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Clinical Trials on X-Linked Hypophosphatemia in United States
Total 1363 results
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Megan WaldropAudentes TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited States
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Roxanna Marie BendixenTerminatedDuchenne Muscular DystrophyUnited States
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Craig McDonald, MDCardero Therapeutics, Inc.CompletedBecker Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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University of FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)Completed
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University of Colorado, DenverCompleted
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National Human Genome Research Institute (NHGRI)CompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalCompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalAsklepios Biopharmaceutical, Inc.CompletedDuchenne Muscular DystrophyUnited States
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AB2 Bio Ltd.CompletedNLRC4-MAS | XIAP DeficiencyUnited States, Canada, Germany
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Minoryx Therapeutics, S.L.Active, not recruitingAdrenoleukodystrophySpain, United States, Hungary, France, Germany, Italy, Netherlands, United Kingdom
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Baylor College of MedicineUniversity of California, San Diego; University of Alabama at Birmingham; Boston... and other collaboratorsCompletedPrader-Willi Syndrome | Rett Syndrome | Angelman Syndrome | Sleep ProblemsUnited States
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Children's National Research InstituteFoundation to Eradicate DuchenneActive, not recruitingDuchenne Muscular DystrophyUnited States
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University of North Carolina, Chapel HillNational Institute of Neurological Disorders and Stroke (NINDS)CompletedMuscular Dystrophy, DuchenneUnited States
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Cooperative International Neuromuscular Research...Completed
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Kevin FlaniganMuscular Dystrophy AssociationTerminated
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AB2 Bio Ltd.Active, not recruitingNLRC4-MAS | XIAP DeficiencyUnited States, Canada, Germany
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Equilibra Bioscience LLCRecruitingHemophilia A | Hemophilia B | Healthy ParticipantsUnited States
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Allergy and Asthma Consultants, Wichita, KansasAidan Foundation; Neil H. Riordan PhDCompletedDuchenne's Muscular DystrophyUnited States
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National Institute of Neurological Disorders and...CompletedMuscular Dystrophy | Muscular DiseaseUnited States
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National Institute of Allergy and Infectious Diseases...Completed
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National Institute of Neurological Disorders and...CompletedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States
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NightstaRx Ltd, a Biogen CompanyCompletedX-Linked Retinitis PigmentosaUnited States, France, United Kingdom, Finland, Netherlands, Germany, Canada
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Kaiser PermanenteKeryx BiopharmaceuticalsCompletedHyperphosphatemiaUnited States
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Cedars-Sinai Medical CenterCompleted
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Washington University School of MedicineBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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Massachusetts General HospitalEuropean Leukodystrophy AssociationRecruitingRestless Legs Syndrome | AdrenoleukodystrophyUnited States, Netherlands
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
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University of OxfordUniversity College, London; University of Southampton; Moorfields Eye Hospital... and other collaboratorsCompleted
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States
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University of FloridaU.S. Army Medical Research and Development CommandRecruitingDuchenne Muscular Dystrophy (DMD)United States
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PTC TherapeuticsCompletedNonsene Mutation Duchenne Muscular DystrophyUnited States
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Avidity Biosciences, Inc.Enrolling by invitationDuchenne Muscular Dystrophy | DMD | Exon 44 | DuchenneUnited States
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Children's Hospital Medical Center, CincinnatiActive, not recruitingMusculoskeletal Abnormalities | Duchenne Muscular DystrophyUnited States
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National Human Genome Research Institute (NHGRI)TerminatedCommunication | Genetic DiseaseUnited States
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Dana-Farber Cancer InstituteBrigham and Women's HospitalCompletedHemophilia A | Hemophilia BUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoChildren's National Research InstituteWithdrawnDuchenne Muscular Dystrophy (DMD)United States
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The Duchenne RegistryParent Project Muscular DystrophyRecruiting
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University of California, DavisNational Institute of Mental Health (NIMH)CompletedFragile X PremutationUnited States
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Canada
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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ReveraGen BioPharma, Inc.Santhera PharmaceuticalsRecruitingBecker Muscular DystrophyUnited States, Italy
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumTerminatedHemophilia A | Hemophilia BUnited States
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ShireCompletedHunter SyndromeSpain, United States, Canada, United Kingdom, France, Australia, Mexico
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Nationwide Children's HospitalParent Project Muscular DystrophyRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States
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Skane University HospitalIndiana Hemophilia &Thrombosis Center, Inc.; Bioverativ Therapeutics Inc.; Swedish...Active, not recruitingFactor IX DeficiencyUnited States
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Completed
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University of Illinois at ChicagoShireCompletedHyperphosphatemia in Chronic Kidney DiseaseUnited States