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Clinical Trials on Transthyretin Gene Mutations
Total 1319 results
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Nir PeledNot yet recruitingNon Small Cell Lung Cancer | EGFR Gene Mutation | Immune Checkpoint InhibitorIsrael
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Pusan National University HospitalRecruitingNon Small Cell Lung Cancer | EGFR Gene MutationKorea, Republic of
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Intergroupe Francophone de Cancerologie ThoraciqueRecruitingNon Small Cell Lung Cancer | ALK Gene MutationFrance
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Dana-Farber Cancer InstituteAbbVie; Pharmacyclics LLC.Active, not recruitingWaldenstrom Macroglobulinemia | MYD88 Gene MutationUnited States
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Memorial Sloan Kettering Cancer CenterCompletedNon Small Cell Lung Cancer | KRAS Gene MutationUnited States
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University of WashingtonNational Cancer Institute (NCI)TerminatedRecurrent Non-Small Cell Lung Carcinoma | EGFR Activating Mutation | Stage IV Non-Small Cell Lung Cancer AJCC v7 | ALK Gene Translocation | Stage IIIB Non-Small Cell Lung Cancer AJCC v7 | ROS1 Gene TranslocationUnited States
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National Cancer Institute (NCI)CompletedTherapy-Related Acute Myeloid Leukemia | Acute Myeloid Leukemia With FLT3/ITD Mutation | FLT3 Gene Mutation | Acute Promyelocytic Leukemia With PML-RARA | Acute Myeloid Leukemia With Inv(16)(p13.1q22) or t(16;16)(p13.1;q22); CBFB-MYH11 | Acute Myeloid Leukemia With t(8;21); (q22; q22.1); RUNX1-RUNX1T1United States
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National Cancer Institute (NCI)CompletedAdult Solid Neoplasm | BRCA1 Mutation Carrier | BRCA2 Mutation CarrierUnited States
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Steen Hvitfeldt PoulsenNovo Nordisk A/SRecruitingQuality of Life | Transthyretin Amyloidosis | Transthyretin Amyloid Cardiomyopathy | Wild-Type Transthyretin-Related (ATTR)AmyloidosisDenmark
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Faeth TherapeuticsActive, not recruitingAdvanced Solid Tumor | PIK3CA Mutation | PTEN Loss of Function MutationUnited States
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Henan Cancer HospitalFundamenta Therapeutics, Ltd.Not yet recruitingAllogeneic, CAR-T, Protein Sequestration, Non-gene EditedChina
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Zhongnan HospitalActive, not recruitingPharmacokinetic | Abiraterone Acetate | Plasma Concentration | Gene Polymorphism | Metabolic AnalysisChina
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Wageningen UniversityDutch Diabetes Research FoundationCompletedExercise | Muscle | Gene Expression | MyokineNetherlands
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Vanderbilt University Medical CenterRecruitingIdiopathic Pulmonary Arterial Hypertension | Heritable Pulmonary Arterial Hypertension | Unaffected Mutation Carriers: Healthy Participants With a Known BMPR2 Gene Mutation and Normal Pulmonary Pressure and RV Function on Echo | Healthy Individuals With no Cardiopulmonary DiseaseUnited States
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Southwest Oncology GroupNational Cancer Institute (NCI)CompletedCCND1 Gene Amplification | CCND2 Gene Amplification | CCND3 Gene Amplification | CDK4 Gene Amplification | Recurrent Squamous Cell Lung Carcinoma | Stage IV Squamous Cell Lung Carcinoma AJCC v7United States
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Medical University of GrazCompletedNFAT Regulated Gene Expression in Tacrolimus Treated PatientsAustria
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Ionis Pharmaceuticals, Inc.AstraZenecaActive, not recruitingTransthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)United States, Spain
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Radiopharm Theranostics, LtdRecruitingNon Small Cell Lung Cancer | PDL1 Gene MutationAustralia
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Cancer Institute and Hospital, Chinese Academy...Not yet recruitingNon Small Cell Lung Cancer | ERBB2 Mutation-Related Tumors | Disitamab Vedotin | ERBB2 Gene Duplication
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The University of Hong KongRecruitingRecurrent Glioblastoma | Recurrent Glioma | Poly ADP Ribose Polymerase (PARP) Inhibitor | PTEN Gene Inactivation | IDH MutationHong Kong
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Istituto Scientifico Romagnolo per lo Studio e...UnknownAML | FLT3-ITD Mutation | FLT3-TKD MutationItaly
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PfizerCompletedTransthyretin (TTR) Amyloid CardiomyopathyUnited States, Taiwan, Canada, Belgium, Australia, Czechia, Sweden, Spain, Italy, Hong Kong, Germany, Netherlands, United Kingdom, France, Japan, Argentina, Brazil
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Instituto Nacional de Cancerologia de MexicoRecruitingALK Gene Mutation | Non-small Cell Lung Cancer Stage IIIBMexico
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N.N. Blokhin National Medical Research Center of...RecruitingNon Small Cell Lung Cancer | EGFR Gene Mutation | T790MRussian Federation
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BiogenRecruitingAmyotrophic Lateral Sclerosis Associated With a SOD1 Gene MutationUnited States, Canada, Spain, Australia, Germany, Italy, Japan, Korea, Republic of, United Kingdom, Belgium, Brazil, France, Poland, Sweden
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Fudan UniversityUnknownLung Cancer, Non-small Cell | EGFR Gene Mutation | EGFR T790MChina
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Steen Hvitfeldt PoulsenCompletedTransthyretin Amyloid Cardiopathy | Mitochondrial PathologyDenmark
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Indonesia UniversityDr Cipto Mangunkusumo General HospitalCompletedin Vitro Fertilization | Acupuncture | Oocyte Maturation | BCL2 Gene mRNA OverexpressionIndonesia
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Pasithea Therapeutics Corp.RecruitingAdvanced Solid Tumors | RAS Mutation | NF1 Mutation | RAF MutationUnited States
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Intellia TherapeuticsRecruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisUnited Kingdom, New Zealand, Sweden
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Intellia TherapeuticsActive, not recruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisFrance, United Kingdom, New Zealand, Sweden
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Abramson Cancer Center at Penn MedicineRecruiting
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Shanghai Changzheng HospitalUnknownRefractory Cancer | Arsenic Trioxide | p53 Mutations | Intractable CancerChina
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RecruitingAnatomic Stage III Breast Cancer AJCC v8 | Anatomic Stage IIIA Breast Cancer AJCC v8 | Anatomic Stage IIIB Breast Cancer AJCC v8 | Anatomic Stage IIIC Breast Cancer AJCC v8 | Prognostic Stage III Breast Cancer AJCC v8 | Prognostic Stage IIIA Breast Cancer AJCC v8 | Prognostic Stage IIIB Breast... and other conditionsUnited States
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Aspira Women's HealthTerminatedHereditary Breast and Ovarian Cancer | Adnexal Mass | Germline BRCA1 Gene Mutation | Germline BRCA2 Gene MutationUnited States
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Assistance Publique - Hôpitaux de ParisInstitut National de la Santé Et de la Recherche Médicale, France; ANSESNot yet recruitingEnvironmental Exposure | Genetic Predisposition | SDH Gene Mutation
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Kymera Therapeutics, Inc.SuspendedNon Hodgkin Lymphoma | Diffuse Large B Cell Lymphoma | DLBCL | MYD88 Gene MutationUnited States, United Kingdom
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Hillel Yaffe Medical CenterUnknown
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University Hospital, MontpellierCompleted
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AZ-VUBAstraZeneca; Kom Op Tegen KankerRecruitingAdvanced Cancers Harbouring Mutations in HRGBelgium
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingHereditary Transthyretin AmyloidosisItaly
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University of EdinburghBritish Heart Foundation; Netherlands Heart Foundation; Deutsches Zentrum für...Recruiting
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Ensho Health Intelligent Systems Inc.Enrolling by invitationTransthyretin Amyloid Cardiomyopathy ("ATTR-CM")Canada
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Prelude TherapeuticsRecruitingAdvanced Solid Tumor | Metastatic Solid Tumor | Non-small Cell Lung Cancers | SMARCA4 Gene MutationUnited States, France, Spain, Singapore, Netherlands
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BayerRecruitingLocally Advanced or Metastatic Solid Tumor Harboring an NTRK Gene FusionUnited States, Austria, Denmark, Germany, Italy, Norway, Spain, United Kingdom, Brazil, Russian Federation, Switzerland, Taiwan, Canada, China, Australia, Greece, Belgium, Sweden, Korea, Republic of, France, Argentina, Finland, Ireland and more
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BayerCompletedWound Healing | Gene Expression | Cell ProliferationGermany
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University Hospital, GhentFox Chase Cancer Center; Ziekenhuis Oost-LimburgCompletedBRCA1 Mutation | BRCA2 Mutation | hCGBelgium
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Jiangsu vcare pharmaceutical technology co., LTDCompletedLocally Advanced or Metastatic Solid Tumor Harboring an NTRK Gene FusionChina
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University of Eastern FinlandDSM Nutritional Products, Inc.CompletedVitamin D Receptor Target Gene Expression | Serum 25(OH)D ConcentrationFinland
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M.D. Anderson Cancer CenterSyndax PharmaceuticalsNot yet recruitingLeukemia | HOX GeneUnited States