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Clinical Trials on X-Linked Hypophosphatemia in United Kingdom
Total 1364 results
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Bio Products LaboratoryCompletedFactor X DeficiencyUnited States, Turkey, Germany, Spain, United Kingdom
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Amicus TherapeuticsRecruiting
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National Institute of Neurological Disorders and...CompletedFabry DiseaseUnited States
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National Institute of Neurological Disorders and...Completed
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O & O Alpan LLCCompletedFabry DiseaseUnited States
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Ohio State UniversityGenzyme, a Sanofi CompanyCompleted
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National Institute of Neurological Disorders and...Completed
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National Institute of Neurological Disorders and...Completed
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University of LeicesterSanofi Pasteur, a Sanofi Company; University Hospitals, Leicester; World Health... and other collaboratorsCompletedInfluenza | Influenza -Like IllnessUnited Kingdom
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Alexion PharmaceuticalsCompletedHypophosphatasia | Bone DiseaseUnited States
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AlexionRecruiting
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IlypsaUnknownKidney Diseases | Renal InsufficiencyUnited States
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Boston Children's HospitalMassachusetts General Hospital; Mayo Clinic; Karolinska University Hospital; Baylor... and other collaboratorsActive, not recruitingAplastic Anemia | Dyskeratosis Congenita | Hoyeraal Hreidarsson Syndrome | Revesz SyndromeUnited States, Norway, Sweden
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia BUnited States
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, Canada
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National Institutes of Health Clinical Center (CC)CompletedNeedle Biopsy | CAT Scan | X-RayUnited States
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Masonic Cancer Center, University of MinnesotaCompletedWolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Sanfilippo Syndrome | GM1 Gangliosidosis | Globoid Cell Leukodystrophy | Tay Sachs Disease | Sandhoffs Disease | I-Cell DiseaseUnited States
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University of UtahGenzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States
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SanofiRecruitingFabry DiseaseItaly, United States, Austria, China, Czechia, Denmark, France, Germany, Greece, Japan, Korea, Republic of, Netherlands, Norway, Spain, Taiwan, Turkey, United Kingdom, Canada, Poland
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsUnited States
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Medy-ToxCompletedLateral Canthal LinesUnited States, Russian Federation, United Kingdom
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National Human Genome Research Institute (NHGRI)TerminatedCitrullinemia | Argininosuccinic Aciduria | Hyperargininemia | Ornithine Carbamoyltransferase Deficiency | Carbamoyl-Phosphate Synthase I Deficiency | N-Acetylglutamate Synthase DeficiencyUnited States
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Medy-ToxCompletedLateral Canthal Lines | Glabellar LinesUnited States, Russian Federation, Germany, Canada, Belgium, United Kingdom
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University of FloridaLive Like Bella Pediatric Cancer ResearchCompletedCommon Variable Immunodeficiency | Severe Combined Immunodeficiency | Sickle Cell Disease | Hurler Syndrome | Chronic Granulomatous Disease | Thalassemia | Wiskott-Aldrich Syndrome | Adrenoleukodystrophy | X-linked Lymphoproliferative Disease | Diamond Blackfan Anemia | Bone Marrow Failure Syndrome | Hemophagocytic... and other conditionsUnited States
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4D Molecular TherapeuticsActive, not recruitingFabry DiseaseUnited States
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Cedars-Sinai Medical CenterNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsUnknown
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsUnited States, Serbia, Malaysia, Thailand, Greece, Japan, Romania
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis | Hurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Krabbe Disease | Adrenoleukodystrophy (ALD) | Hunter Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Metachromatic Leukodystrophy (MLD) | Maroteaux-Lamy SyndromeUnited States
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SanofiRecruitingFabry's DiseaseUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsUnited States
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy Type 3United States
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University of Maryland, BaltimoreCompletedOsteoporosis PseudogliomaUnited States
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National Institute of Neurological Disorders and...CompletedHealthy | Fabry Disease | Cerebrovascular AccidentUnited States
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Fresenius Medical Care North AmericaCompleted
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SanofiTerminatedArteriosclerosis | Obesity | Carotid Artery Plaque | Metabolic Syndrome XUnited States, France, Canada, Netherlands, Spain, United Kingdom
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Amicus TherapeuticsCompletedFabry DiseaseJapan, Taiwan, Turkey, United States, Brazil
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Denver Nephrologists, P.C.CM&D Pharma LimitedCompletedChronic Kidney Disease | HyperphosphatemiaUnited States
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Cooperative International Neuromuscular Research...Carolinas Medical Center lead study siteCompletedBecker Muscular Dystrophy | Limb-Girdle Muscular Dystrophy, Type 2A (Calpain-3 Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2B (Miyoshi Myopathy, Dysferlin Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2I (FKRP-deficiency)United States
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University of Maryland, BaltimoreChildren's Hospital of PhiladelphiaWithdrawnOsteoporosis Pseudoglioma SyndromeUnited States
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National Institute of Neurological Disorders and...CompletedFabry DiseaseUnited States
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Genzyme, a Sanofi CompanyCompleted
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Virginia Commonwealth UniversityCompletedCardiovascular Diseases | Obesity | Insulin Resistance | Metabolic Syndrome XUnited States
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University of IowaTerminatedObesity | Metabolic Syndrome XUnited States
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Genzyme, a Sanofi CompanyWithdrawn
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Amicus TherapeuticsApproved for marketingPhysician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry DiseaseFabry DiseaseUnited States, Australia
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Amicus TherapeuticsCompletedFabry DiseaseUnited States
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Baylor College of MedicineCompletedMetabolic Syndrome X | Heart Failure, CongestiveUnited States
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ShireCompleted
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Lysosomal and Rare Disorders Research and Treatment...Recruiting