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Clinical Trials on Ullrich Congenital Muscular Dystrophy
Total 2164 results
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Cure HHTUniversity of North CarolinaNot yet recruitingEpistaxis | Hereditary Hemorrhagic Telangiectasia
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Unity Health TorontoUnited States Department of DefenseActive, not recruitingHereditary Hemorrhagic Telangiectasia | Epistaxis NosebleedCanada
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Sanifit Therapeutics S. A.Clinipace WorldwideCompletedCardiovascular Diseases | Cardiovascular Abnormalities | ESRD | Coronary Artery Calcification | Endstage Renal Disease | Calcifications, VascularSpain, United States, United Kingdom
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University of MinnesotaAmerican Rhinologic SocietyCompletedEpistaxis | Hereditary Hemorrhagic TelangiectasiaUnited States
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IRCCS Policlinico S. MatteoCompletedEpistaxis | Hereditary Hemorrhagic TelangiectasiaItaly
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University of Colorado, DenverPKD FoundationCompletedPolycystic Kidney, Autosomal DominantUnited States
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Changlin MeiThe First Affiliated Hospital with Nanjing Medical University; The First Affiliated... and other collaboratorsCompletedPolycystic Kidney, Type 1 Autosomal Dominant DiseaseChina
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University Hospital TuebingenCompleted
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UMC UtrechtRecruitingPseudoxanthoma ElasticumNetherlands
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)CompletedHypertension, Pulmonary | ThalassemiaUnited States
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University of PittsburghTerminatedEnd Stage Renal Disease | Arteriovenous Fistula | Arteriovenous GraftUnited States
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University Health Network, TorontoEnrolling by invitationHypermobile Ehlers-Danlos Syndrome | Ehlers-Danlos Syndrome | Vascular Ehlers-Danlos Syndrome | Hypermobile EDS (hEDS) | EDS | Classical Ehlers-Danlos Syndrome | Classical EDS (cEDS) | Vascular EDS (vEDS)Canada
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National Cheng-Kung University HospitalCompletedDiabetes Mellitus | Arteriovenous Fistula | End-stage Kidney DiseaseTaiwan
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Washington University School of MedicineRecruitingSevere Combined Immunodeficiency | Chronic Granulomatous Disease | DiGeorge Syndrome | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | X-linked Lymphoproliferative Syndrome | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | IPEX | Autoimmune Lymphoproliferative Syndrome | Common Variable... and other conditionsUnited States
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VenoStentRecruitingChronic Kidney Diseases | Renal Insufficiency | Renal Failure | End Stage Renal Disease | Hemodialysis Access Failure | ESRD | Arteriovenous Fistula | Vascular Access Complication | Catheter Complications | Catheter DysfunctionUnited States
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yuanli ZhaoPeking University International HospitalRecruitingEpilepsy | Seizures | Seizures, Epileptic | Cavernous Malformation, Cerebral | Cavernous Angioma | Cavernous Hemangioma | Cavernous Hemangioma of BrainChina
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University Hospital, Strasbourg, FranceCompleted
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AJapan
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AItaly, Sweden, Netherlands, Austria, Spain, United States, Switzerland, Germany, France, Hungary, Greece, Slovenia, Czechia, Slovakia, Poland
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Novo Nordisk A/SCompletedComparison of the Action of Drugs in the Body and Safety of N8 and Advate® in Haemophilia A SubjectsCongenital Bleeding Disorder | Haemophilia ASpain, Germany, Switzerland, Italy, Israel
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Germany, Switzerland, United Kingdom, Italy, Japan, Turkey
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia ASpain, Germany, Malaysia, Latvia
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited Kingdom, Malaysia
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Duke UniversityCompleted
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rEVO BiologicsCompletedAntithrombin Deficiency, CongenitalFrance, United Kingdom, Germany, United States, Sweden, Italy
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Unity Health TorontoNational Institutes of Health (NIH)RecruitingEpistaxis | Hereditary Hemorrhagic Telangiectasia | NosebleedsCanada
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Hospices Civils de LyonCompletedTelangiectasia, Hereditary Hemorrhagic | Rendu Osler DiseaseFrance
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Washington University School of MedicineCompletedHereditary Hemorrhagic TelangiectasiaUnited States
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Hospices Civils de LyonTerminatedEpistaxis | Hereditary Hemorrhagic TelangiectasiaFrance
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Sultan Qaboos UniversityRecruitingAnalgesia | Varicocele | Hydrocele | Inguinal Surgery | Undescended Testes | Torsion Testis | Ilioinguinal Nerve BlockOman
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Washington University School of MedicineRecruiting
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University of UtahThe Hospital for Sick Children; Boston Children's HospitalCompletedAtherosclerosis | Down Syndrome | Cardiovascular Risk FactorUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AMexico
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Vanderbilt University Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS); Aminu Kano... and other collaboratorsCompletedStroke | Sickle Cell DiseaseNigeria
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Medical University of South CarolinaNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedSickle Cell Disease | Stroke IschemicUnited States
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University of Southern CaliforniaNational Heart, Lung, and Blood Institute (NHLBI)CompletedCerebrovascular Disorders | Anemia, Sickle Cell | Blood Disease | Cerebrovascular Accident
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Novo Nordisk A/STerminatedHealthy | Congenital Bleeding Disorder | Haemophilia AAustria, Spain, United Kingdom, France, Germany
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AAustria, Spain, United States, Germany, Serbia, Taiwan, Bulgaria
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Netherlands, Spain, Germany, France, Denmark
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St. Joseph's Hospital and Medical Center, PhoenixTranslational Genomics Research InstituteTerminatedIntraventricular Hemorrhage | Spina BifidaUnited States
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Alice K. GongTerminatedInfantile Hemangioma | Very Low Birth Weight InfantsUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Sickle Cell | Blood Disease | Cerebrovascular Accident
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Sickle Cell | Blood Disease | Cerebrovascular Accident
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Marie Luise Bisgaard, MDUnknownVon Hippel-Lindaus DiseaseDenmark
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Glanzmann's DiseaseSpain, Bulgaria, Pakistan, Belgium, Germany, France, United Kingdom, Italy, Hungary, Netherlands, United States, Algeria, Austria, Sweden, Switzerland
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University Hospital TuebingenTerminatedHemangioma of Preterm Infants
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Centre Hospitalier Universitaire de Saint EtienneEnrolling by invitationStroke | Apnea SyndromeFrance
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University of AarhusLundbeck Foundation; AP Moeller Foundation; The Korning Foundation DenmarkCompletedAortic Aneurysm | Turner Syndrome | Klinefelter Syndrome | Triple X Syndrome | 47 XYY SyndromeDenmark
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Mayo ClinicRecruitingChronic Kidney Diseases | Transplant | Neurogenic Bladder | Bladder Outlet Obstruction | Bladder Dysfunction | Bladder Exstrophy | Bladder Absence | Posterior Urethral Valve | Failure, KidneyUnited States
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Sklifosovsky Institute of Emergency CareRecruitingArteriovenous Malformations | Tumor, Brain | Cavernoma | Intracerebral HematomaRussian Federation