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Clinical Trials on X-linked Protoporphyria
Total 2378 results
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Seaside Therapeutics, Inc.Completed
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Stanford UniversityCompleted
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NeuroVia, Inc.UnknownX-Linked AdrenoleukodystrophyUnited States
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Massachusetts General HospitalNational Institutes of Health (NIH)UnknownHealthy | Fragile X SyndromeUnited States
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Craig EricksonHealx LimitedRecruitingFragile X SyndromeUnited States
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Elizabeth Berry-KravisCompletedFragile X SyndromeUnited States
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Spain
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Rowan UniversityUniversity of Pennsylvania; FRAXA Research FoundationUnknown
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Hoffmann-La RocheCompleted
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Hoffmann-La RocheCompletedFragile X SyndromeFrance, Spain, United States, Peru, Canada, United Kingdom, Chile, Argentina, Mexico, Sweden
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Yolanda de Diego OteroCompletedFragile X SyndromeSpain
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Brigham and Women's HospitalCompleted
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FDA Office of Orphan Products DevelopmentSt. Luke's-Roosevelt Hospital CenterCompletedErythropoietic Protoporphyria
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Thomas S. ScanlanWithdrawnAdrenomyeloneuropathy | X-Linked AdrenoleukodystrophyUnited States
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... and other collaboratorsNot yet recruiting
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Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
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Children's Hospital of Fudan UniversityRecruiting
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Tetra Discovery PartnersEnrolling by invitationFragile X SyndromeUnited States
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Healx LimitedWithdrawnFragile X SyndromeUnited States, Australia
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Children's Hospital Medical Center, CincinnatiCompleted
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Université de SherbrookeFRAXA Research FoundationCompleted
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NovartisCompletedFragile X SyndromeFrance, Italy, Switzerland
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Neuren Pharmaceuticals LimitedCompleted
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Randi J. Hagerman, MDCompleted
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Indiana UniversityIndiana Clinical and Translational Sciences InstituteCompleted
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Indiana University School of MedicineCompletedFragile X SyndromeUnited States
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Hoffmann-La RocheCompleted
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Novartis PharmaceuticalsTerminatedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, Denmark, Italy, Netherlands, Spain, Sweden, United Kingdom, France
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Stanford UniversityNational Institute of Mental Health (NIMH); Autism SpeaksCompleted
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FRAXA Research FoundationFragile X Research Foundation of CanadaCompleted
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, France, Canada, Denmark, Indonesia, Italy, Netherlands, Spain, Sweden, Turkey, United Kingdom
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.SuspendedFragile X SyndromeUnited States
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NeuropharmCompleted
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Primary Immune Deficiency Disorders | Hyper-IgM Syndrome | X-linked AgammaglobulinaemiaUnited States, United Kingdom, Hungary
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University of AlbertaSt. Justine's HospitalRecruitingNeurobehavioral Manifestations | Genetic Diseases, X-Linked | Mental Retardation, X-Linked | Intellectual Disability | Fragile X Syndrome | Sex Chromosome Disorders | Fragile X Mental Retardation Syndrome | Trinucleotide Repeat Expansion | Fra(X) Syndrome | FXSCanada
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ACADIA Pharmaceuticals Inc.CompletedRett SyndromeUnited States
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ACADIA Pharmaceuticals Inc.Completed
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IRCCS Eugenio MedeaAssociazione Italiana Rett (AIRett) O.n.l.u.s.Completed
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Rett Syndrome Research TrustDuke UniversityCompletedRett SyndromeUnited States
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Anavex Life Sciences Corp.International Rett Syndrome Foundation Rettsyndrome.orgCompleted
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Montefiore Medical CenterRett Syndrome Research TrustCompleted
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Montefiore Medical CenterRett Syndrome Research TrustCompletedRett SyndromeUnited States
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Assistance Publique Hopitaux De MarseilleCompleted
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Edimer PharmaceuticalsCompleted
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Medical University of ViennaCompleted