PTEN Hamartoma Tumor Syndrome | PTEN Hamartoma SyndromeUnited States
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David E GerberCancer Prevention Research Institute of Texas; Sagimet Biosciences Inc.Recruiting
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Shanghai Pulmonary Hospital, Shanghai, ChinaCompletedEGFR Gene Mutation | Lung Adenocarcinoma Stage IIIChina
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Chul KimBristol-Myers Squibb; AstraZeneca; Walter Reed National Military Medical Center; Hackensack Meridian HealthActive, not recruitingNonsmall Cell Lung Cancer | EGFR Gene MutationUnited States
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Korean Association for the Study of Targeted TherapyChonnam National University Hospital; Kyungpook National University Hospital; Konkuk University Medical Center and other collaboratorsCompletedHER2 Gene Mutation | Adenocarcinoma Lung Stage IVKorea, Republic of
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The Fourth Affiliated Hospital of Zhejiang University...CompletedNSCLC | EGFR Gene Mutation | Non-small-lung-cell CancerChina
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Fondazione I.R.C.C.S. Istituto Neurologico Carlo...University of Campania "Luigi Vanvitelli"; IRCCS National Neurological Institute...Active, not recruitingParkinson Disease | GBA Gene MutationItaly
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The Affiliated Hospital of Xuzhou Medical UniversityRecruitingType 2 Diabetes Mellitus | Genetic Mutations | Gene Polymorphisms | Susceptibility, GeneticChina
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Masonic Cancer Center, University of MinnesotaRecruitingAcute Myeloid Leukemia | Juvenile Myelomonocytic Leukemia | Acute Lymphoblastic Leukemia | AML | Acute Leukemia | Neurofibromatosis 1 | Hematologic Malignancy | Myelodysplasia | Minimal Residual Disease | Chromosome Abnormality | Monosomy 7 | Remission | Somatic Mutation | Cytogenetic Abnormality | TP53 | Fetal Hemoglobin | Intrachromosomal Amplification of Chromosome... and other conditionsUnited States
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PfizerNot yet recruitingTransthyretin Amyloidosis Cardiomyopathy (ATTR-CM)United States
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Igentify LtdSheba Medical CenterUnknown
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Poznan University of Life SciencesRecruitingSkeletal Muscle Performance | Gene PolymorphismsPoland
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Murdoch Childrens Research InstituteRoyal Children's Hospital; Peter MacCallum Cancer Centre, AustraliaNot yet recruitingArteriovenous Malformations | Vascular Malformations | MAP2K1 Gene Mutation | PIK3CA-related Overgrowth Spectrum | Vascular Anomalies | Lymphangioma | Lymphatic Malformation | KRAS G12D | Venous Malformation | Vascular Anomaly | KRAS G12C | PI3K Gene Mutation | Slow-Flow Vascular Malformation | Fast-Flow Vascular... and other conditionsAustralia
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Memorial Sloan Kettering Cancer CenterCompletedOvarian Cancer | Non Small Cell Lung Cancer | RET Gene Mutation | BRAF Gene MutationUnited States
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Ohio State University Comprehensive Cancer CenterCompletedBRCA1 Gene Mutation | BRCA2 Gene Mutation | Ductal Breast Carcinoma in Situ | Atypical Ductal Breast Hyperplasia | Lobular Breast Carcinoma in SituUnited States
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Memorial Sloan Kettering Cancer CenterUniversity of Pennsylvania; University of California, Los Angeles; Dana-Farber... and other collaboratorsActive, not recruiting
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Oregon Health and Science UniversityAttralus, Inc.RecruitingAmyloidosis | Transthyretin AmyloidosisUnited States
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Prothena Biosciences LimitedTerminatedAmyloidogenic Transthyretin (ATTR) AmyloidosisUnited States, Spain, Sweden, Portugal
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Fábio FernandesPfizerUnknown
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Alnylam PharmaceuticalsCompletedTransthyretin Mediated Amyloidosis (ATTR)United Kingdom, France, Portugal, Sweden
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI); Spectrum Pharmaceuticals, IncActive, not recruitingEGFR Exon 20 Mutation | ERBB2 Gene Mutation | Recurrent Lung Non-Small Cell Carcinoma | Stage IV Non-Small Cell Lung Cancer AJCC v7United States
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Philippe DebonnaireNot yet recruitingTransthyretin Amyloid Cardiomyopathy
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Qianqian QuNot yet recruitingMalignant Tumor of the Ovary | XRCC2 Gene Mutation
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Second Affiliated Hospital of Nanchang UniversityNanchang UniversityUnknownNon-small Cell Lung Cancer | EGFR Gene MutationChina
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Sichuan Cancer Hospital and Research InstituteNot yet recruitingNon-squamous Non-small Cell Lung Cancer | EGFR Gene MutationChina
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University Hospital, MontpellierHôpital Cochin; Hôpital Necker-Enfants Malades; Foch Hospital, Suresnes, FRANCERecruitingCystic Fibrosis | CFTR Gene MutationFrance
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Li Zhang, MDNot yet recruiting
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PfizerCompletedHereditary Transthyretin Amyloidosis (ATTRv) Cardiomyopathy (CM), Mixed PhenotypeUnited States
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The First Affiliated Hospital with Nanjing Medical...RecruitingDLBCL | Untreated | MYC Gene RearrangementChina
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Blood Transfusion Centre of SloveniaCompletedMetabolomics | Gene Expression | Immunological StatusSlovenia
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Massachusetts General HospitalRecruitingLynch Syndrome | Genetic Predisposition to Disease | Prostate Cancer | BRCA1 Mutation | BRCA2 Mutation | Prostatic Neoplasm | ATM Gene Mutation | MMR MutationUnited States
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Academic and Community Cancer Research UnitedNational Cancer Institute (NCI)Active, not recruitingMetastatic Colorectal Adenocarcinoma | Stage IV Colorectal Cancer AJCC v8 | Stage IVA Colorectal Cancer AJCC v8 | Stage IVB Colorectal Cancer AJCC v8 | Stage IVC Colorectal Cancer AJCC v8 | Stage III Colorectal Cancer AJCC v8 | Stage IIIA Colorectal Cancer AJCC v8 | Stage IIIB Colorectal Cancer AJCC... and other conditionsUnited States