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Clinical Trials on X-linked Adrenoleukodystrophy
Total 2355 results
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Edimer PharmaceuticalsCompletedX-Linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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Edimer PharmaceuticalsCompletedHypohidrotic Ectodermal Dysplasia | X-Linked Hypohidrotic Ectodermal DysplasiaUnited States
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Edimer PharmaceuticalsNational Foundation of Ectodermal DysplasiaCompletedHypohidrotic Ectodermal Dysplasia | X-Linked Hypohidrotic Ectodermal DysplasiaUnited States
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Assistance Publique - Hôpitaux de ParisRecruitingAdrenoleukodystrophy | Adrenomyeloneuropathy | Metachromatic Leukodystrophy | Adult-Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaFrance
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Ionis Pharmaceuticals, Inc.Not yet recruitingMethyl CpG Binding Protein 2 (MECP2) Duplication Syndrome
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Rare Thyroid Therapeutics International ABVitaccess LtdCompletedAllan-Herndon-Dudley Syndrome | Monocarboxylate Transporter 8 (MCT8) DeficiencyUnited Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...WithdrawnGranulomatous Disease, Chronic, X-linked, VariantUnited Kingdom
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National Institute of Allergy and Infectious Diseases...CompletedImmunoproliferative DisorderUnited States
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAutism Spectrum Disorder | Autistic Disorder | Fragile X Syndrome | Asperger SyndromeUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingNeurodegenerative Diseases | Ataxia | Cerebellar Ataxia | Leukodystrophy | Adrenomyeloneuropathy | LBSL | Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate Elevation | Leukoencephalopathy With Brain Stem and Spinal Cord Involvement and High Lactate Syndrome (Disorder)United States
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Astellas Gene TherapiesActive, not recruitingX-Linked Myotubular MyopathyUnited States, Canada, France, Germany
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State University of New York - Upstate Medical...TerminatedFamilial Encephalopathy With Neuroserpin Inclusion Bodies | X-linked Mental Retardation | Congenital Vertical Talus | Idiopathic Generalised Epilepsy | Familial DementiaUnited States
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Kyowa Kirin Co., Ltd.Active, not recruiting
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Baylor College of MedicineCompleted
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Primary Immune Deficiency Disorders | X-linked Agammaglobulinaemia | Hyperimmunoglobulin M SyndromeUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingAutism Spectrum Disorder | Fragile X Syndrome | Developmental Delay | Genetic Disorder | Asperger DisorderUnited States
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ProgenaBiomeRecruitingAutism Spectrum Disorder | Autistic Disorder | Autism | Autism, Akinetic | Autism; Atypical | Autism; Psychopathy | Autism Fragile Syndrome X | Autism With High Cognitive Abilities | Autism-Related Speech Delay | Autism, Susceptibility to, 6 | Autism Spectrum Disorder High-Functioning | Autistic Thinking | Autism... and other conditionsUnited States
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Rare Thyroid Therapeutics International ABPremier Research Group plc; Egetis TherapeuticsRecruitingMonocarboxylate Transporter 8 Deficiency | Allan-Herndon-Dudley SyndromeUnited States, United Kingdom, Netherlands
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International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University of... and other collaboratorsRecruitingNervous System Diseases | Neurologic Manifestations | Neurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Neurodevelopmental Disorders | Neurologic Disorder | Rett Syndrome | Genetic Disease | Rett Syndrome, AtypicalUnited States
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Universitair Ziekenhuis BrusselMarguerite - Marie Delacroix FoundationNot yet recruitingClassical Lissencephalies and Subcortical Band HeterotopiasBelgium
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Bambino Gesù Hospital and Research InstituteAutour Des Williams; AceaUnknownFragile X Syndrome | Williams SyndromeItaly
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis | Hurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Krabbe Disease | Adrenoleukodystrophy (ALD) | Hunter Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Metachromatic Leukodystrophy (MLD) | Maroteaux-Lamy SyndromeUnited States
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Rare Thyroid Therapeutics International ABEgetis Therapeutics; AnovoRxAvailableMonocarboxylate Transporter 8 Deficiency | Allan-Herndon-Dudley SyndromeUnited States
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University Hospital ErlangenPervormance GmbHCompletedShort Term Effects and Risks of Physical Exercise in Subjects With Hypohidrotic Ectodermal DysplasiaX-Linked Hypohidrotic Ectodermal Dysplasia | Exercise-induced Rise of Body TemperatureGermany
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Ionis Pharmaceuticals, Inc.RecruitingMethyl CpG Binding Protein 2 (MECP2) Duplication SyndromeUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingGranuloma | Granulomatous Disease, Chronic | Leukocyte Disease | Genetic Disease, X-Linked | Genetic Disease, InbornUnited States
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BiogenCompletedChoroideremiaUnited States, Germany, France
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Duke UniversityFoundation Fighting BlindnessWithdrawnChoroideremiaUnited States
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University of AlbertaCanadian Institutes of Health Research (CIHR); Imperial College London; University... and other collaboratorsCompleted
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University of AlbertaTerminated
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Jakub AntczakCompletedAdrenomyeloneuropathy | Hereditary Spastic ParaplegiaPoland
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Rush University Medical CenterEmory UniversityEnrolling by invitationTuberous Sclerosis | Fragile X Syndrome | Rett Syndrome | Hamartoma Syndrome, Multiple | Angelman Syndrome | Creatine Deficiency, X-linked | Telomeric 22Q13 Monosomy Syndrome | Chromosome 15Q, Partial DeletionUnited States
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University of California, DavisEunice Kennedy Shriver National Institute of Child Health and Human Development...Enrolling by invitationIntellectual Disability | Down Syndrome | Attention Deficit Hyperactivity Disorder | Fragile X SyndromeUnited States
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4D Molecular TherapeuticsActive, not recruitingChoroideremiaUnited States
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4D Molecular TherapeuticsTerminated
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University of OxfordUniversity College, London; Moorfields Eye Hospital NHS Foundation TrustCompleted
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STZ eyetrialUniversity Hospital TuebingenCompleted
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome, Preserved Speech Variant | Mecp2 Duplication Syndrome | Rett-related DisordersUnited States
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University Hospital, BrestUnknownDysautonomia | Masculinity | MECP2-Related Severe Neonatal EncephalopathyFrance
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Fairview University Medical CenterTerminatedImmunologic Deficiency Syndromes | Common Variable Immunodeficiency | Severe Combined Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Graft Versus Host Disease | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | Virus-Associated... and other conditionsUnited States
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Rocket Pharmaceuticals Inc.Recruiting
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University of California, San DiegoRocket Pharmaceuticals Inc.Recruiting
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TakedaRecruitingSpinal and Bulbar Muscular AtrophyJapan
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Novartis PharmaceuticalsCompletedSpinal and Bulbar Muscular AtrophyUnited States, Germany, Italy, Denmark
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InnoVec Biotherapeutics Inc.Peking Union Medical College HospitalRecruitingEye Diseases | Retinal Degeneration | Retinal Disease | RetinoschisisChina
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BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Chronic Granulomatous DiseaseUnited States
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Gianni SoraruMario Negri Institute for Pharmacological ResearchRecruitingSpinal and Bulbar Muscular AtrophyItaly