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Clinical Trials on X-Linked Hypophosphatemia in United Kingdom
Total 1359 results
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University College, LondonTerminatedHemophilia BIreland, United Kingdom, Italy, United States
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Rare... and other collaboratorsCompletedErythropoietic Protoporphyria | EPP | XLP | X-Linked Protoporphyria | XLPP | X-Linked Dominant Erythropoietic Protoporphyria | XLEPP | XLDPUnited States
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Haemophilia A | Haemophilia BUnited Kingdom
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Haemophilia A | Haemophilia BUnited Kingdom
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GenethonActive, not recruitingWiskott-Aldrich SyndromeUnited Kingdom, France
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National Institute of Allergy and Infectious Diseases...RecruitingGranuloma | Granulomatous Disease, Chronic | Leukocyte Disease | Genetic Disease, X-Linked | Genetic Disease, InbornUnited States
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Astellas Gene TherapiesActive, not recruitingX-Linked Myotubular MyopathyUnited States, Canada, France, Germany
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Medexus Pharma, Inc.TerminatedHemophilia BUnited States, United Kingdom, India
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Spain, Denmark, France, Belgium, Italy, Netherlands, Switzerland
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ShireCompletedHunter SyndromeSpain, United States, Canada, United Kingdom, France, Australia, Mexico
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Duke UniversityFoundation Fighting BlindnessWithdrawnChoroideremiaUnited States
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BayerCompletedHemophilia A | Hemophilia BUkraine, United Kingdom, Bulgaria, Germany, Japan
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BBulgaria, United States, United Kingdom, Russian Federation, Switzerland
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Wave Life Sciences Ltd.CompletedDuchenne Muscular DystrophyBelgium, United Kingdom, France, United States, Italy, Canada, Netherlands
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Rush University Medical CenterEmory UniversityEnrolling by invitationTuberous Sclerosis | Fragile X Syndrome | Rett Syndrome | Hamartoma Syndrome, Multiple | Angelman Syndrome | Creatine Deficiency, X-linked | Telomeric 22Q13 Monosomy Syndrome | Chromosome 15Q, Partial DeletionUnited States
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ShireCompletedHunter SyndromeUnited States, United Kingdom, Canada
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Royal Free Hospital NHS Foundation TrustUnknown
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NightstaRx Ltd, a Biogen CompanyCompletedX-Linked Retinitis PigmentosaUnited States, France, United Kingdom, Finland, Netherlands, Germany, Canada
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Rare Thyroid Therapeutics International ABEgetis Therapeutics; AnovoRxAvailableMonocarboxylate Transporter 8 Deficiency | Allan-Herndon-Dudley SyndromeUnited States
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TakedaAvailableHunter SyndromeUnited States, Australia, Mexico, Spain, United Kingdom
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaBelgium, Canada, United States, Israel, United Kingdom, Spain, Denmark, France, Italy, Netherlands, Switzerland
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Fairview University Medical CenterTerminatedImmunologic Deficiency Syndromes | Common Variable Immunodeficiency | Severe Combined Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Graft Versus Host Disease | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | Virus-Associated... and other conditionsUnited States
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Vifor Fresenius Medical Care Renal PharmaCompletedHyperphosphatemiaSpain, Netherlands, Germany, Italy, France, Greece, United Kingdom
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Taiwan, United Kingdom, Australia, Canada, Germany, Spain
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Ionis Pharmaceuticals, Inc.RecruitingMethyl CpG Binding Protein 2 (MECP2) Duplication SyndromeUnited States
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University of California, San DiegoRocket Pharmaceuticals Inc.Recruiting
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4D Molecular TherapeuticsActive, not recruitingChoroideremiaUnited States
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University of California, DavisEunice Kennedy Shriver National Institute of Child Health and Human Development...Enrolling by invitationIntellectual Disability | Down Syndrome | Attention Deficit Hyperactivity Disorder | Fragile X SyndromeUnited States
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Primary Immune Deficiency Disorders | X-linked Agammaglobulinaemia | Hyperimmunoglobulin M SyndromeUnited States
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BiogenCompletedChoroideremiaUnited States, Germany, France
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Sheffield Teaching Hospitals NHS Foundation TrustNational Institute for Health Research, United Kingdom; Alexion Pharmaceuticals...Completed
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SanofiCompletedHemophilia A | Hemophilia BBulgaria, Switzerland, United Kingdom, United States, Russian Federation
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Great Ormond Street Hospital for Children NHS Foundation...Catholic University of the Sacred Heart; Università degli Studi di Ferrara; Universidad... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyDenmark, France, Italy, Netherlands, Spain, United Kingdom
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4D Molecular TherapeuticsTerminated
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis IIUnited States, Spain, United Kingdom, Czechia, France, Canada, Italy, Belgium, Netherlands, Germany, Argentina, Sweden, Turkey, Colombia, Brazil
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Ultragenyx Pharmaceutical IncTerminatedHemophilia BUnited States, United Kingdom, Bulgaria
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome, Preserved Speech Variant | Mecp2 Duplication Syndrome | Rett-related DisordersUnited States
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Rocket Pharmaceuticals Inc.Recruiting
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Chronic Granulomatous DiseaseUnited States
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International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University of... and other collaboratorsRecruitingNervous System Diseases | Neurologic Manifestations | Neurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Neurodevelopmental Disorders | Neurologic Disorder | Rett Syndrome | Genetic Disease | Rett Syndrome, AtypicalUnited States
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Eunice Kennedy Shriver National Institute of Child...University of MinnesotaCompleted
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Brunel UniversityRoyal Free Hospital NHS Foundation TrustRecruiting
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Manchester University NHS Foundation TrustNorthern Care Alliance NHS Foundation TrustActive, not recruiting
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of SheffieldActive, not recruiting
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ReveraGen BioPharma, Inc.University of Pittsburgh; Cooperative International Neuromuscular Research...CompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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Novartis PharmaceuticalsCompletedSpinal and Bulbar Muscular AtrophyUnited States, Germany, Italy, Denmark
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University Hospital, Basel, SwitzerlandCompletedDuchenne Muscular DystrophyFrance, Spain, Germany, Netherlands, Switzerland, United Kingdom
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Baxalta now part of ShireCompletedHemophilia BRussian Federation, Ukraine, India, Poland, Romania, United Kingdom