- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on X-linked Adrenoleukodystrophy
Total 2358 results
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Ning Wang, MD., PhD.Recruiting
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CHU de Quebec-Universite LavalRecruitingDuchenne Muscular DystrophyCanada
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Percheron TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited Kingdom, Australia, Serbia, Turkey, Bulgaria
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Medexus Pharma, Inc.CompletedHemophilia BTurkey, Brazil, Georgia, Moldova, Republic of, South Africa, Ukraine
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitationDuchenne Muscular DystrophyUnited States
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Belgium, Israel, Spain, Canada, Australia, Switzerland, United Kingdom, France, China, Netherlands, Italy, Austria, Czechia
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Daiichi Sankyo Co., Ltd.Orphan Disease Treatment Institute Co., Ltd.Completed
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Novo Nordisk A/SEnrolling by invitationHaemophilia BNetherlands, United Kingdom
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Swedish Orphan BiovitrumCerner EnvizaActive, not recruitingHemophilia BCzechia, Greece, Ireland, Italy, Norway, Saudi Arabia, Spain, Sweden, United Kingdom
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Belgium, Spain, United Kingdom, Netherlands, Germany, Canada, Italy
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Lokman Hekim ÜniversitesiCompletedDuchenne Muscular DystrophyTurkey
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Capricor Inc.Active, not recruiting
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States
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Jerry R. MendellDuchenne Alliance; Milo TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Children's National Research InstituteFoundation to Eradicate DuchenneActive, not recruitingDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.TerminatedAn Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyUnited States, Belgium, Canada, Spain, United Kingdom, Czechia, Germany, Israel, Bulgaria, France, Italy, Poland, Sweden
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ApcinteX LtdCentessa Pharmaceuticals plcActive, not recruitingHemophilia A | Hemophilia BGeorgia, Moldova, Republic of, United Kingdom
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Daiichi Sankyo Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyJapan
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Freeline TherapeuticsTerminatedHemophilia BUnited Kingdom
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey
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Santhera PharmaceuticalsNo longer availableDuchenne Muscular DystrophyUnited States
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PfizerCompletedDuchenne Muscular DystrophyChina
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ENCellCompletedDuchenne Muscular DystrophyKorea, Republic of
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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Hacettepe UniversityActive, not recruitingDuchenne Muscular DystrophyTurkey
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NS Pharma, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Canada
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National Center of Neurology and Psychiatry, JapanNippon Shinyaku Co., Ltd.Completed
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Hacettepe UniversityCompletedMuscular Dystrophy, DuchenneTurkey
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Cure Rare Disease, IncUniversity of Massachusetts, WorcesterActive, not recruiting
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Swedish Orphan BiovitrumKantar Health; Cerner Enviza (former Kantar Health)CompletedHemophilia A | Hemophilia BFrance
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Hadassah Medical OrganizationCompletedDuchenne Muscular Dystrophy
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States, Canada
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States, Canada, Australia, United Kingdom, Germany, Ireland, Israel, Sweden
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Karadeniz Technical UniversityCompleted
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ItalfarmacoCompletedBecker Muscular DystrophyNetherlands, Italy
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
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Craig McDonald, MDCardero Therapeutics, Inc.Completed
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University of North Carolina, Chapel HillNational Institute of Neurological Disorders and Stroke (NINDS)CompletedMuscular Dystrophy, DuchenneUnited States
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Wave Life Sciences Ltd.TerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Czechia, Canada, France, Italy, Sweden
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Baxalta now part of ShireCompletedHemophilia BPoland, United Kingdom, Spain, Bulgaria, Romania, Japan, Russian Federation, Brazil, Chile, Sweden, Colombia, Ukraine, Argentina, Czechia
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Baxalta now part of ShireCompletedHemophilia BColombia, Bulgaria, Chile, Poland, Romania, Argentina, Czechia, Russian Federation, Ukraine, United Kingdom
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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McMaster UniversityCanadian Hemophilia SocietyCompletedHemophilia A | Hemophilia BCanada
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University of Sao PauloCompletedDuchenne Muscular Dystrophy
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SanofiCompletedHemophilia A | Hemophilia BBulgaria, Switzerland, United Kingdom, United States, Russian Federation
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumTerminatedHemophilia A | Hemophilia BUnited States
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Bioverativ Therapeutics Inc.Swedish Orphan Biovitrum; Syntonix Pharmaceuticals, Inc.Completed
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University of Sao PauloCompletedDuchenne Muscular DystrophyBrazil
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States