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Clinical Trials on X-linked Adrenal Hypoplasia Congenita
Total 2205 results
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Yolanda de Diego OteroCompletedFragile X SyndromeSpain
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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Edimer PharmaceuticalsCompleted
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... and other collaboratorsNot yet recruiting
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Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
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Children's Hospital of Fudan UniversityRecruiting
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Tetra Discovery PartnersEnrolling by invitationFragile X SyndromeUnited States
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Healx LimitedWithdrawnFragile X SyndromeUnited States, Australia
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Children's Hospital Medical Center, CincinnatiCompleted
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Université de SherbrookeFRAXA Research FoundationCompleted
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NovartisCompletedFragile X SyndromeFrance, Italy, Switzerland
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Neuren Pharmaceuticals LimitedCompleted
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Randi J. Hagerman, MDCompleted
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Indiana UniversityIndiana Clinical and Translational Sciences InstituteCompleted
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Indiana University School of MedicineCompletedFragile X SyndromeUnited States
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Hoffmann-La RocheCompleted
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Novartis PharmaceuticalsTerminatedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, Denmark, Italy, Netherlands, Spain, Sweden, United Kingdom, France
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Stanford UniversityNational Institute of Mental Health (NIMH); Autism SpeaksCompleted
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FRAXA Research FoundationFragile X Research Foundation of CanadaCompleted
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, France, Canada, Denmark, Indonesia, Italy, Netherlands, Spain, Sweden, Turkey, United Kingdom
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.SuspendedFragile X SyndromeUnited States
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NeuropharmCompleted
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Great Ormond Street Hospital for Children NHS Foundation...UnknownX-linked Severe Combined ImmunodeficiencyUnited Kingdom
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Lehigh UniversityCompletedCongenital Adrenal HyperplasiaUnited States
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Beijing Tiantan HospitalRecruiting
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University of MinnesotaNo longer availableX-linked AdrenoleukodystrophyUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...The Stop ALD FoundationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophyNetherlands
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Astellas Gene TherapiesActive, not recruitingX-Linked Myotubular MyopathyUnited States, Canada, France, Germany
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Diurnal LimitedNational Institutes of Health Clinical Center (CC)CompletedAdrenogenital Syndrome | Congenital Adrenal Hyperplasia | 21-Hydroxylase DeficiencyUnited States
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Hospices Civils de LyonCompletedAdrenal Hyperplasia, CongenitalFrance
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National Institute of Allergy and Infectious Diseases...RecruitingX-linked Severe Combined Immunodeficiency (XSCID)United States
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); Assisi Foundation; California...SuspendedSevere Combined Immunodeficiency Disease, X-linkedUnited States
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Assistance Publique - Hôpitaux de ParisCompletedX-linked Severe Combined ImmunodeficiencyFrance
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Assistance Publique - Hôpitaux de ParisBraintaleNot yet recruitingX-linked Adrenoleukodystrophy
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Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W. Moser... and other collaboratorsCompletedX-linked AdrenoleukodystrophyUnited States
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Shenzhen Geno-Immune Medical InstituteUnknown
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NeuroVia, Inc.WithdrawnX-Linked AdrenoleukodystrophyAustralia, Argentina, United Kingdom, Colombia, Chile, France, Russian Federation, Ukraine
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Shenzhen Geno-Immune Medical InstituteUnknownSCID, X LinkedChina
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... and other collaboratorsNot yet recruitingFragile X Syndrome
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Stanford UniversityThe John Merck FundCompletedFragile X Syndrome | Disruptive BehaviorUnited States
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Stanford UniversityCompletedDevelopmental Disabilities | Fragile X SyndromeUnited States
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Onofre, Aurora Pujol, M.D.Instituto de Salud Carlos III; Fundacion Hesperia; ELA España AssociationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophySpain
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Hugo W. Moser Research Institute at Kennedy Krieger...European Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyUnited States
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Murdoch Childrens Research InstituteUniversity of Sydney; Sydney Children's Hospitals Network; Women's and Children... and other collaboratorsActive, not recruitingAutosomal Recessive Disorder | X-Linked Genetic DiseasesAustralia