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Clinical Trials on X-linked Adrenal Hypoplasia Congenita
Total 2203 results
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Green Cross CorporationCompletedMucopolysaccharidosis IIKorea, Republic of
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Janssen-Ortho Inc., CanadaCompletedAutistic Disorder | Developmental Disabilities | Rett Syndrome | Asperger Syndrome | DCild Development Disorders, Pervasive
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Eunice Kennedy Shriver National Institute of Child...University of MinnesotaCompleted
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Northwell HealthCompletedPure Red Cell Aplasia | Diamond Blackfan Anemia | Blackfan Diamond Syndrome | DBA | Congenital Hypoplastic AnemiaUnited States
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Kyowa Kirin, Inc.CompletedX-Linked HypophosphatemiaUnited States
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-linked Hypophosphatemia (XLH)Sweden, Spain, United Kingdom, Italy, Austria, France
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Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingNeurodegenerative Diseases | Ataxia | Cerebellar Ataxia | Leukodystrophy | Adrenomyeloneuropathy | LBSL | Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate Elevation | Leukoencephalopathy With Brain Stem and Spinal Cord Involvement and High Lactate Syndrome (Disorder)United States
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Institute for Neurodegenerative DisordersCompletedParkinson Disease | Alzheimer Disease | Mild Cognitive Impairment | Fragile X Syndrome | Huntington Disease | Autistic Spectrum DisordersUnited States
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Janssen Pharmaceutical K.K.RecruitingX-Linked Retinitis PigmentosaJapan
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Frontera TherapeuticsPeking Union Medical College Hospital; Eye & ENT Hospital of Fudan University; Henan Provincial People's HospitalRecruitingX-Linked Retinitis PigmentosaChina
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Janssen Pharmaceutical K.K.CompletedX-Linked Retinitis PigmentosaJapan
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Michael A BelfortBaylor College of Medicine; Universitaire Ziekenhuizen KU LeuvenCompletedCongenital Abnormalities | Hernia | Pathological Conditions, Anatomical | Hernia, Diaphragmatic | Congenital Diaphragmatic Hernia | Fetal Anomaly | Pulmonary Hypoplasia | Hernia, DIaphragmatic, Congenital | Fetal SurgeryUnited States
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Nido Biosciences, Inc.RecruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseKorea, Republic of, Denmark, Italy, United Kingdom
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AO GENERIUMRecruitingMetabolic Diseases | Mucopolysaccharidosis Type IIRussian Federation
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Assistance Publique - Hôpitaux de ParisInstitut National de la Santé Et de la Recherche Médicale, France; Association...RecruitingAmyotrophic Lateral Sclerosis | Kennedy DiseaseFrance
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JCR Pharmaceuticals Co., Ltd.RecruitingMucopolysaccharidosis IIUnited States, Germany, Spain, France, Brazil, Argentina, Turkey, United Kingdom, Poland, Italy
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Denali Therapeutics Inc.Enrolling by invitationMucopolysaccharidosis IIUnited States, Canada, Belgium, Czechia, Netherlands
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Denali Therapeutics Inc.Active, not recruitingMucopolysaccharidosis IIUnited States, Netherlands, Canada, United Kingdom
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JCR Pharmaceuticals Co., Ltd.Enrolling by invitationMucopolysaccharidosis IIUnited States
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Rocket Pharmaceuticals Inc.Active, not recruitingDanon DiseaseUnited States
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JCR Pharmaceuticals Co., Ltd.Completed
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REGENXBIO Inc.CompletedMucopolysaccharidosis IIBrazil, United States, United Kingdom
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REGENXBIO Inc.Enrolling by invitation
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National Human Genome Research Institute (NHGRI)CompletedAutism | Asperger's Syndrome | Rett's DisorderUnited States
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ArmaGen, IncCompletedMucopolysaccharidosis IIUnited States, Germany, Philippines
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Soma JyonouchiBaylor College of MedicineCompletedX-linked Thrombocytopenia | Wiskott-Aldrich Syndrome (WAS)United States
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Ramathibodi HospitalAstraZenecaCompletedSpinobulbar Muscular Atrophy | Kennedy's DiseaseThailand
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National Institute of Neurological Disorders and...CompletedSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
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University of Mississippi Medical CenterCompletedAutistic Disorder | Rett Syndrome | Asperger Syndrome | Pervasive Developmental Disorder | Childhood Disintegrative DisorderUnited States
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Baylor College of MedicineCompletedCongenital Heart Disease | Cardiac Disease | Hypoplastic Left Heart | Cyanotic Congenital Heart DiseaseUnited States
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Emory UniversityChildren's Healthcare of AtlantaTerminatedSickle Cell Disease | Fanconi Anemia | Thalassemia | Severe Congenital Neutropenia | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Leukocyte Adhesion Deficiency | Dyskeratosis-congenita | Chediak-Higashi Syndrome | Chronic-granulomatous Disease | Schwachman-Diamond...United States
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University Hospital, GasthuisbergThe University of Texas Health Science Center, Houston; Baylor College of Medicine and other collaboratorsCompletedCongenital Diaphragmatic Hernia | Pulmonary Hypoplasia | Fetal SurgeryUnited Kingdom, Canada, United States, Belgium, Germany, Italy, France, Australia, Poland, Spain
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Children's Hospital Medical Center, CincinnatiRecruitingHypoplastic Left Heart Syndrome (HLHS)United States, United Kingdom, Canada
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Completed
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Spain, Denmark, France, Belgium, Italy, Netherlands, Switzerland
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BiogenCompletedX-Linked Retinitis PigmentosaUnited States, United Kingdom
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4D Molecular TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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NightstaRx Ltd, a Biogen CompanyCompletedChoroideremiaFinland, United States, Canada, Denmark, Netherlands, Germany, United Kingdom, Brazil, France
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Applied Genetic Technologies CorpCompletedX-Linked Retinitis PigmentosaUnited States
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Rocket Pharmaceuticals Inc.RecruitingDanon DiseaseUnited States
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University of ManchesterManchester University NHS Foundation Trust; Great Ormond Street Hospital for... and other collaboratorsRecruiting
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GC Biopharma CorpRecruitingMucopolysaccharidosis II | Hunter SyndromeKorea, Republic of
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis IIUnited States, Spain, United Kingdom, Czechia, France, Canada, Italy, Belgium, Netherlands, Germany, Argentina, Sweden, Turkey, Colombia, Brazil
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Homology Medicines, IncWithdrawnMucopolysaccharidosis IIUnited States, Canada
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IIBrazil
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ShireCompletedMucopolysaccharidosis IIUnited States, United Kingdom, Brazil, Germany
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AO GENERIUMCompletedA Multi-cohort Study of the Tolerance, Safety, and Pharmacokinetics of GNR-055 in Healthy VolunteersMetabolic Diseases | Mucopolysaccharidosis Type IIRussian Federation
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Hacettepe UniversityCompletedChewing Problem | Swallowing DisorderTurkey
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GlaxoSmithKlineCompletedMucopolysaccharidosis IIJapan
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Green Cross CorporationUnknownMucopolysaccharidosis II