- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Veteran Families in United Kingdom
Total 620 results
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Inozyme PharmaEngage Health Inc.; GACI GlobalCompletedGeneralized Arterial Calcification in Infancy | Autosomal Recessive Hypophosphatemic Rickets Type 2United States
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Kyowa Hakko Kirin Pharma, Inc.Completed
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Acceleron Pharma, Inc., a wholly-owned subsidiary...Active, not recruitingPulmonary Arterial HypertensionFrance, Germany, United States, Australia, Belgium, Canada, Israel, Italy, Mexico, Netherlands, Spain, United Kingdom
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PfizerTerminatedPulmonary Arterial HypertensionUnited States, Netherlands, Canada, Belgium, France, Germany, Italy, Spain, United Kingdom, Australia, Poland, Austria, Brazil, Israel, Argentina, Mexico
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Lung Biotechnology PBCCompletedPulmonary Arterial HypertensionUnited States, Belgium, Ireland
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West Penn Allegheny Health SystemJohns Hopkins University; University of Colorado, Denver; Massachusetts General... and other collaboratorsWithdrawnPulmonary Arterial Hypertension | Pulmonary Hypertension | PAH WHO Group IUnited States
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Megan BallingerCompleted
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Sidney Kimmel Comprehensive Cancer Center at Johns...ChiRhoClin, Inc.; The V Foundation for Cancer ResearchCompletedEarly Pancreatic Neoplasia | Familial Pancreatic NeoplasiaUnited States
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Aires Pharmaceuticals, Inc.CompletedPulmonary Arterial Hypertension | Pulmonary HypertensionUnited States
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ActelionWithdrawnPulmonary Arterial HypertensionUnited States
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Kawut, Steven, MDNational Heart, Lung, and Blood Institute (NHLBI); Columbia UniversityCompletedHypertension, PulmonaryUnited States
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Aerovate TherapeuticsRecruitingPulmonary Arterial HypertensionUnited States, Belgium, Italy, Spain, Australia, Canada, China, Singapore, France, United Kingdom, Latvia, Mexico, Argentina, Israel, South Africa, Chile, Poland, Germany, Portugal, Colombia
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The Familial Hypercholesterolemia FoundationRecruitingHypercholesterolemiaUnited States
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University of PennsylvaniaLancaster General Hospital; The Familial Hypercholesterolemia FoundationCompleted
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National Institute of Dental and Craniofacial Research...RecruitingOsteomalacia | Tumor Induced Osteomalcia | Familial Tumoral CalcinosisUnited States
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In His ImageKos PharmaceuticalsCompletedDyslipidemia | Hyperlipidemia | Mixed HyperlipidemiaUnited States
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V-Wave LtdRecruitingPulmonary Arterial HypertensionUnited States, Canada, Mexico
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Boston Children's HospitalWellth Inc.; MMAS-8 with permission from Dr Donald Morisky. as written belowRecruitingAdherence, Medication | Familial HypercholesterolemiaUnited States
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Children's Mercy Hospital Kansas CityCompletedHypophosphatemic Rickets, X-Linked DominantUnited States
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University of PennsylvaniaRegeneron PharmaceuticalsCompleted
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Redwood Dermatology SciencesUltragenyx Pharmaceutical IncCompletedPain, Chronic | Hypophosphatemia | Hypophosphatemic RicketsUnited States
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Indiana UniversityCompletedAutosomal Dominant Hypophosphatemic RicketsUnited States
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Eidos Therapeutics, a BridgeBio companyCompletedFamilial ATTR-CM (ATTRm-CM, or FAC) | Wild-type ATTR-CM (ATTRwt-CM)United States
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedHypophosphatemic Rickets, X Linked DominantUnited States
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Idorsia Pharmaceuticals Ltd.TerminatedPulmonary Arterial HypertensionUnited States, France, Switzerland
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Allegheny Singer Research Institute (also known...CompletedPulmonary Arterial HypertensionUnited States
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United TherapeuticsTerminatedCardiovascular Diseases | Vascular Diseases | Lung Diseases | Hypertension | Pulmonary Arterial Hypertension | Familial Primary Pulmonary Hypertension | Hypertension, Pulmonary | Pulmonary Hypertension | PAH | Respiratory Tract Disease | Connective Tissue DiseaseSpain, United States, Australia, Canada, United Kingdom, Italy, Argentina, Austria, Belgium, Brazil, Germany, Poland
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Kyowa Kirin Pharmaceutical Development LtdActive, not recruitingX-Linked HypophosphatemiaSpain, Italy, United Kingdom, France, Belgium, Denmark, Germany, Hungary, Portugal, Norway, Switzerland, Israel, Netherlands, Czechia, Bulgaria, Sweden, Slovenia, Ireland, Latvia, Slovakia
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ActelionCompletedPulmonary Arterial HypertensionUnited States
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Geno LLCWithdrawnPulmonary Arterial HypertensionUnited States
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Bellus Health IncNational Institute of Neurological Disorders and Stroke (NINDS)CompletedStroke | Neurologic Diseases, GeneralUnited States
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PfizerTerminatedPulmonary Arterial Hypertension | Pulmonary HypertensionUnited States, Romania, Ukraine
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BayerCompletedPulmonary Arterial HypertensionBelgium, France, Spain, Portugal, Turkey, United States, Germany, Korea, Republic of, Mexico, Austria, Canada, Denmark, Poland, Italy, Greece, Taiwan, Czechia, Netherlands, Japan, Brazil, United Kingdom
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ActelionCompletedPulmonary Arterial HypertensionUnited States
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolemiaUnited States, Austria, Canada, Czech Republic, Denmark, France, Israel, Netherlands, Norway, Russian Federation, South Africa, Spain, Sweden, United Kingdom
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American Medical Association FoundationWithdrawnIdiopathic Pulmonary Arterial Hypertension.United States
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Yale UniversityCompleted
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedHyperparathyroidism | Hypophosphatemia, FamilialUnited States
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United TherapeuticsTerminatedPulmonary Arterial HypertensionUnited States
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Kyowa Hakko Kirin Pharma, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Canada
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United TherapeuticsCompletedPulmonary Arterial HypertensionUnited States
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ActelionCompletedPulmonary Arterial HypertensionUnited States, Germany
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Essentia HealthSt. Luke's Hospital of Duluth; WHITESIDE Institute for Clinical ResearchRecruitingFamilial Hypercholesterolemia | Genetic Disease | Cholesterol, ElevatedUnited States
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University of South FloridaWithdrawnPulmonary Arterial Hypertension | Familial Primary Pulmonary Hypertension | Idiopathic Pulmonary Arterial Hypertension | Primary Pulmonary HypertensionUnited States
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Merck Sharp & Dohme LLCCompletedHypercholesterolemia | Familial HypercholesterolemiaUnited States, Germany, Japan, Korea, Republic of, Mexico, Norway, Turkey, United Kingdom
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GB002, Inc.Not yet recruitingPulmonary Arterial HypertensionUnited States
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National Institutes of Health Clinical Center (CC)CompletedSecondary Pulmonary Arterial HypertensionUnited States
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Pfizer's Upjohn has merged with Mylan to form Viatris...CompletedPulmonary Hypertension, Familial Persistent, of the NewbornUnited States, Belgium, United Kingdom, Spain, Denmark, Germany, Sweden, Canada, France, Italy, Netherlands, Norway
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Canada, Brazil, Taiwan, Singapore, South Africa, United Kingdom
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Medical Research Laboratories InternationalTerminatedFamilial HypercholesterolemiaNetherlands, United States, Norway