- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on X-Linked Hypophosphatemia in United States
Total 1363 results
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Nationwide Children's HospitalCompleted
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National Human Genome Research Institute (NHGRI)Completed
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Kevin FlaniganWithdrawnDuchenne Muscular DystrophyUnited States
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Alan Neuromedical Technologies, LLCCompleted
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Cooperative International Neuromuscular Research...United States Department of DefenseTerminated
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Canada
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Canada
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Spain, Denmark, France, Belgium, Italy, Netherlands, Switzerland
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Nido Biosciences, Inc.RecruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseKorea, Republic of, Denmark, Italy, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterCompletedBecker Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterTerminatedMuscular DystrophyUnited States
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Cedars-Sinai Medical CenterParent Project Muscular DystrophyCompleted
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Cedars-Sinai Medical CenterCompleted
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Cedars-Sinai Medical CenterMuscular Dystrophy AssociationCompleted
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National Center for Research Resources (NCRR)Children's National Research InstituteCompletedMuscular Dystrophy, DuchenneUnited States
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Not yet recruiting
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The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...RecruitingDuchenne Muscular DystrophyUnited States
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Massachusetts General HospitalBoston Children's HospitalRecruitingDuchenne Muscular DystrophyUnited States
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University of PittsburghRecruitingDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Jerry R. MendellDuchenne Alliance; Milo TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Cure Rare Disease, IncUniversity of Massachusetts, WorcesterActive, not recruiting
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Craig McDonald, MDCardero Therapeutics, Inc.Completed
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University of FloridaEngage Health Inc.CompletedDuchenne Muscular DystrophyUnited States
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University of FloridaCureDuchenneCompletedMuscular Dystrophy, DuchenneUnited States
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University of FloridaUnited States Department of DefenseCompletedDuchenne Muscular DystrophyUnited States
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Jerry R. MendellEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDuchenne Muscular DystrophyUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical CenterCompletedDuchenne Muscular DystrophyUnited States
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Institute for Neurodegenerative DisordersCompletedParkinson Disease | Alzheimer Disease | Mild Cognitive Impairment | Fragile X Syndrome | Huntington Disease | Autistic Spectrum DisordersUnited States
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TakedaTakeda Development Center Americas, Inc.RecruitingHunter Syndrome | Mucopolysaccharidosis (MPS)United States
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TakedaAvailableHunter SyndromeUnited States, Australia, Mexico, Spain, United Kingdom
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Bio Products LaboratoryCompletedPrimary Immunodeficiency | Wiskott-Aldrich Syndrome | Hypogammaglobulinemia | Common Variable Hypogammaglobulinemia | X-linked Hypogammaglobulinemia | Immunodeficiency With Hyper-IgMUnited States
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaBelgium, Canada, United States, Israel, United Kingdom, Spain, Denmark, France, Italy, Netherlands, Switzerland
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Sangamo TherapeuticsTerminated
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Rare Disease Research, LLCSarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyUnited States
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St. Jude Children's Research HospitalRecruitingHemophilia B | Gene TherapyUnited States
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CSL BehringRecruiting
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Cedars-Sinai Medical CenterCompleted
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University of South FloridaMerck Sharp & Dohme LLCTerminatedX-linked Agammaglobulinemia | Specific Antibody Deficiency | Common Variable Immune DeficiencyUnited States
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, France, Germany, Italy, Netherlands, United Kingdom
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsActive, not recruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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Minoryx Therapeutics, S.L.Active, not recruitingAdrenoleukodystrophySpain, United States, Hungary, France, Germany, Italy, Netherlands, United Kingdom
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis IIUnited States, Spain, United Kingdom, Czechia, France, Canada, Italy, Belgium, Netherlands, Germany, Argentina, Sweden, Turkey, Colombia, Brazil
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Baylor College of MedicineUniversity of California, San Diego; University of Alabama at Birmingham; Boston... and other collaboratorsCompletedPrader-Willi Syndrome | Rett Syndrome | Angelman Syndrome | Sleep ProblemsUnited States
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Children's National Research InstituteFoundation to Eradicate DuchenneActive, not recruitingDuchenne Muscular DystrophyUnited States
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University of North Carolina, Chapel HillNational Institute of Neurological Disorders and Stroke (NINDS)CompletedMuscular Dystrophy, DuchenneUnited States
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Cooperative International Neuromuscular Research...Completed
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Kevin FlaniganMuscular Dystrophy AssociationTerminated