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Clinical Trials on X-linked Retinoschisis in Canada
Total 241 results
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... and other collaboratorsRecruitingX Linked Myotubular MyopathyUnited Kingdom, Canada, United States
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The Hospital for Sick ChildrenCompletedX-linked Lymphoproliferative Syndrome Type 2 (XLP-2)Canada
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Astellas Gene TherapiesCompletedX-linked Myotubular MyopathyUnited States, France, United Kingdom, Canada, Germany
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University of California, DavisUniversity of Alberta; St. Justine's HospitalRecruitingNeurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Fragile X Syndrome | Sex Chromosome Disorders | Fragile X Mental Retardation Syndrome | Trinucleotide Repeat Expansion | Fra(X) Syndrome | FXS | Mental Retardation, X LinkedUnited States, Canada
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Université de SherbrookeFRAXA Research FoundationCompletedFragile X SyndromeCanada
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Université de SherbrookeFRAXA Research FoundationCompleted
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FRAXA Research FoundationFragile X Research Foundation of CanadaCompleted
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Anagnostou, Evdokia, M.D.Unity Health Toronto; Holland Bloorview Kids Rehabilitation Hospital; Ontario...Unknown
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University of AlbertaSt. Justine's HospitalRecruitingNeurobehavioral Manifestations | Genetic Diseases, X-Linked | Mental Retardation, X-Linked | Intellectual Disability | Fragile X Syndrome | Sex Chromosome Disorders | Fragile X Mental Retardation Syndrome | Trinucleotide Repeat Expansion | Fra(X) Syndrome | FXSCanada
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, Canada
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Nova Mentis Life Science CorpKGK Science Inc.RecruitingCognitive Dysfunction | Fragile X Syndrome | BehaviorCanada
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University of AlbertaCanadian Institutes of Health Research (CIHR); Imperial College London; University... and other collaboratorsCompleted
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University of AlbertaTerminated
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NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHCompletedRett SyndromeCanada, Australia, United Kingdom
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Novartis PharmaceuticalsTerminatedFragile X SyndromeGermany, United States, Switzerland, Australia, Canada, Denmark, France, Italy, United Kingdom, Spain
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Switzerland, Germany, Australia, Canada, Denmark, France, Italy, Spain, United Kingdom
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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Ultragenyx Pharmaceutical IncTerminatedCreatine Deficiency, X-linkedUnited States, Canada
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Hoffmann-La RocheCompletedFragile X SyndromeFrance, Spain, United States, Peru, Canada, United Kingdom, Chile, Argentina, Mexico, Sweden
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Astellas Gene TherapiesActive, not recruitingX-Linked Myotubular MyopathyUnited States, Canada, France, Germany
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4D Molecular TherapeuticsTerminated
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University of British ColumbiaVancouver General HospitalWithdrawn
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REGENXBIO Inc.Withdrawn
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Jazz PharmaceuticalsGW PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Canada, Italy, Spain, United Kingdom, Australia
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, France, Canada, Denmark, Indonesia, Italy, Netherlands, Spain, Sweden, Turkey, United Kingdom
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Canada
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Denali Therapeutics Inc.Enrolling by invitationMucopolysaccharidosis IIUnited States, Canada, Belgium, Czechia, Netherlands
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Children's Hospital of Eastern OntarioCompletedDuchenne Muscular DystrophyCanada
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McMaster UniversityCanadian Hemophilia SocietyCompletedHemophilia A | Hemophilia BCanada
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Denali Therapeutics Inc.Active, not recruitingMucopolysaccharidosis IIUnited States, Netherlands, Canada, United Kingdom
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CHU de Quebec-Universite LavalRecruitingDuchenne Muscular DystrophyCanada
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McMaster UniversityEnrolling by invitationWeb Accessible Population Pharmacokinetics Service - Hemophilia: Sources of Variability (WAPPS-Hemo)Hemophilia A | Hemophilia BCanada
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Homology Medicines, IncWithdrawnMucopolysaccharidosis IIUnited States, Canada
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BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedDuchenne Muscular DystrophyCanada
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ShireCompletedHunter SyndromeUnited States, Spain, Canada, United Kingdom, Mexico, Australia, France
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ItalfarmacoCompletedDuchenne and Becker Muscular Dystrophy | Polycytemia VeraCanada
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TakedaRecruitingHunter SyndromeCanada, France
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Santhera PharmaceuticalsSanthera PharmaceuticalsActive, not recruitingDuchenne Muscular DystrophyCanada
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Acceleron Pharma Inc. (a wholly owned subsidiary...Terminated
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NightstaRx Ltd, a Biogen CompanyCompletedChoroideremiaFinland, United States, Canada, Denmark, Netherlands, Germany, United Kingdom, Brazil, France
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VI | Mucopolysaccharidosis Type IV | Mucopolysaccharidosis Type VIIUnited States, Canada
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The Hospital for Sick ChildrenCompletedHemophilia A | Hemophilia BCanada, Brazil
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University of British ColumbiaBiogenCompletedHemophilia A, Congenital | Hemophilia B, CongenitalCanada
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PepGen IncRecruitingDuchenne Muscular DystrophyCanada
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The Hospital for Sick ChildrenCanadian Hemophilia SocietyCompletedHemophilia A | Hemophilia B | Factor IX Deficiency | Factor VIII DeficiencyCanada
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AB2 Bio Ltd.CompletedNLRC4-MAS | XIAP DeficiencyUnited States, Canada, Germany
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Spain, Denmark, France, Belgium, Italy, Netherlands, Switzerland
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AB2 Bio Ltd.Active, not recruitingNLRC4-MAS | XIAP DeficiencyUnited States, Canada, Germany