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Clinical Trials on X-Linked Hypophosphatemia
Total 2588 results
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
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Craig McDonald, MDCardero Therapeutics, Inc.Completed
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University of North Carolina, Chapel HillNational Institute of Neurological Disorders and Stroke (NINDS)CompletedMuscular Dystrophy, DuchenneUnited States
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Wave Life Sciences Ltd.TerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Czechia, Canada, France, Italy, Sweden
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Baxalta now part of ShireCompletedHemophilia BPoland, United Kingdom, Spain, Bulgaria, Romania, Japan, Russian Federation, Brazil, Chile, Sweden, Colombia, Ukraine, Argentina, Czechia
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Baxalta now part of ShireCompletedHemophilia BColombia, Bulgaria, Chile, Poland, Romania, Argentina, Czechia, Russian Federation, Ukraine, United Kingdom
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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McMaster UniversityCanadian Hemophilia SocietyCompletedHemophilia A | Hemophilia BCanada
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University of Sao PauloCompletedDuchenne Muscular Dystrophy
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SanofiCompletedHemophilia A | Hemophilia BBulgaria, Switzerland, United Kingdom, United States, Russian Federation
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumTerminatedHemophilia A | Hemophilia BUnited States
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Bioverativ Therapeutics Inc.Swedish Orphan Biovitrum; Syntonix Pharmaceuticals, Inc.Completed
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University of Sao PauloCompletedDuchenne Muscular DystrophyBrazil
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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University of FloridaEngage Health Inc.CompletedDuchenne Muscular DystrophyUnited States
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Taiho Pharmaceutical Co., Ltd.Completed
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Hacettepe UniversityUnknownDuchenne Muscular DystrophyTurkey
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Summit TherapeuticsTerminatedDuchenne Muscular DystrophyUnited States, United Kingdom
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Ohio State UniversityUniversity of Colorado, Denver; University of California, Los Angeles; Vanderbilt... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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EspeRare FoundationCompletedMuscular Dystrophy, DuchenneItaly, France, Spain, United Kingdom
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University of FloridaCureDuchenneCompletedMuscular Dystrophy, DuchenneUnited States
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PfizerTerminatedHemophilia A | Hemophilia BUnited States
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PfizerCompletedHemophilia A | Hemophilia B
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Akashi TherapeuticsTerminatedDuchenne Muscular DystrophyUnited States
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GlaxoSmithKlineCompletedMuscular DystrophiesFrance, Denmark, Germany, Belgium, Spain, Turkey, Korea, Republic of, Brazil, Netherlands, Italy, Chile, Japan, Canada, Hungary, Russian Federation, Czechia, Poland, Norway, Argentina, Taiwan
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Cedars-Sinai Medical CenterCompleted
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University of South FloridaMerck Sharp & Dohme LLCTerminatedX-linked Agammaglobulinemia | Specific Antibody Deficiency | Common Variable Immune DeficiencyUnited States
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University of MinnesotaFairview Health ServicesWithdrawnDuchenne Muscular Dystrophy
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PTC TherapeuticsParexel; Dohmen Life Science ServicesApproved for marketingDuchenne Muscular DystrophyUnited States
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University of FloridaUnited States Department of DefenseCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyBelgium, Netherlands, Italy, Sweden
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Jerry R. MendellEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDuchenne Muscular DystrophyUnited States
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CSL BehringCompletedHemophilia BUnited States, Japan, Israel, Austria, Bulgaria, France, Germany, Italy, Russian Federation, Spain
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Boston Children's HospitalBeth Israel Deaconess Medical CenterCompletedDuchenne Muscular DystrophyUnited States
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University of GaziantepIstınye University, Cukurova University, Yıldırım Beyazıt University, Gaziantep...UnknownDuchenne Muscular DystrophyTurkey
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GlaxoSmithKlineWithdrawnMuscular Dystrophies
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedDuchenne Muscular DystrophyCanada
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Wyeth is now a wholly owned subsidiary of PfizerCompletedHemophilia B | Hemophilia
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Shenzhen Beike Bio-Technology Co., Ltd.The Second Affiliated Hospital of Kunming Medical UniversityUnknownDuchenne Muscular DystrophyChina
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Nationwide Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...CompletedDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...Completed
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Cooperative International Neuromuscular Research...Completed
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PfizerCompletedHemophilia BUnited States, Spain, Croatia, Serbia, Russian Federation, Canada, Hungary, Italy, Romania
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Wyeth is now a wholly owned subsidiary of PfizerCompleted
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Massachusetts General HospitalEuropean Leukodystrophy AssociationRecruitingRestless Legs Syndrome | AdrenoleukodystrophyUnited States, Netherlands
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Sangamo TherapeuticsActive, not recruitingHemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis IIUnited States
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Minoryx Therapeutics, S.L.Active, not recruitingCerebral AdrenoleukodystrophySpain, Germany, France, Argentina
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Wiskott-Aldrich Syndrome | X-linked Agammaglobulinemia | Primary Immune Deficiency Disorders | Hyper-IgM SyndromeUnited States, Chile, Israel