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Clinical Trials on Unilineage Bone Marrow Failure Disorders in United Kingdom
Total 4739 results
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingModerate Aplastic Anemia | Unilineage Bone Marrow Failure DisordersUnited States
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Elixirgen Therapeutics, Inc.Not yet recruiting
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King's College Hospital NHS TrustRecruiting
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Cellenkos, Inc.Active, not recruitingBone Marrow DiseaseUnited States
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St. Jude Children's Research HospitalActive, not recruitingAplastic Anemia | Bone Marrow Failure SyndromeUnited States
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National Cancer Institute (NCI)RecruitingInherited Bone Marrow Failure Syndrome | Familial Platelet Disorder With Predisposition to Myeloid MalignanciesUnited States
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Children's Hospital of PhiladelphiaAvailableLeukemia | Immunodeficiencies | Bone Marrow Failure SyndromeUnited States
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Elixirgen Therapeutics, Inc.RecruitingBone Marrow Failure | Telomere ShorteningUnited States
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Henry Ford Health SystemCompletedHematologic Disorders and Bone Marrow Failure, Hematopoietic Stem Cell Transplantation (HSCT) or Cellular Therapy (CART)United States
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Johns Hopkins All Children's HospitalRecruitingSevere Aplastic Anemia | Bone Marrow Failure Syndrome | Hemoglobinopathy (Disorder)United States
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Emory UniversityTerminated
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Medical College of WisconsinChildren's Hospital of PhiladelphiaCompletedMalignant Diseases (ie, Leukemia, MDS, Lymphoma) | Non-malignant Diseases (ie, Bone Marrow Failure Syndromes)United States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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King's College Hospital NHS TrustCompletedMyelodysplastic Syndromes | Leukemia, Myeloid, Acute | Bone Marrow Transplantation | Aplastic AnemiaUnited Kingdom
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Columbia UniversityTerminatedLymphoma | Leukemia | Histiocytosis | Bone Marrow Failure Syndromes | ImmunodeficienciesUnited States
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European Society for Blood and Marrow TransplantationGenzyme, a Sanofi CompanyCompletedAplastic AnemiaSwitzerland, United Kingdom, Germany, Italy, France, Saudi Arabia
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Children's Hospital of PhiladelphiaCompletedBone Marrow Failure Syndromes | Immunodeficiencies | Immune Dysregulation SyndromesUnited States
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University of California, San FranciscoTerminatedMyeloid Malignancy | Metabolic Disease | Bone Marrow Failure Syndrome | Transfusion-dependent Red Blood Cell (RBC) Defect | Congenital Immunodeficiency | Severe Immune DysregulationUnited States
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Sidney Kimmel Comprehensive Cancer Center at Johns...CompletedAplastic Anemia | Immunosuppression | Severe Aplastic Anemia | Bone Marrow FailureUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic Anemia | Telomere Biology Disorders | Inherited Bone Marrow Failure SyndromesUnited States
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Franziska WachterHarvard Clinical and Translational Science Center (Harvard Catalyst)RecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | MDS | Aml | Myeloid Neoplasm | Myeloid Malignancies | Inherited Bone Marrow Failure SyndromeUnited States
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Bellicum PharmaceuticalsTerminatedHemoglobinopathies | Hemophagocytic Lymphohistiocytosis | Metabolic Disorders | Primary Immune Deficiency Disorders | Inherited Bone Marrow Failure SyndromeUnited States
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Children's Hospital of PhiladelphiaRecruiting
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European Society for Blood and Marrow TransplantationNovartis; PfizerCompletedSevere Aplastic AnemiaSwitzerland, Netherlands, France, Italy, Spain, United Kingdom
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic Anemia | Single Lineage Cytopenias, T-LGL | Hypoplastic MDSUnited States
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Mitchell Horwitz, MDGenzyme, a Sanofi CompanyCompletedFailure of Bone Marrow GraftUnited States
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Sidney Kimmel Comprehensive Cancer Center at Johns...CompletedBone Marrow Failure Syndromes | Severe Aplastic AnemiaUnited States
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University College, LondonBloodwiseCompletedHodgkin's Lymphoma | Non-Hodgkin's Lymphoma | Myelodysplastic Syndrome | Acute Myeloid Leukaemia | Chronic Lymphocytic Leukaemia | Acute Lymphoblastic Leukaemia | Chronic Myeloid Leukaemia | Acquired Bone Marrow Failure Syndromes | Other Haematological Malignancies; Unrelated HSCT IndicatedUnited Kingdom
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Emory UniversityWithdrawnHematopoietic and Lymphoid Cell Neoplasm | Leukemia | Anemia | Myelodysplastic Syndrome | Aplastic Anemia | Bone Marrow FailureUnited States
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Novartis PharmaceuticalsActive, not recruitingAplastic AnemiaThailand, Russian Federation, Portugal, United Kingdom, Hong Kong, United States
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Memorial Sloan Kettering Cancer CenterRecruitingAplastic Anemia | Cytopenia | Hypocellular MarrowUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAplastic AnemiaUnited States
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The Cleveland ClinicAstellas Pharma US, Inc.Terminated
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Mayo ClinicCompletedAnemia, AplasticUnited States
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...TerminatedAplastic AnemiaUnited States
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St. Jude Children's Research HospitalCompleted
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M.D. Anderson Cancer CenterTerminatedLeukemia | Aplastic Anemia | Non Hodgkin's LymphomaUnited States
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The Cleveland ClinicCompletedAplastic AnemiaUnited States
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M.D. Anderson Cancer CenterCompletedAplastic AnemiaUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)Terminated
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Fred Hutchinson Cancer CenterUniversity of California, Los Angeles; Oregon Health and Science University; Ohio... and other collaboratorsCompletedAnemia, AplasticUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAplastic AnemiaUnited States
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Mayo ClinicRecruitingHematologic Neoplasms | Myeloid Malignancy | Cytopenia | Bone Marrow Failure Syndrome | Clonal Cytopenia of Undetermined Significance | Clonal Hematopoiesis of Indeterminate Potential | Low Risk Myelodysplastic Syndrome | Inherited Bone Marrow Failure Syndrome | Clonal Expansion | Hereditary Neoplastic... and other conditionsUnited States
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European Society for Blood and Marrow TransplantationCHUGAI sanofi-aventisTerminatedAplastic AnaemiaFrance, Netherlands, Germany, United Kingdom, Switzerland, Italy, Sweden, Greece, Czechia
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UCSF Benioff Children's Hospital OaklandNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Medical... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited Kingdom, United States, Germany
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknown
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Inherited Bone Marrow Failure SyndromeUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingMDS (Myelodysplastic Syndrome) | Severe Aplastic AnemiaUnited States
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National Institute of Environmental Health Sciences...Completed