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Clinical Trials on X-Linked Hypophosphatemia in United Kingdom
Total 1360 results
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Washington University School of MedicineUniversity of California, Davis; Nationwide Children's Hospital; University of... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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PfizerRecruitingDuchenne Muscular DystrophyUnited States
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Akashi TherapeuticsTerminatedDuchenne Muscular DystrophyUnited States
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ArdelyxCompletedHyperphosphatemiaUnited States
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PedNet Haemophilia Research FoundationLund University HospitalRecruitingFactor IX Deficiency | Factor VIII DeficiencyNorway, Austria, Belgium, Canada, Czechia, Denmark, Finland, France, Germany, Greece, Ireland, Israel, Italy, Netherlands, Portugal, Spain, Sweden, Switzerland, United Kingdom
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Epirium Bio Inc.CompletedBecker Muscular DystrophyUnited States
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University of FloridaU.S. Army Medical Research and Development CommandRecruitingDuchenne Muscular Dystrophy (DMD)United States
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PTC TherapeuticsCompletedNonsene Mutation Duchenne Muscular DystrophyUnited States
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Avidity Biosciences, Inc.Enrolling by invitationDuchenne Muscular Dystrophy | DMD | Exon 44 | DuchenneUnited States
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Children's Hospital Medical Center, CincinnatiActive, not recruitingMusculoskeletal Abnormalities | Duchenne Muscular DystrophyUnited States
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National Human Genome Research Institute (NHGRI)TerminatedCommunication | Genetic DiseaseUnited States
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Dana-Farber Cancer InstituteBrigham and Women's HospitalCompletedHemophilia A | Hemophilia BUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoChildren's National Research InstituteWithdrawnDuchenne Muscular Dystrophy (DMD)United States
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Amicus TherapeuticsCompletedFabry DiseaseUnited Kingdom, United States
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Amicus TherapeuticsTerminatedFabry DiseaseUnited Kingdom, United States, Australia, Brazil, France
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Capricor Inc.Active, not recruiting
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Nationwide Children's HospitalParent Project Muscular DystrophyRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States
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Skane University HospitalIndiana Hemophilia &Thrombosis Center, Inc.; Bioverativ Therapeutics Inc.; Swedish...Active, not recruitingFactor IX DeficiencyUnited States
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Completed
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Cooperative International Neuromuscular Research...Washington University School of Medicine; Children's National Research Institute and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Australia, Italy
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Santhera PharmaceuticalsTerminatedDuchenne Muscular Dystrophy (DMD)United States, Spain, Netherlands, Sweden, Germany, France, Belgium, United Kingdom, Italy, Ireland, Switzerland, Austria, Bulgaria, Hungary, Israel
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University of California, DavisNational Institute of Mental Health (NIMH)CompletedFragile X PremutationUnited States
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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NS Pharma, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Canada
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Amy K. Dickey, M.D.Wake Forest University Health Sciences; University of TexasRecruitingErythropoietic Protoporphyria | X-linked ProtoporphyriaUnited States
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Spark TherapeuticsChildren's Hospital of Philadelphia; University of Pittsburgh; St. James's Hospital... and other collaboratorsTerminated
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Cooperative International Neuromuscular Research...Completed
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PfizerActive, not recruitingHemophilia A | Hemophilia BUnited States, Canada, Spain, Australia, Korea, Republic of, Taiwan, Brazil, Italy, Japan, Turkey, Germany, United Kingdom, Saudi Arabia, France, Sweden, Belgium, Greece, Israel
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Korea, Republic of, Italy, United Kingdom, Canada, Poland, Spain, France, Germany, Belgium, Australia, Czechia, Serbia, Greece, Argentina, Bulgaria, Denmark, Hungary, India, Ireland, Israel, Mexico, Russian Federation, ...
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Sangamo TherapeuticsActive, not recruitingHemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis IIUnited States
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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Edgewise Therapeutics, Inc.Worldwide Clinical TrialsCompletedBecker Muscular Dystrophy | Healthy VolunteerUnited States
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Spark TherapeuticsChildren's Hospital of Philadelphia; Royal Prince Alfred Hospital, Sydney,... and other collaboratorsCompleted
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Skulpt, Inc.National Institute of Neurological Disorders and Stroke (NINDS)CompletedDuchenne Muscular DystrophyUnited States
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University of Illinois at ChicagoShireCompletedHyperphosphatemia in Chronic Kidney DiseaseUnited States
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AvigenThe University of Texas Health Science Center, Houston; Children's Hospital... and other collaboratorsTerminatedHemophilia BUnited States
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Bioverativ Therapeutics Inc.Swedish Orphan Biovitrum; Syntonix Pharmaceuticals, Inc.Completed
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Massachusetts General HospitalNorthwestern University; University of Florida; University of Minnesota; Henry... and other collaboratorsRecruitingALS | Kennedy Disease | MND (Motor Neurone DIsease) | PLS | PMA - Progressive Muscular Atrophy | PBP - Progressive Bulbar PalsyUnited States, Italy
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ProtalixChiesi Farmaceutici S.p.A.CompletedFabry DiseaseUnited States, Spain, United Kingdom, Paraguay
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CSL BehringEnrolling by invitation
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States
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Processa PharmaceuticalsTerminated
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Sarepta Therapeutics, Inc.TerminatedMuscular Dystrophy, DuchenneUnited States, Canada
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...UnknownDuchenne Muscular DystrophyUnited States, Canada
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitation
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey