- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Ullrich Congenital Muscular Dystrophy
Total 2156 results
-
Zhejiang UniversityYake Biotechnology Ltd.RecruitingVasculitis | Amyloidosis | Autoimmune Hemolytic Anemia | POEMS SyndromeChina
-
Kerecis Ltd.Active, not recruiting
-
University Health Network, TorontoNot yet recruitingIrritable Bowel Syndrome | Gastrointestinal Dysfunction | Ehlers-Danlos Syndrome | Hypermobility SyndromeCanada
-
Vanderbilt University Medical CenterAminu Kano Teaching HospitalActive, not recruitingStroke | Sickle Cell Disease | Sickle Cell Anemia | Stroke, Ischemic | Silent Cerebral Infarct | Silent StrokeNigeria, United States
-
National Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Disease | Pulmonary Hypertension | Secondary Pulmonary Arterial HypertensionNigeria
-
HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); Thalassemia Clinical Research...CompletedHematologic Diseases | Iron Overload | Hypertension, Pulmonary | Osteoporosis | Thalassemia | Beta-Thalassemia | Anemia, Cooley'sUnited States, Canada
-
National Institutes of Health Clinical Center (CC)National Cancer Institute (NCI)CompletedKidney Cancer | Von Hippel-lindau SyndromeUnited States
-
New York Institute of TechnologyRecruitingPain, Chronic | Ehlers-Danlos SyndromeUnited States
-
Hadassah Medical OrganizationUnknownBrittle Cornea Syndrome | Ehlers-Danlos Syndrome Type 6Israel
-
University of MichiganNational Institute on Disability, Independent Living, and Rehabilitation...CompletedSpinal Cord Diseases | Spinal Stenosis | Spinal Cord Injury | Spina Bifida | Syringomyelia | Spinal Neoplasms | Transverse Myelitis | Spinal Cord Involvement | Polio and Post-polio SyndromeUnited States
-
Boston Children's HospitalBoston Children's Hospital - Children's Rare Disease Cohorts InitiativeRecruitingMovement Disorders | Neurodegenerative Diseases | Motor Neuron Disease | Spasticity, Muscle | Pediatric Disorder | Hereditary Spastic ParaplegiaUnited States
-
Mayo ClinicRecruitingAutosomal Dominant Polycystic Kidney | Autosomal Dominant Polycystic Liver Disease | Renal Cyst | Hepatic CystUnited States
-
Taipei Medical University Shuang Ho HospitalUniversity of Southern CaliforniaEnrolling by invitationChronic Kidney Diseases | Autosomal Dominant Polycystic Kidney DiseaseTaiwan
-
National Institute of Neurological Disorders and...CompletedAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Hereditary Spastic ParaplegiaUnited States
-
Mayo ClinicRecruitingIschemic Stroke | Transient Ischemic Attack | Moyamoya Disease | Subarachnoid Hemorrhage | Vascular Dementia | Arteriovenous Fistula | Aneurysmal Subarachnoid Hemorrhage | Leukoaraiosis | Cerebrovascular Disease | Intracerebral Hemorrhage | Anoxic Brain Injury | Reversible Cerebral Vasoconstriction Syndrome | C... and other conditionsUnited States
-
National Heart, Lung, and Blood Institute (NHLBI)CompletedChronic Kidney Disease | Sickle Cell Disease | Pulmonary HypertensionUnited States
-
Genetic Disease InvestigatorsOptos, PLCCompletedMultiple Sclerosis | Ehlers-Danlos SyndromeUnited States
-
National Cancer Institute (NCI)CompletedKidney Cancer | Hippel-Lindau DiseaseUnited States
-
Betta Pharmaceuticals Co., Ltd.Not yet recruitingRenal Cell Carcinoma | Solid Tumor | Von Hippel-Lindau DiseaseChina
-
UNC Lineberger Comprehensive Cancer CenterLantheus Medical ImagingCompletedKidney Disease, Chronic | Von-Hippel LindauUnited States
-
University of Illinois at ChicagoPatient-Centered Outcomes Research Institute; American Heart Association; University... and other collaboratorsCompletedMyocardial Infarction | Heart Failure | Pneumonia | Chronic Obstructive Pulmonary Disease | Sickle Cell DiseaseUnited States
-
National Cancer Institute (NCI)CompletedRenal Cancer | Von Hippel LindauUnited States
-
M.D. Anderson Cancer CenterPfizerTerminatedRenal Cell Carcinoma | Von Hippel-Lindau Syndrome | HemangioblastomaUnited States
-
Milton S. Hershey Medical CenterDysautonomia InternationalCompletedPostural Tachycardia Syndrome | Ehlers-Danlos SyndromeUnited States
-
National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Sickle Cell | Blood Disease | Chlamydia Infections | Cerebrovascular Accident
-
Inozyme PharmaGACI GlobalNot yet recruitingATP-Binding Cassette Subfamily C Member 6 Deficiency | Ectonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency
-
University Health Network, TorontoRecruitingHypermobile EDS (hEDS) | Hypermobility SyndromeCanada
-
National Institute of Allergy and Infectious Diseases...RecruitingEosinophilic Esophagitis | Atopic Dermatitis | Food Allergy | Loeys-Dietz SyndromeUnited States
-
Queen Mary University of LondonUniversity College, LondonCompletedIrritable Bowel Syndrome | Functional Gastrointestinal Disorders | Hypermobile Ehlers-Danlos SyndromeUnited Kingdom
-
University of RochesterRecruitingLymphoma | Myelodysplastic Syndromes | Multiple Myeloma | Solid Tumor | Acute Leukemia | Aplastic Anemia | Chronic Leukemia | Immune Deficiency Disorder | Congenital Hematological Disorder | Metabolism DisorderUnited States
-
The University of Texas Health Science Center,...Society for Pediatric DermatologyCompletedTuberous Sclerosis | Neurofibromatoses | Neurofibroma | AngiofibromaUnited States
-
Masonic Cancer Center, University of MinnesotaNational Cancer Institute (NCI)TerminatedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Fanconi Anemia | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative Diseases | Graft Versus Host Disease | Diamond-blackfan AnemiaUnited States
-
Massachusetts General HospitalRecruitingBone Marrow and Kidney Transplant for Patients With Chronic Kidney Disease and Blood Disorders (BMT)Autoimmune Diseases | Multiple Myeloma | Hodgkin Disease | AL Amyloidosis | Myelofibrosis | Chronic Kidney Disease | Sickle Cell Anemia | Thalassemia | Aplastic Anemia | Chronic Lymphocytic Leukemia (CLL) | Acute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS) | Non-Hodgkin... and other conditionsUnited States
-
University of California, San DiegoNew York University; Heinrich-Heine University, Duesseldorf; Universität TübingenRecruitingGenetic Disease | Mitochondrial Encephalomyopathies | Neonatal Encephalopathy | Mutation | Hereditary Spastic Paraplegia | White Matter Disease | Spastic ParaplegiaUnited States
-
M.D. Anderson Cancer CenterNational Cancer Institute (NCI)TerminatedMeningioma | Neuroendocrine Neoplasm | Multiple Endocrine Neoplasia Type 1 | Von Hippel-Lindau Syndrome | Metastatic Well Differentiated Neuroendocrine Neoplasm | Somatostatin Positive Neoplastic Cells PresentUnited States
-
RFM Renal Treatment ServicesUnknownChronic Kidney Disease | Left Ventricular Hypertrophy | Renal OsteodystrophyTurkey
-
Travere Therapeutics, Inc.RecruitingFocal Segmental Glomerulosclerosis | Immunoglobulin A Nephropathy | Minimal Change Disease | Alport Syndrome | IgA VasculitisUnited States, Italy, Netherlands, Poland, Spain, United Kingdom, Germany, Sweden
-
University of ZurichUnknownPustular Psoriasis | Erosive Pustular Dermatosis of the Scalp | Behcet's Disease | Dermatitis Herpetiformis | Pyoderma Gangrenosum | Linear IgA Bullous Dermatosis | Other Specified Inflammatory Disorders of Skin or Subcutaneous Tissue | Sweet's Syndrome | Bowel-associated Dermatosis-arthritis Syndrome | Acute Generalized Exanthematous Pustulosis and other conditionsSwitzerland
-
Genetic Disease InvestigatorsCompletedVenous Insufficiency | Postural Orthostatic Tachycardia Syndrome | Dysautonomia | Ehlers Danlos Syndrome | External HydrocephalusUnited States
-
Westlake UniversityBeijing Obstetrics and Gynecology HospitalCompletedPregnancy Complications | Preterm Birth | Gestational Diabetes | Pregnancy Loss | Recurrent Pregnancy Loss | Birth Defect | Gestational Hypertension | Pregnancy Induced Hypertension | Health Problems in PregnancyChina
-
National Institute of Neurological Disorders and...CompletedNeoplasms | Kidney Neoplasms | Kidney Diseases | Retinal Diseases | DeafnessUnited States
-
Peking University First HospitalRecruitingRenal Cell Carcinoma | VHL SyndromeChina
-
IRCCS San RaffaeleUniversità Vita-Salute San RaffaeleRecruitingCarcinoma, Renal Cell | Von Hippel-Lindau DiseaseItaly
-
RWTH Aachen UniversityCompletedCognitive Impairment | Postural Tachycardia Syndrome | Dysautonomia | Pure Autonomic Failure | Ehlers-Danlos Syndrome | Autonomic FailureGermany
-
Nanjing Jinling HospitalPeking University; Shandong University; Sun Yat-sen University; Huazhong University... and other collaboratorsUnknownPreterm Birth | Low Birth Weight | Birth Defects | Gestational Diabetes | Fetal Death | Stillbirth | Spontaneous Abortion | Gestational Hypertension | Pregnancy With Medical Condition (Non-Specific)China
-
Centre Hospitalier Universitaire DijonCompletedNew Phenotype (Combining Premature White Hair, Polycystic Kidney Disease, Aortic Dilation/Dissection and Lymphopenia)France
-
National Cancer Institute (NCI)RecruitingNeuroendocrine Tumors | Von Hippel-Lindau Disease | VHL Pancreatic Neuroendocrine TumorsUnited States
-
University Hospital, AngersUnknownType 2 Diabetes | Chronic Kidney Disease | Pseudoxanthoma ElasticumFrance
-
Motric BioRecruitingStroke | Multiple Sclerosis | Cerebral Palsy | Spinal Cord Injuries | Dystonia | Muscle Spasticity | Hereditary Spastic Paraplegia | Hypertonia, MuscleUnited States
-
Augusta UniversityCompletedVascular Diseases | Body Weight Changes | Cardiovascular Abnormalities | HIV-1-infection | Body Fat Disorder | HIV-Associated Lipodystrophy Syndrome | Antiviral Drug Adverse Reaction | Abnormality of Adipose TissueUnited States