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Clinical Trials on Ullrich Congenital Muscular Dystrophy
Total 2178 results
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Vanderbilt University Medical CenterAminu Kano Teaching Hospital; Murtala Muhammed Specialist HospitalCompletedStroke | Sickle Cell Disease | Sickle Cell AnemiaNigeria
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CerecareCompletedEds, Unspecified TypeFrance
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Disease | Pulmonary HypertensionUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AFrance, United States, Denmark, Netherlands, Sweden, Spain, Germany, Switzerland, Taiwan, Japan, United Kingdom, Croatia, Italy, Malaysia, Brazil, Australia, Hungary, Israel, Turkey, Puerto Rico, Norway, Korea, Republic of, Bulgaria, Russian...
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AChina
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National Heart, Lung, and Blood Institute (NHLBI)MallinckrodtCompletedSickle Cell Anemia | Pulmonary HypertensionUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoTerminatedSickle Cell Disease | Pulmonary HypertensionUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Spain, Germany, Switzerland, Serbia, Taiwan, United Kingdom, Croatia, Italy, Malaysia, Brazil, Japan, Denmark, Hungary, Israel, Turkey, Russian Federation, Former Serbia and Montenegro
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National Heart, Lung, and Blood Institute (NHLBI)TerminatedSickle Cell Disease | Pulmonary HypertensionUnited States, United Kingdom
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ActelionTerminatedPulmonary HypertensionUnited States, France, United Kingdom, Netherlands
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ActelionNational Heart, Lung, and Blood Institute (NHLBI)TerminatedSickle Cell Anemia | Pulmonary HypertensionUnited States, Netherlands, United Kingdom
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Federal University of São PauloCompletedSickle Cell Anemia | Pulmonary Hypertension
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Institut National de la Santé Et de la Recherche...Recruiting
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Taipei Tzu Chi Hospital, Buddhist Tzu Chi Medical...RecruitingMetabolic Syndrome | Sarcopenia | Prader-Willi SyndromeTaiwan
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University Hospital TuebingenRecruitingHereditary Spastic Paraplegia | Hereditary, Spastic Paraplegia, Autosomal DominantGermany
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University Hospital, BrestCompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)France
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Medical University of ViennaUnknownPolycystic Kidney, Type 1 Autosomal Dominant Disease | Polycystic Kidney, Type 2 Autosomal Dominant DiseaseAustria
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Flex Pharma, Inc.TerminatedCharcot-Marie-Tooth DiseaseUnited States
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Mario Negri Institute for Pharmacological ResearchCompletedAutosomal Dominant Polycystic Kidney DiseaseItaly
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Mayo ClinicPolycystic Kidney Disease FoundationCompletedKidney, Polycystic, Autosomal DominantUnited States
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The Rogosin InstituteWeill Medical College of Cornell University; New York Presbyterian HospitalWithdrawnAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Inozyme PharmaIQVIA BiotechActive, not recruitingPseudoxanthoma Elasticum | Generalized Arterial Calcification of Infancy | ATP-Binding Cassette Subfamily C Member 6 DeficiencyUnited States, United Kingdom
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Barau Dikko Teaching HospitalRecruitingStroke | Sickle Cell DiseaseNigeria
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Spain, Australia, France, Thailand, Italy, Malaysia, Austria, Greece, Japan, Taiwan, Canada, Israel, Algeria, Argentina, Bulgaria, Germany, Romania
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State University of New York at BuffaloSuspendedCognitive Impairment | Cardiovascular Abnormalities | Spinal Cord Injuries | Cerebrovascular Disease; SequelaeUnited States
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Vanderbilt University Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes... and other collaboratorsCompletedStroke | Sickle Cell Disease | Sickle Cell AnemiaNigeria
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University College, LondonUniversity College London HospitalsUnknown
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National Heart, Lung, and Blood Institute (NHLBI)Withdrawn
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Netherlands, Austria, Spain, Germany, Macedonia, The Former Yugoslav Republic of, Taiwan, United Kingdom, Italy, Malaysia, Thailand, France, Greece, Turkey, Japan, South Africa, Romania
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National Institutes of Health Clinical Center (CC)Completed
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Sweden, Spain, Germany, United Kingdom, Denmark, France, Japan
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI)TerminatedPulmonary HypertensionUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia B | HaemostasisUnited States
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Duke UniversityCompletedSickle Cell DiseaseUnited States
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University of North Carolina, Chapel HillDuke UniversityWithdrawnSickle Cell Disease | Pulmonary Hypertension
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Namita SoodCompletedSickle Cell Anemia | Pulmonary HypertensionUnited States
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Assistance Publique - Hôpitaux de ParisUnknownSickle Cell DiseaseFrance
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University of Colorado, DenverUniversity of MarylandRecruitingPolycystic Kidney, Autosomal DominantUnited States
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Dufresne, Craig, MD, PCRecruitingFreeman-Sheldon Syndrome | Whistling Face Syndrome | Freeman-Sheldon Syndrome Variant | Sheldon-Hall Syndrome | Gordon Syndrome | Arthrogryposis Distal Type 3 | Arthrogryposis Distal Type 1 | Freeman-Burian SyndromeUnited States
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Taipei Tzu Chi Hospital, Buddhist Tzu Chi Medical...CompletedBody Weight Changes | Sarcopenia | Prader Labhart Willi SyndromeTaiwan
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Regional Hospital HolstebroCompletedChronic Kidney Diseases | Polycystic Kidney, Autosomal DominantDenmark
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University of ChicagoWithdrawn
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University of Colorado, DenverNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedPolycystic Kidney, Autosomal DominantUnited States
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Mayo ClinicCompletedKidney Disease | Autosomal Dominant Polycystic Kidney DiseaseUnited States
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Otsuka Pharmaceutical Development & Commercialization...Otsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States, Argentina, Australia, Belgium, Brazil, Canada, Czech Republic, France, Germany, Italy, Japan, Netherlands, Norway, Poland, Romania, Spain, Sweden, Switzerland, Turkey, United Kingdom
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Mario Negri Institute for Pharmacological ResearchTerminatedSirolimus In Autosomal Dominant Polycystic Kidney Disease And Severe Renal Insufficiency (SIRENA-II)Autosomal Dominant Polycystic Kidney Disease (ADPKD)Italy
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Glostrup University Hospital, CopenhagenUnknownOptic Atrophy, Autosomal DominantDenmark
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Cure HHTUniversity of Colorado, Denver; Massachusetts General Hospital; Mayo Clinic; Children... and other collaboratorsRecruitingArteriovenous Malformations | Epistaxis | Hereditary Hemorrhagic Telangiectasia | GastroIntestinal Bleeding | Telangiectasia | Vascular Malformation | Cerebral Arteriovenous MalformationsUnited States
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Imperial College LondonRecruitingChronic Kidney Diseases | Renal Failure | End Stage Renal DiseasesUnited Kingdom
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Terumo Medical CorporationCompletedBenign Prostatic Hyperplasia | Arteriovenous Malformations | Uterine Fibroid | Hypervascular TumorsUnited States