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Clinical Trials on Trifunctional Protein Deficiency in Poland
Total 894 results
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Medical University of LodzRecruitingPostoperative Complications | Postoperative Pain | Vitamin D Deficiency | Hypocalcemia | Hypoparathyroidism Postprocedural | Postoperative Nausea | Voice HoarsenessPoland
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Children's Memorial Health Institute, PolandDepartment of Internal Medicine, Hypertension and Vascular Diseases, The...Not yet recruitingGlucose 6 Phosphatase DeficiencyPoland
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LG Life SciencesBioPartners GmbHCompletedAdult Growth Hormone Deficiency | Pituitary DisordersUnited States
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Polish Myeloma ConsortiumRoche Pharma AG; Bioscience, S.A.UnknownWaldenstrom MacroglobulinemiaPoland
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ShireCompleted
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Teva Pharmaceutical Industries, Ltd.TerminatedGrowth Hormone-DeficiencyBelarus, Bulgaria, Georgia, Greece, Hungary, Israel, Poland, Romania, Russian Federation, Serbia, Spain, Turkey, Ukraine
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Children's Memorial Health Institute, PolandSiemens Healthcare Sp. z o.o.RecruitingDemyelinating Diseases | Urinary Incontinence | Brain Tumor | Headache | Visual Impairment | Growth Deficiency | Psychomotor Retardation, Mild to SeverePoland
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Fundación para la Investigación del Hospital Clínico...Completed
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Oregon Health and Science UniversityAlaska Department of Health and Social ServicesCompletedCarnitine Palmitoyl Transferase Type 1A (CPT1A) DeficiencyUnited States
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CENTOGENE GmbH RostockCompletedHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | C1 Esterase Inhibitor Deficiency | HAE | Angio Edema | C4 Deficiency | Hereditary Angioedema Type IIITurkey, Armenia, Georgia, India, Peru, Poland, Romania
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Stowarzyszenie Pomocy Chorym na Zakrzepicę i Skazy...Unknown
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Medical University of WarsawNot yet recruitingHIV Infections | HIV-1-infection | Resistant InfectionPoland
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Bio Products LaboratoryCompletedHaemophilia BPoland, Ukraine
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Centre Leon BerardRecruitingCancer | Cancer Metastatic | ALK Fusion Protein Expression | FGFR2 Gene Translocation | FGFR3 Gene Translocation | NTRK Family Gene Mutation | Gene Fusion | ROS1 Gene Translocation | NTRK Gene Fusion Overexpression | ATIC-ALK Fusion Protein Expression | BCR-FGFR1 Fusion Protein Expression | COL1A1-PDGFB Fusion... and other conditionsFrance, Denmark, Netherlands, Austria, Germany, Italy, United Kingdom, Czechia, Poland, Slovenia, Spain
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National Center for Research Resources (NCRR)University of PennsylvaniaCompletedOsteoporosis | Growth Hormone DeficiencyUnited States
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Glycomine, Inc.Active, not recruitingPhosphomannomutase 2 DeficiencyUnited States, Spain, Portugal, Belgium, Czechia, France, Italy, Netherlands, Poland
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Spark TherapeuticsCompletedHematologic Diseases | Blood Coagulation Disorders, Inherited | Coagulation Protein Disorders | Hemorrhagic Disorders | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Gene Therapy | Blood Coagulation Disorder | Gene Transfer | Adeno-Associated Virus (AAV) | Factor VIII (FVIII) | Factor VIII (FVIII)... and other conditionsUnited States
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Hoffmann-La RocheCompleted
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, United Kingdom, Spain, Italy, Brazil, Canada, Poland
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Vifor PharmaICON Clinical Research; American Regent, Inc.CompletedChronic Kidney Disease | Iron Deficiency AnaemiaUnited Kingdom, United States, Australia, Austria, Belgium, Czech Republic, Denmark, France, Germany, Greece, Italy, Netherlands, Norway, Poland, Portugal, Romania, Spain, Sweden, Turkey
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Janssen Research & Development, LLCWithdrawnRelapsed/ Refractory Multiple MyelomaUnited States, Poland
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University of ChicagoActive, not recruitingMultiple MyelomaUnited States, Poland
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Baxalta now part of ShireCompletedHemophilia ACzechia, Bulgaria, Hungary, Poland
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Polish Myeloma ConsortiumJanssen-Cilag Ltd.; Bioscience, S.A.Recruiting
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AEterna ZentarisCompletedDiagnosis of Adult Growth Hormone Deficiency (AGDH)United States
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Erasmus Medical CenterUnknownIschemia | Oxygen DeficiencyNetherlands
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OctapharmaCompletedPrimary Immune Deficiency DisorderUnited States, Canada, Czechia, Hungary, Poland, Russian Federation, Slovakia
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TakedaRecruitingAlpha1-Antitrypsin DeficiencyItaly, United States, Poland, Portugal
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Erasme University HospitalUnknownMultiple Myeloma and Plasma Cell NeoplasmBelgium, Poland
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CSL BehringCompletedHereditary Angioedema Types I and IIBulgaria, Hungary, Poland, Romania
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Bio Products LaboratoryTerminatedHaemophilia AColombia, Germany, Poland
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Bio Products LaboratoryCompleted
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AMAG Pharmaceuticals, Inc.RecruitingChronic Kidney Disease; Iron Deficiency AnemiaUnited States, Hungary, Lithuania, Mexico, Poland
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Institut National de la Santé Et de la Recherche...RecruitingInfections | Autoimmune Diseases | Diagnosis | Immune DeficiencyFrance, United States, Australia, Belgium, Japan, Netherlands
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Kaiser PermanenteOregon Health and Science UniversityCompletedObesity | Vitamin D Deficiency | Menopause, Premature | Hot FlushesUnited States
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Pharvaris Netherlands B.V.RecruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Bulgaria, Czechia, Hungary, Spain, France, Germany, Poland, Canada, Israel
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CSL BehringParexelCompletedVon Willebrand DiseaseBulgaria, Poland, Russian Federation, Ukraine
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Ferring PharmaceuticalsCompletedIdiopathic Growth Hormone DeficiencyHungary, India, Israel, Poland, Romania, Russian Federation, Ukraine
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Oregon Health and Science UniversityAarhus University HospitalUnknownAdults Growth Hormone Deficiency.United States
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TakedaRecruitingMultiple Myeloma | Secondary Immunodeficiency (SID)Greece, Spain, Italy, Romania, Argentina, Czechia, France, Germany, Poland, Sweden, Turkey
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AMAG Pharmaceuticals, Inc.CompletedIron Deficiency AnemiaUnited States, Canada, Hungary, Latvia, Poland, Lithuania, Puerto Rico
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Bio Products LaboratoryCompletedHaemophilia BPoland, Romania, Russian Federation
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Pomeranian Medical University SzczecinNot yet recruitingOxygen Deficiency | Corona Virus Infection | ARDS Due to Disease Caused by Severe Acute Respiratory Syndrome Coronavirus 2Poland
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Watson PharmaceuticalsCompletedIron Deficiency AnemiaUnited States, Canada, Mexico, Bulgaria, India, Russian Federation, Croatia, Poland
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The Cleveland ClinicMassachusetts General Hospital; Oregon Health and Science University; Allegheny...CompletedAdult Growth Hormone Deficiency | Hypothalamic-pituitary DisordersUnited States
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Grifols Therapeutics LLCCompletedAlpha₁-Antitrypsin DeficiencyUnited States
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Michigan Technological UniversityWithdrawnHyper IgD Syndrome | Mevalonate Kinase DeficiencyUnited States, Netherlands
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Grifols Therapeutics LLCEnrolling by invitationPulmonary Emphysema in Alpha-1 Antitrypsin DeficiencyUnited States, New Zealand, Denmark, Australia, Finland, Estonia, Canada, Poland, Russian Federation, Sweden, France
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Oregon Health and Science UniversityTerminatedImmune System Diseases | Lipid Metabolism, Inborn Errors | Mevalonic Aciduria | Mevalonate Kinase Deficiency | Periodic Fever Syndromes, HereditaryUnited States
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Watson PharmaceuticalsCompletedAnemiaUnited States, Poland, Mexico, Serbia, Russian Federation