- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on X-linked Hypophosphatemia (XLH)
Total 1545 results
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Sangamo TherapeuticsActive, not recruitingHemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis IIUnited States
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Minoryx Therapeutics, S.L.Active, not recruitingCerebral AdrenoleukodystrophySpain, Germany, France, Argentina
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Wiskott-Aldrich Syndrome | X-linked Agammaglobulinemia | Primary Immune Deficiency Disorders | Hyper-IgM SyndromeUnited States, Chile, Israel
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Lancashire Teaching Hospitals NHS Foundation TrustDuchenne UKRecruiting
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BioMarin PharmaceuticalRecruitingDuchenne Muscular DystrophySpain, Turkey, United Kingdom, Italy
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Hospices Civils de LyonRecruiting
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Solid Biosciences Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Hoffmann-La RocheSarepta Therapeutics, Inc.RecruitingDuchenne Muscular DystrophySpain, Germany, Italy
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BiocadRecruitingStudy of the Safety, Pharmacodynamics and Efficacy of ANB-002 in Patients With Hemophilia B (SAFRAN)Hemophilia BRussian Federation
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West China HospitalRecruiting
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Hacettepe UniversityNot yet recruitingDuchenne Muscular DystrophyTurkey
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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PepGen IncRecruitingDuchenne Muscular DystrophyCanada
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.RecruitingDuchenne Muscular DystrophyUnited States
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St. Jude Children's Research HospitalNot yet recruiting
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Bahçeşehir UniversityRecruitingHemophilia A | Hemophilia BTurkey
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Beni-Suef UniversityNot yet recruitingDuchenne Muscular Dystrophy
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingStudy of Genotype and Phenotype Characterization in Duchenne Muscular Dystrophy With Small MutationsMuscular Dystrophy, DuchenneItaly
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Institute of Hematology & Blood Diseases HospitalNot yet recruiting
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Muş Alparlan UniversityHacettepe UniversityRecruitingDuchenne Muscular DystrophyTurkey
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.Medpace, Inc.; SYSNAV; ImagingNMDRecruitingBecker Muscular DystrophyUnited States, Spain, Netherlands, United Kingdom
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ReveraGen BioPharma, Inc.Santhera PharmaceuticalsRecruitingBecker Muscular DystrophyUnited States, Italy
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Institute of Hematology & Blood Diseases HospitalRecruiting
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PfizerRecruitingHemophilia A | Hemophilia BHong Kong, Spain, Serbia, Turkey, United States, China, Mexico, South Africa, India, Japan, Taiwan, Croatia, Korea, Republic of, Oman, Italy, Canada, France
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Taiho Pharmaceutical Co., Ltd.RecruitingDuchenne Muscular DystrophyJapan
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GenethonRecruiting
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McMaster UniversityRecruiting
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Solid Biosciences Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States
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CSL BehringEnrolling by invitation
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CSL BehringActive, not recruiting
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Edgewise Therapeutics, Inc.Medpace, Inc.CompletedBecker Muscular DystrophyUnited States
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Spain, Canada, Australia, China, Italy, Belgium, France, Netherlands, Austria, United Kingdom
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PfizerActive, not recruitingHemophilia A | Hemophilia BUnited States, Canada, Spain, Australia, Korea, Republic of, Taiwan, Brazil, Italy, Japan, Turkey, Germany, United Kingdom, Saudi Arabia, France, Sweden, Belgium, Greece, Israel
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Halic UniversityIstanbul University; Biruni UniversityCompletedDuchenne Muscular DystrophyTurkey
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PfizerActive, not recruitingHemophilia BUnited States, Canada, Australia, Turkey
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PfizerActive, not recruitingMuscular Dystrophy, DuchenneUnited States, Australia
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Korea, Republic of, Italy, United Kingdom, Canada, Poland, Spain, France, Germany, Belgium, Australia, Czechia, Serbia, Greece, Argentina, Bulgaria, Denmark, Hungary, India, Ireland, Israel, Mexico, Russian Federation, ...
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Sarepta Therapeutics, Inc.Hansa Biopharma ABActive, not recruitingDuchenne Muscular DystrophySpain
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Wave Life Sciences Ltd.Active, not recruitingDuchenne Muscular DystrophyJordan, United Kingdom
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Hacettepe UniversityCompleted
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Çağtay MadenCompleted
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Hacettepe UniversityCompleted
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Sarepta Therapeutics, Inc.Hoffmann-La RocheActive, not recruitingDuchenne Muscular DystrophyUnited States, Japan, Taiwan, Belgium, Spain, Germany, Hong Kong, Italy, United Kingdom
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ItalfarmacoCromsourceEnrolling by invitationDuchenne Muscular DystrophySpain, United States, Canada, Belgium, France, Israel, Italy, Netherlands, Serbia, Germany, United Kingdom
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Kevin FlaniganSarepta Therapeutics, Inc.Completed
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Kevin FlaniganActive, not recruitingDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
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Solid Biosciences Inc.CompletedDuchenne Muscular DystrophyUnited States