- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on X-Linked Hypophosphatemia in United Kingdom
Total 1359 results
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Novo Nordisk A/SEnrolling by invitationHaemophilia BNetherlands, United Kingdom
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Hoffmann-La RocheCompleted
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Seaside Therapeutics, Inc.SuspendedFragile X SyndromeUnited States
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Elizabeth Berry-KravisNational Institute of Neurological Disorders and Stroke (NINDS); Novartis PharmaceuticalsCompleted
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Nova Mentis Life Science CorpFourthWall TestingRecruitingAutism Spectrum Disorder | Fra(X) SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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ShireCompletedHunter SyndromeUnited Kingdom, United States, Brazil
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Stanford UniversityCompletedIntellectual Disability | Fragile X SyndromeUnited States
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Denali Therapeutics Inc.Active, not recruitingMucopolysaccharidosis IIUnited States, Netherlands, Canada, United Kingdom
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Neurogene Inc.RecruitingRett SyndromeUnited States
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National Human Genome Research Institute (NHGRI)CompletedRett SyndromeUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Zynerba Pharmaceuticals, Inc.CompletedFragile X SyndromeUnited States, New Zealand, Australia
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... and other collaboratorsRecruiting
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Edison Pharmaceuticals IncWithdrawn
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)CompletedRett SyndromeUnited States
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Boston Children's HospitalInternational Rett Syndrome FoundationCompleted
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The Cleveland ClinicTerminated
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationCompleted
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Neuren Pharmaceuticals LimitedBaylor College of Medicine; International Rett Syndrome FoundationCompleted
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Seaside Therapeutics, Inc.Completed
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Healx LimitedWithdrawnFragile X SyndromeUnited States, Australia
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRecruiting
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Hoffmann-La RocheCompleted
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Cangene CorporationWithdrawnHemophilia BUnited Kingdom, United States
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Sarepta Therapeutics, Inc.British Medical Research CouncilCompletedDuchenne Muscular DystrophyUnited Kingdom
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Anavex Life Sciences Corp.International Rett Syndrome Foundation Rettsyndrome.orgCompleted
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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University College, LondonRecruiting
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Ovid Therapeutics Inc.Completed
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Rett Syndrome Research TrustVanderbilt University Medical CenterCompleted
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BioMarin PharmaceuticalRecruitingDuchenne Muscular DystrophySpain, United Kingdom
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Wave Life Sciences Ltd.Active, not recruitingDuchenne Muscular DystrophyJordan, United Kingdom
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Summit TherapeuticsCompletedDuchenne Muscular DystrophyUnited Kingdom
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of Alabama... and other collaboratorsRecruiting
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Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
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Tetra Discovery PartnersEnrolling by invitationFragile X SyndromeUnited States
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research TrustUnknownRett SyndromeUnited States
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ACADIA Pharmaceuticals Inc.Completed
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Neuren Pharmaceuticals LimitedCompleted
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Bio Products LaboratoryCompletedHaemophilia BUnited Kingdom
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ShireCompletedMucopolysaccharidosis IIUnited States, United Kingdom, Brazil, Germany
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ShireCompletedHunter SyndromeUnited States, United Kingdom
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedSevere Combined Immunodeficiency | Adenosine Deaminase Deficiency | Immune System Disorder | Autosomal Recessive Disorder | Purine-Nucleoside Phosphorylase Deficiency | Severe Combined Immunodeficiency With Absence of T and B Cells | X-Linked Severe Combined ImmunodeficiencyUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Stanford UniversityTerminatedFragile X Syndrome (FXS) | Idiopathic Intellectual Developmental Disorder (IDD)United States
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Indiana UniversityCompletedFragile X Syndrome | Autism Spectrum DisordersUnited States