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Clinical Trials on Vulnerable Families in Austria
Total 119 results
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Austrian Academic Institute for Clinical NutritionMedical University of ViennaCompletedHeterozygous Familial HypercholesterolemiaAustria
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Medical University InnsbruckUnknownFamilial Hypobetalipoproteinaemia - Heterozygous Form | Low-LDL-syndromeAustria
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Regina Steringer-MascherbauerUnknownPulmonary Arterial Hypertension WHO Group IAustria
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The University of Western AustraliaNational Health and Medical Research Council, AustraliaUnknownFamilial Hypercholesterolaemia | HypertriglyceridaemiaAustralia
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Michael FrassCompleted
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Medical University of ViennaUnknown
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Australia, Austria, Netherlands, Taiwan, Ukraine
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Medical University of GrazCompleted
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Medical University of GrazLudwig Boltzmann Institute for Lung Vascular ResearchCompletedIdiopathic Pulmonary Arterial HypertensionAustria
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Orthopedic Hospital Vienna SpeisingCompleted
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Medical University of ViennaUnknown
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Australia, Austria, Canada, France, Greece, Italy, Japan, South Africa, Ukraine
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Arrowhead PharmaceuticalsCompletedHypertriglyceridemia | Familial ChylomicronemiaAustralia, Canada, New Zealand
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Medical University InnsbruckUnknownCardiovascular Diseases | Diabetes Mellitus | Familial Renal GlucosuriaAustria
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Arrowhead PharmaceuticalsActive, not recruitingHomozygous Familial HypercholesterolemiaAustralia, Canada, United States, South Africa
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Medical University of ViennaUnknownType 2 Diabetes Mellitus | Type 1 Diabetes Mellitus | Healthy Volunteers | Prediabetes (Insulin Resistance, Impaired Glucose Tolerance) | Familiar Hypocalcuric HypercalcemiaAustria
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AOP Orphan Pharmaceuticals AGNot yet recruitingPulmonary Arterial HypertensionSpain, Austria, France, Hungary
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa, Australia, Austria, Canada, Czechia, France, Greece, Italy, Japan, Ukraine
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PfizerCompletedTransthyretin Amyloidosis Cardiomyopathy (ATTR-CM)Italy, Romania, France, Australia, Austria, Portugal, Slovakia, Slovenia, Spain, United Kingdom
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CENTOGENE GmbH RostockAlnylam PharmaceuticalsRecruitingCardiomyopathies | Polyneuropathies | Transthyretin Amyloidosis | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid PolyneuropathyGermany, Austria, Switzerland
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United TherapeuticsTerminatedPulmonary Arterial HypertensionAustralia
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Arrowhead PharmaceuticalsActive, not recruitingFamilial ChylomicronemiaKorea, Republic of, Canada, Australia, Singapore, Belgium, Spain, Japan, United States, Austria, Germany, Ireland, Oman, Poland, Israel, New Zealand, Argentina, France, Croatia, Mexico, Serbia, Turkey
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Mirum Pharmaceuticals, Inc.Active, not recruitingProgressive Familial Intrahepatic Cholestasis (PFIC)United States, Argentina, France, Singapore, United Kingdom, Belgium, Turkey, Austria, Brazil, Canada, Colombia, Germany, Italy, Lebanon, Mexico, Poland
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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ActelionCompletedPulmonary Arterial HypertensionUnited Kingdom, Austria, Belgium, France, Germany, Hungary, Italy, Poland
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BayerCompletedPulmonary Arterial HypertensionGermany, Austria
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Mirum Pharmaceuticals, Inc.CompletedProgressive Familial Intrahepatic Cholestasis (PFIC)Italy, United States, Argentina, France, Singapore, United Kingdom, Austria, Brazil, Mexico, Lebanon, Germany, Turkey, Poland, Belgium, Canada, Colombia, Hungary
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Bial - Portela C S.A.CompletedPulmonary Arterial HypertensionAustria, Germany, Italy, Portugal, Spain, United Kingdom
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Arrowhead PharmaceuticalsCompletedDyslipidemias | Hypertriglyceridemia | Familial HypercholesterolemiaAustralia, New Zealand
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-linked Hypophosphatemia (XLH)Sweden, Spain, United Kingdom, Italy, Austria, France
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Respira Therapeutics, Inc.CompletedPulmonary Arterial HypertensionAustralia
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Novartis PharmaceuticalsCompletedPulmonary Arterial HypertensionAustria, Germany, United States, United Kingdom
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Regeneron PharmaceuticalsSanofiCompletedHomozygous Familial HypercholesterolemiaUnited States, South Africa, Canada, Greece, Japan, Ukraine, Austria, Czechia, France, Germany, Italy, Taiwan, Turkey
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ActelionCompletedPulmonary Arterial HypertensionCanada, United Kingdom, Italy, United States, Netherlands, Australia, Austria, Belgium, France, Germany, Spain
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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ActelionCompletedPulmonary Arterial Hypertension Related to Eisenmenger PhysiologyCanada, United Kingdom, Italy, United States, Netherlands, Australia, Austria, Belgium, France, Germany, Spain
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AmgenCompletedHeterozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Norway, Belgium, Turkey, Australia, New Zealand, Austria, Czechia, South Africa, Poland, Spain, Switzerland, Netherlands, Taiwan, Finland, Brazil, Portugal, Slovenia, Russian Federation, Hungary, United... and more
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AmgenCompletedSevere Familial HypercholesterolemiaItaly, Czechia, United States, Israel, New Zealand, South Africa, France, Spain, Australia, Belgium, Canada, Netherlands, Hong Kong, Brazil, United Kingdom, Greece, Japan, Lebanon
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Bristol-Myers SquibbTerminatedPrimary Familial Dilated CardiomyopathyUnited States, Germany, Spain, United Kingdom
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AOP Orphan Pharmaceuticals AGEnrolling by invitationPulmonary Arterial HypertensionFrance, Spain, Germany, Italy, Hungary, Austria, Czechia, Poland, Romania
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Heidelberg UniversityMerck Sharp & Dohme LLCRecruitingSystemic Sclerosis | Pulmonary Vascular Disorder | Primary Pulmonary Hypertension | Other Systemic Involvement of Connective TissueAustria, Germany, Italy, France, Switzerland
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AOP Orphan Pharmaceuticals AGGCP-Service International Ltd. & Co. KG; ANOVA CRO s.r.o.; PharmaLex Belgium; Aixial...RecruitingPulmonary Arterial HypertensionAustria, Spain, France, Germany, Italy, Czechia, Hungary, Poland, Portugal, Romania
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Gilead SciencesTerminatedPulmonary Arterial HypertensionUnited States, Israel, Australia, Canada, Mexico, Spain, Belgium, Austria, Germany, United Kingdom
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Novartis PharmaceuticalsCompletedElevated Cholesterol | Homozygous Familial Hypercholesterolemia | Heterozygous Familial Hypercholesterolemia | ASCVDUnited States, Canada, Czechia, Denmark, Germany, Hungary, Netherlands, Poland, South Africa, Spain, Sweden, Ukraine, United Kingdom
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Novartis PharmaceuticalsTerminatedPulmonary Arterial HypertensionGermany, Belgium, United Kingdom, United States, Lithuania, Italy, Australia
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Poland, Argentina, Australia, Belgium, France, Germany, Japan, Netherlands, Portugal, Spain, Sweden, United Kingdom, Canada, Czechia, Denmark, Hungary, Ireland, Norway, Korea, Republic of, Austria, Croatia, Israel, Latvia, Lithuan... and more
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Novartis PharmaceuticalsCompletedPulmonary Arterial HypertensionGermany, Belgium, United States, Lithuania, United Kingdom, Italy, Australia
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Kastle Therapeutics, LLCCompletedHypercholesterolemia | Heterozygous FamilialUnited States, Italy, Poland, Ukraine, United Kingdom, Germany, Hong Kong, Taiwan, Spain, Argentina, Belgium, Israel, Malaysia, South Africa, Turkey, Netherlands, Korea, Republic of, Canada, New Zealand, Russian Federation, Brazil, Austral... and more
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Amryt PharmaRecruitingHomozygous Familial HypercholesterolemiaItaly, United States, Argentina, Canada, France, Greece, Netherlands, United Kingdom
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ActelionCompletedPulmonary Arterial HypertensionUnited States, Spain, Denmark, Canada, Germany, United Kingdom, Belgium, Austria, Netherlands, Australia, France, Ireland, Sweden, Italy, Switzerland