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Clinical Trials on X-Linked Hypophosphatemia in United States
Total 1363 results
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Hoffmann-La RocheCompletedFragile X SyndromeFrance, Spain, United States, Peru, Canada, United Kingdom, Chile, Argentina, Mexico, Sweden
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Hugo W. Moser Research Institute at Kennedy Krieger...European Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyUnited States
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS); Vanderbilt...RecruitingRett Syndrome | Rett Syndrome, Atypical | RTTUnited States
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RespireRxFRAXA Research FoundationCompletedFragile X Syndrome | AutismUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, United Kingdom
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Edimer PharmaceuticalsCompletedHypohidrotic Ectodermal Dysplasia | X-Linked Hypohidrotic Ectodermal DysplasiaUnited States
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Edimer PharmaceuticalsNational Foundation of Ectodermal DysplasiaCompletedHypohidrotic Ectodermal Dysplasia | X-Linked Hypohidrotic Ectodermal DysplasiaUnited States
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Hoffmann-La RocheCompleted
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Primary Immune Deficiency Disorders | Hyper-IgM Syndrome | X-linked AgammaglobulinaemiaUnited States, United Kingdom, Hungary
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ProgenaBiomeRecruitingAutism Spectrum Disorder | Autistic Disorder | Autism | Autism, Akinetic | Autism; Atypical | Autism; Psychopathy | Autism Fragile Syndrome X | Autism With High Cognitive Abilities | Autism-Related Speech Delay | Autism, Susceptibility to, 6 | Autism Spectrum Disorder High-Functioning | Autistic Thinking | Autism... and other conditionsUnited States
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Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
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Tetra Discovery PartnersEnrolling by invitationFragile X SyndromeUnited States
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAutism Spectrum Disorder | Autistic Disorder | Fragile X Syndrome | Asperger SyndromeUnited States
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State University of New York - Upstate Medical...TerminatedFamilial Encephalopathy With Neuroserpin Inclusion Bodies | X-linked Mental Retardation | Congenital Vertical Talus | Idiopathic Generalised Epilepsy | Familial DementiaUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingAutism Spectrum Disorder | Fragile X Syndrome | Developmental Delay | Genetic Disorder | Asperger DisorderUnited States
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, France, Canada, Denmark, Indonesia, Italy, Netherlands, Spain, Sweden, Turkey, United Kingdom
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National Institute of Dental and Craniofacial Research...TerminatedOsteomalaciaUnited States
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Neuren Pharmaceuticals LimitedCompleted
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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University of StrathclydeUnknownOsteopenia of Prematurity | HypophosphataemiaUnited Kingdom
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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ACADIA Pharmaceuticals Inc.CompletedRett SyndromeUnited States
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ACADIA Pharmaceuticals Inc.Completed
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Neuren Pharmaceuticals Limitedrettsyndrome.orgCompleted
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National Institute of Allergy and Infectious Diseases...RecruitingGranuloma | Granulomatous Disease, Chronic | Leukocyte Disease | Genetic Disease, X-Linked | Genetic Disease, InbornUnited States
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Edimer PharmaceuticalsCompletedX-Linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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Newron Pharmaceuticals SPATerminatedRett SyndromeUnited States, India, United Kingdom, Australia, Italy
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Duke UniversityFoundation Fighting BlindnessWithdrawnChoroideremiaUnited States
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Rush University Medical CenterEmory UniversityEnrolling by invitationTuberous Sclerosis | Fragile X Syndrome | Rett Syndrome | Hamartoma Syndrome, Multiple | Angelman Syndrome | Creatine Deficiency, X-linked | Telomeric 22Q13 Monosomy Syndrome | Chromosome 15Q, Partial DeletionUnited States
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Jazz PharmaceuticalsGW PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Canada, Italy, Spain, United Kingdom, Australia
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Fairview University Medical CenterTerminatedImmunologic Deficiency Syndromes | Common Variable Immunodeficiency | Severe Combined Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Graft Versus Host Disease | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | Virus-Associated... and other conditionsUnited States
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCDKL5 | Rett Syndrome | MECP2 Duplication | FOXG1 DisordersUnited States
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Rare Thyroid Therapeutics International ABPremier Research Group plc; Egetis TherapeuticsRecruitingMonocarboxylate Transporter 8 Deficiency | Allan-Herndon-Dudley SyndromeUnited States, United Kingdom, Netherlands
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Ultragenyx Pharmaceutical IncTerminatedCreatine Deficiency, X-linkedUnited States, Canada
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome | MECP2 Duplication Disorder | Rett-related DisorderUnited States
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHCompletedRett SyndromeCanada, Australia, United Kingdom
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Jazz PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Spain, Italy, United Kingdom
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University of California, San DiegoRocket Pharmaceuticals Inc.Recruiting
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ACADIA Pharmaceuticals Inc.CompletedRett SyndromeUnited States
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Edimer PharmaceuticalsCompletedX-Linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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Anavex Life Sciences Corp.Completed
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Rare... and other collaboratorsCompletedErythropoietic Protoporphyria | EPP | XLP | X-Linked Protoporphyria | XLPP | X-Linked Dominant Erythropoietic Protoporphyria | XLEPP | XLDPUnited States
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Eunice Kennedy Shriver National Institute of Child...University of MinnesotaCompleted
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4D Molecular TherapeuticsActive, not recruitingChoroideremiaUnited States
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedRett Syndrome | CDKL5 Disorder | MECP2 Duplication dIsorder | FOXG1 SyndromeUnited States
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Astellas Gene TherapiesActive, not recruitingX-Linked Myotubular MyopathyUnited States, Canada, France, Germany
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Rare Thyroid Therapeutics International ABEgetis Therapeutics; AnovoRxAvailableMonocarboxylate Transporter 8 Deficiency | Allan-Herndon-Dudley SyndromeUnited States