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Clinical Trials on X-linked Adrenoleukodystrophy in United Kingdom
Total 1264 results
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Children's Hospital Medical Center, CincinnatiRush University Medical CenterCompleted
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Great Ormond Street Hospital for Children NHS Foundation...National Institute for Health Research, United Kingdom; The Freya FoundationRecruitingPyruvate Dehydrogenase Complex Deficiency | Pyruvate Dehydrogenase E1 Alpha Deficiency | Pyruvate Dehydrogenase E1-Beta Deficiency | Pyruvate Dehydrogenase E2 Deficiency | Pyruvate Dehydrogenase Phosphatase DeficiencyUnited Kingdom
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Massachusetts General HospitalNational Institutes of Health (NIH)UnknownHealthy | Fragile X SyndromeUnited States
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Rett Syndrome Research TrustNot yet recruitingRett SyndromeUnited States
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Craig EricksonHealx LimitedRecruitingFragile X SyndromeUnited States
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Elizabeth Berry-KravisCompletedFragile X SyndromeUnited States
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Janssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, United Kingdom
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Rowan UniversityUniversity of Pennsylvania; FRAXA Research FoundationUnknown
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Denali Therapeutics Inc.CompletedMucopolysaccharidosis IIUnited Kingdom, United States, Netherlands
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BiogenCompletedX-Linked Retinitis PigmentosaUnited States, United Kingdom
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Imperial College LondonSarepta Therapeutics, Inc.; Department of Health, United KingdomCompletedDuchenne Muscular DystrophyUnited Kingdom
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Children's Hospital Medical Center, CincinnatiCompleted
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Randi J. Hagerman, MDCompleted
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Indiana UniversityIndiana Clinical and Translational Sciences InstituteCompleted
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Indiana University School of MedicineCompletedFragile X SyndromeUnited States
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Stanford UniversityNational Institute of Mental Health (NIMH); Autism SpeaksCompleted
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Summit TherapeuticsCompletedModified Diet Trial: A Study of SMT C1100 in Paediatric Patients With DMD Who Follow a Balanced DietMuscular Dystrophy, DuchenneUnited Kingdom
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NeuropharmCompleted
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Spain
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Rett Syndrome Research TrustDuke UniversityCompletedRett SyndromeUnited States
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Montefiore Medical CenterRett Syndrome Research TrustCompleted
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Montefiore Medical CenterRett Syndrome Research TrustCompletedRett SyndromeUnited States
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Edimer PharmaceuticalsCompleted
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Lancashire Teaching Hospitals NHS Foundation TrustDuchenne UKRecruiting
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Sheffield Children's NHS Foundation TrustSheffield Hallam University; National Institute for Health Research, United... and other collaboratorsActive, not recruiting
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GenethonInstitute of MyologyUnknownDuchenne Muscular DystrophyUnited Kingdom, France
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Eunice Kennedy Shriver National Institute of Child...University of WashingtonUnknownWiskott-Aldrich Syndrome | Leukocyte Adhesion Deficiency Syndrome | X-Linked Agammaglobulinemia | X-Linked Hyper IgM SyndromeUnited States
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Stanford UniversityThe John Merck FundCompletedFragile X Syndrome | Disruptive BehaviorUnited States
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Stanford UniversityCompletedDevelopmental Disabilities | Fragile X SyndromeUnited States
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Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
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MeiraGTx UK II LtdSyne Qua Non Limited; Bionical EmasCompletedGene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR)X-Linked Retinitis PigmentosaUnited Kingdom, United States
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Hoffmann-La RocheCompleted
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Seaside Therapeutics, Inc.SuspendedFragile X SyndromeUnited States
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Alcobra Ltd.CompletedFragile X SyndromeUnited States, Israel
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Novo Nordisk A/SEnrolling by invitationHaemophilia BNetherlands, United Kingdom
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ShireCompletedHunter SyndromeUnited Kingdom, United States, Brazil
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Rett Syndrome Research TrustCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...Terminated
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Eunice Kennedy Shriver National Institute of Child...UnknownRett SyndromeUnited States
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Denali Therapeutics Inc.Active, not recruitingMucopolysaccharidosis IIUnited States, Netherlands, Canada, United Kingdom
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Elizabeth Berry-KravisNational Institute of Neurological Disorders and Stroke (NINDS); Novartis PharmaceuticalsCompleted
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Stanford UniversityCompletedIntellectual Disability | Fragile X SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Nova Mentis Life Science CorpFourthWall TestingRecruitingAutism Spectrum Disorder | Fra(X) SyndromeUnited States
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... and other collaboratorsRecruiting
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Edison Pharmaceuticals IncWithdrawn
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)CompletedRett SyndromeUnited States
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Boston Children's HospitalInternational Rett Syndrome FoundationCompleted