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Clinical Trials on X-Linked Hypophosphatemic Rickets in Australia
Total 148 results
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaKorea, Republic of, Canada, United States, Australia, Japan, United Kingdom, Sweden
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-linked Hypophosphatemia (XLH)Sweden, Spain, United Kingdom, Italy, Austria, France
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Orthopedic Hospital Vienna SpeisingCompleted
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Murdoch Childrens Research InstituteUniversity of Sydney; Sydney Children's Hospitals Network; Women's and Children... and other collaboratorsActive, not recruitingAutosomal Recessive Disorder | X-Linked Genetic DiseasesAustralia
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Center for Eye Research AustraliaCompleted
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Anavex Life Sciences Corp.Completed
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Medical University of ViennaCompleted
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Healx LimitedWithdrawnFragile X SyndromeUnited States, Australia
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Kiora Pharmaceuticals, Inc.RecruitingRetinitis Pigmentosa | ChoroideremiaAustralia
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Zynerba Pharmaceuticals, Inc.RecruitingFragile X SyndromeUnited States, Australia, United Kingdom, Ireland
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Mitsubishi Tanabe Pharma America Inc.RecruitingErythropoietic Protoporphyria (EPP) | X-Linked Protoporphyria (XLP)United States, Spain, France, Japan, United Kingdom, Italy, Australia, Poland, Bulgaria, Czechia, Netherlands
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Newron Pharmaceuticals SPATerminatedRett SyndromeUnited States, India, United Kingdom, Australia, Italy
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHCompletedRett SyndromeCanada, Australia, United Kingdom
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Mobius Medical Pty Ltd.University of Melbourne; Australian National University; Centre for Eye Research... and other collaboratorsCompleted
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Center for Eye Research AustraliaAustralian National University; Commonwealth Scientific and Industrial Research... and other collaboratorsEnrolling by invitation
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Zynerba Pharmaceuticals, Inc.CompletedFragile X SyndromeUnited States, New Zealand, Australia
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NeuroVia, Inc.WithdrawnX-Linked AdrenoleukodystrophyAustralia, Argentina, United Kingdom, Colombia, Chile, France, Russian Federation, Ukraine
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Novartis PharmaceuticalsTerminatedFragile X SyndromeGermany, United States, Switzerland, Australia, Canada, Denmark, France, Italy, United Kingdom, Spain
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Zynerba Pharmaceuticals, Inc.Enrolling by invitationFragile X SyndromeUnited States, United Kingdom, New Zealand, Australia
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Switzerland, Germany, Australia, Canada, Denmark, France, Italy, Spain, United Kingdom
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Novartis PharmaceuticalsTerminatedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, Denmark, Italy, Netherlands, Spain, Sweden, United Kingdom, France
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, France, Canada, Denmark, Indonesia, Italy, Netherlands, Spain, Sweden, Turkey, United Kingdom
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Jazz PharmaceuticalsGW PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Canada, Italy, Spain, United Kingdom, Australia
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Medical University of GrazCompletedBipolar Affective DisorderAustria
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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PfizerActive, not recruitingMuscular Dystrophy, DuchenneUnited States, Australia
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ShireCompletedHunter SyndromeUnited States, Spain, Canada, United Kingdom, Mexico, Australia, France
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Spark TherapeuticsChildren's Hospital of Philadelphia; University of Pittsburgh; St. James's Hospital... and other collaboratorsTerminated
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CSL BehringCompletedHemophilia BGermany, Australia, Italy, Israel, Czech Republic, Spain, France, Canada, Austria, Russian Federation
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Hospital RudolfstiftungOesterreichische MuskelforschungCompletedCarrier of Duchenne Muscular DystrophyAustria
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Spark TherapeuticsCompletedHematologic Diseases | Hemophilia A | Blood Coagulation Disorders, Inherited | Coagulation Protein Disorders | Hemorrhagic Disorders | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Blood Coagulation Disorder | Factor VIII DeficiencyUnited States, Australia, Thailand, Canada
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Cooperative International Neuromuscular Research...Washington University School of Medicine; Children's National Research Institute and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Australia, Italy
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Percheron TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited Kingdom, Australia, Serbia, Turkey, Bulgaria
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ShireCompletedHunter SyndromeSpain, United States, Canada, United Kingdom, France, Australia, Mexico
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedHemophilia BUnited States, United Kingdom, South Africa, Netherlands, Ireland, Australia
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TakedaAvailableHunter SyndromeUnited States, Australia, Mexico, Spain, United Kingdom
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The University of QueenslandRecruitingPulmonary Fibrosis | Dyskeratosis Congenita | Telomere Shortening | Telomere DiseaseAustralia
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States, Canada, Argentina, Australia, Israel, Italy
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Weill Medical College of Cornell UniversityBayer; University Hospital, BonnCompletedHemophilia A | Hemophilia BUnited States, Israel, Australia, Italy, Sweden, Germany, Japan, Netherlands, Taiwan
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Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, France, Germany
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PfizerRecruitingHemophilia A | Hemophilia BAustralia, United States, Turkey
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ReveraGen BioPharma, Inc.University of Pittsburgh; Cooperative International Neuromuscular Research...CompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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Amicus TherapeuticsCompleted
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ReveraGen BioPharma, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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ReveraGen BioPharma, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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PfizerActive, not recruitingHemophilia BUnited States, Canada, Australia, Turkey
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4D Molecular TherapeuticsActive, not recruiting
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Amicus TherapeuticsCompletedFabry DiseaseAustralia, Brazil