- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Usability
Total 1731 results
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ShireCompletedMucopolysaccharidosis IIUnited States, United Kingdom, Brazil, Germany
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AO GENERIUMCompletedA Multi-cohort Study of the Tolerance, Safety, and Pharmacokinetics of GNR-055 in Healthy VolunteersMetabolic Diseases | Mucopolysaccharidosis Type IIRussian Federation
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Hacettepe UniversityCompletedChewing Problem | Swallowing DisorderTurkey
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Hospices Civils de LyonUnknownWilliams-Beuren Syndrome | Micro-duplication 7q11.23 Syndrome | VasculopathyFrance
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University Hospital, ToursCompletedHealthy Volunteers | Autism | Fragile-X Syndrome (FXS)France
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GlaxoSmithKlineCompletedMucopolysaccharidosis IIJapan
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Green Cross CorporationUnknownMucopolysaccharidosis II
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National Institute of Mental Health (NIMH)CompletedSchizophrenia | Bipolar Disorder | Attention Deficit Disorder With Hyperactivity | Mental Retardation | Mental Disorder Diagnosed in ChildhoodUnited States
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National Center for Research Resources (NCRR)University of California, San DiegoCompleted
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Uskudar UniversityRecruitingLesch-Nyhan SyndromeTurkey
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National Hospital Organization Nagoya Medical CenterRecruitingAcute Lymphoblastic Leukemia | Down Syndrome | Childhood CancerTaiwan, Thailand, Hong Kong, Singapore, Malaysia, Japan
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Eunice Kennedy Shriver National Institute of Child...RecruitingAutism Spectrum Disorder | Fragile X Syndrome | Developmental Delay | Genetic Disorder | Asperger DisorderUnited States
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ShireCompletedHunter SyndromeUnited States, Spain, Canada, United Kingdom, Mexico, Australia, France
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Green Cross CorporationCompleted
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University of California, San FranciscoNational Human Genome Research Institute (NHGRI)CompletedEpilepsy | Cerebral Palsy | Intellectual Disability | Developmental Delay | Metabolic Disease | Neuro-Degenerative Disease | Encephalopathy | Birth Defect | Multiple Congenital Anomaly | Developmental DefectUnited States
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Lundquist Institute for Biomedical Innovation at...Active, not recruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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Universidad Industrial de SantanderUniversity of North Carolina, Chapel HillCompletedMicrocephaly | Mental RetardationColombia
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University of South FloridaUniversity of California, Los Angeles; Temple UniversityCompletedGeneralized Anxiety Disorder | Social Phobia | Separation Anxiety Disorder | Specific Phobia | Autism | Autism Spectrum Disorders | Obsessive-compulsive Disorder | Asperger's Syndrome | Pervasive Developmental Disability - Not Otherwise SpecifiedUnited States
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ShireCompleted
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Institut Jerome LejeuneFondation Jérôme LejeuneCompletedObstructive Sleep Apnea Syndrome | Down SyndromeFrance
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Green Cross CorporationUnknownThe Long-term Safety Study of Idursulfase-beta in Hunter Syndrome(Mucopolysaccharidosis II) PatientsHunter SyndromeKorea, Republic of
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TakedaRecruiting
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Children's Hospital of Eastern OntarioThe Physicians' Services Incorporated FoundationRecruitingChild | Obstructive Sleep Apnea | Down SyndromeCanada
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National Cancer Institute (NCI)SuspendedDown Syndrome | Recurrent B Acute Lymphoblastic LeukemiaUnited States, Canada, Puerto Rico, Australia
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TakedaAvailableHunter SyndromeUnited States, Australia, Mexico, Spain, United Kingdom
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Institut Jerome LejeuneHôpital Necker-Enfants MaladesActive, not recruitingDown Syndrome | Obstructive Sleep Apnea of NewbornFrance
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TakedaCompletedMucopolysaccharidosis (MPS)Brazil
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Vancouver General HospitalNovo Nordisk A/STerminated
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Green Cross CorporationCompleted
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Maimonides Medical CenterFoundation for Prader-Willi ResearchRecruitingBody Weight | Hyperphagia | Prader-Willi Syndrome | Mood | Behavior | Excessive Daytime SleepinessUnited States
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Maimonides Medical CenterRecruitingAggression | Behavioral Symptoms | Pathologic Processes | Nervous System Diseases | Obesity | Neurologic Manifestations | Neurobehavioral Manifestations | Congenital Abnormalities | Overnutrition | Nutrition Disorders | Genetic Diseases, Inborn | Intellectual Disability | Self-Injurious Behavior | Abnormalities, Multiple and other conditionsUnited States
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Duke UniversityRecruiting
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University of AlbertaSt. Justine's HospitalRecruitingNeurobehavioral Manifestations | Genetic Diseases, X-Linked | Mental Retardation, X-Linked | Intellectual Disability | Fragile X Syndrome | Sex Chromosome Disorders | Fragile X Mental Retardation Syndrome | Trinucleotide Repeat Expansion | Fra(X) Syndrome | FXSCanada
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingCardiovascular Disease | Williams Syndrome | Supravalvular Aortic StenosisUnited States
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Oregon Health and Science UniversityActive, not recruitingObstructive Sleep Apnea of ChildUnited States
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ShireCompletedHunter SyndromeUnited States, United Kingdom
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Diskapi Yildirim Beyazit Education and Research...UnknownCerebral Palsy | Covid19 | Telemedicine | Disability, Developmental | Caregiver Quality of LifeTurkey
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Stanford UniversityTerminatedFragile X Syndrome (FXS) | Idiopathic Intellectual Developmental Disorder (IDD)United States
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Bambino Gesù Hospital and Research InstituteAutour Des Williams; AceaUnknownFragile X Syndrome | Williams SyndromeItaly
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National Taiwan University HospitalUnknownRett Syndrome | Tourette Syndrome | Tic DisordersTaiwan
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Universidad de GuanajuatoCompletedDown Syndrome | Metabolic Syndrome XMexico
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Myelodysplastic/Myeloproliferative NeoplasmsUnited States, Canada, Puerto Rico, Australia, Netherlands, New Zealand, Switzerland
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Children's Health IrelandBelfast Health and Social Care Trust; University of Edinburgh; University Hospital... and other collaboratorsRecruitingQuality of Life | Obstructive Sleep Apnea | Down Syndrome | Behavior | Adherence, TreatmentUnited Kingdom, Ireland
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TakedaTakeda Development Center Americas, Inc.RecruitingHunter Syndrome | Mucopolysaccharidosis (MPS)United States
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ShireCompletedHunter SyndromeUnited Kingdom, United States, Brazil
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Hospices Civils de LyonCompletedAutism Spectrum Disorder | Williams Beuren Syndrome
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Sanko UniversityCompletedCerebral Palsy | Muscular Dystrophy | Down Syndrome | Parents | Spina BifidaTurkey
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Pharnext SACompletedCharcot-Marie-Tooth Disease | Hereditary Neuropathy With Liability to Pressure Palsies | Genetic DisordersFrance
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Children's Hospital of PhiladelphiaCompletedObstructive Sleep Apnea Syndrome | Down SyndromeUnited States