- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Vitelliform Macular Dystrophy
Total 52448 results
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GlaxoSmithKlineCompletedMuscular DystrophiesFrance, Denmark, Germany, Belgium, Spain, Turkey, Korea, Republic of, Brazil, Netherlands, Italy, Chile, Japan, Canada, Hungary, Russian Federation, Czechia, Poland, Norway, Argentina, Taiwan
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Cedars-Sinai Medical CenterCompleted
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University of MinnesotaFairview Health ServicesWithdrawnDuchenne Muscular Dystrophy
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PTC TherapeuticsParexel; Dohmen Life Science ServicesApproved for marketingDuchenne Muscular DystrophyUnited States
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University of FloridaUnited States Department of DefenseCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyBelgium, Netherlands, Italy, Sweden
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Jerry R. MendellEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDuchenne Muscular DystrophyUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical CenterCompletedDuchenne Muscular DystrophyUnited States
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University of GaziantepIstınye University, Cukurova University, Yıldırım Beyazıt University, Gaziantep...UnknownDuchenne Muscular DystrophyTurkey
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GlaxoSmithKlineWithdrawnMuscular Dystrophies
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedDuchenne Muscular DystrophyCanada
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Shenzhen Beike Bio-Technology Co., Ltd.The Second Affiliated Hospital of Kunming Medical UniversityUnknownDuchenne Muscular DystrophyChina
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Nationwide Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...CompletedDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...Completed
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Cooperative International Neuromuscular Research...Completed
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Sarepta Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Red Nucleus Enterprise Solutions, LLCRecruiting
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Egyptian Chinese UniversityBenha UniversityRecruitingDuchenne Muscular DystrophyEgypt
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ItalfarmacoRecruitingDuchenne Muscular DystrophyCanada, Italy, France, Belgium, Germany, Netherlands, United Kingdom
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Sarepta Therapeutics, Inc.Hoffmann-La RocheRecruitingDuchenne Muscular DystrophyUnited States, Japan, Spain, Italy
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Virginia Commonwealth UniversityNorthwestern University; University of RochesterRecruitingDuchenne Muscular DystrophyUnited States
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University of FloridaRecruiting
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Santhera PharmaceuticalsSanthera PharmaceuticalsActive, not recruitingDuchenne Muscular DystrophyCanada
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Sarepta Therapeutics, Inc.Active, not recruitingMuscular Dystrophy, DuchenneUnited States, Korea, Republic of, India, Slovenia, Turkey, United Kingdom, Germany, Switzerland, Spain, Czechia, France, Serbia, Taiwan, Netherlands, Mexico, Colombia, Denmark, New Zealand, Norway, Greece, Hungary, Ireland, Italy, Jo... and more
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Belgium, Korea, Republic of, Taiwan, Canada, Australia, Germany, Japan, France, Italy, United Kingdom, Russian Federation, Israel, Switzerland
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Edgewise Therapeutics, Inc.Medpace, Inc.Enrolling by invitationBecker Muscular DystrophyUnited States, Netherlands
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Sheffield Children's NHS Foundation TrustSheffield Hallam University; National Institute for Health Research, United... and other collaboratorsActive, not recruiting
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyKorea, Republic of, Chile, Japan, China, United Kingdom, Netherlands, Spain, Norway, Russian Federation, Australia, Greece, Italy, New Zealand, Turkey, Mexico, Czechia, Canada
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University College, LondonRadboud University Medical Center; Groupe Hospitalier Pitie-Salpetriere; Leiden... and other collaboratorsCompletedDuchenne Muscular DystrophyNetherlands, France, United Kingdom
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Santhera PharmaceuticalsAvailableDuchenne Muscular DystrophyUnited States, Canada, Israel
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophyKorea, Republic of, Chile, Taiwan, China, United States, United Kingdom, Netherlands, Spain, Australia, Norway, Russian Federation, Greece, Italy, Turkey, Mexico, Canada, Hong Kong, New Zealand, Ukraine
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Hacettepe UniversityCompletedDuchenne Muscular DystrophyTurkey
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.TerminatedMuscular Dystrophy, DuchenneUnited States, Canada
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ReveraGen BioPharma, Inc.University of Pittsburgh; Newcastle University; European Union; Cooperative International...CompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, United Kingdom, Spain, Netherlands, Sweden, Czechia, Australia, Greece, Israel
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Haukeland University HospitalExtrastiftelsenCompleted
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Phrixus Pharmaceuticals, Inc.Charley's FundTerminated
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Acceleron Pharma Inc. (a wholly owned subsidiary...Terminated
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Newcastle... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Germany, Italy
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ItalfarmacoSyneos HealthCompletedDuchenne Muscular DystrophyUnited States, Italy, Spain, Canada, Belgium, France, Germany, Israel, Netherlands, Serbia, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Haukeland University HospitalOslo University Hospital; Norwegian School of Sport SciencesCompletedDuchenne Muscular DystrophyNorway
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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Santhera PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Austria, France, Germany, Italy, Spain, Switzerland
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Charite University, Berlin, GermanyCompletedDuchenne Muscular DystrophyGermany
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Taiho Pharmaceutical Co., Ltd.Completed
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ReveraGen BioPharma, Inc.University of Pittsburgh; Cooperative International Neuromuscular Research...CompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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Rare Disease Research, LLCSarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyUnited States