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Clinical Trials on beta-Thalassemia in Poland
Total 20 results
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Imara, Inc.Terminatedβ ThalassemiaIsrael, France, Malaysia, Turkey, Denmark, Georgia, Greece, Italy, Lebanon, Morocco, Netherlands, Tunisia, United Kingdom
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Prothya BiosolutionsTerminated
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Brown UniversityNational Institute of General Medical Sciences (NIGMS)Recruiting
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Amsterdam UMC, location VUmcNational Research Council, Institute of Biomedical EngineeringCompletedGlucocorticoid-induced Glucometabolic Abnormalities | Glucocorticoid-induced Beta-cell DysfunctionNetherlands
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Washington University School of MedicineHealthCore-NERI; Pediatric Blood and Marrow Transplant ConsortiumCompletedSevere ThalassemiaUnited States
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Chantal KatsRecruitingInfection, Bacterial | Beta-lactam Antibiotics | Critical Care | Risk Model | Therapeutic Drug MonitoringNetherlands
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The Netherlands Cancer InstituteEli Lilly and Company; Universitaire Ziekenhuizen KU Leuven; European Organisation... and other collaboratorsWithdrawnGalunisertib and Capecitabine in Advanced Resistant TGF-beta Activated Colorectal Cancer (EORTC1615)Colorectal Cancer MetastaticNetherlands
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Amsterdam UMC, location VUmcCompletedDiabetes Mellitus | Steroid Diabetes | Glucocorticoid-induced Diabetes | Beta-cell FunctionNetherlands
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LMU KlinikumSeventh Framework Programme; NBIA AllianceRecruitingNeurodegeneration With Brain Iron Accumulation (NBIA) | Pantothenate Kinase-associated Neurodegeneration (PKAN) | Aceruloplasminemia | Beta-Propeller Protein-Associated Neurodegeneration (BPAN) | Mitochondrial Membrane Protein Associated Neurodegeneration (MPAN) | Fatty Acid Hydroxylase-associated... and other conditionsCanada, Czechia, Germany, Italy, Netherlands, Poland, Serbia, Spain
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Bristol-Myers SquibbRecruitingAnemiaThailand, China, Canada, Turkey, Greece, Taiwan, Italy, Hong Kong
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Life Molecular Imaging SACompletedAlzheimer Disease | Amyloid Beta-ProteinUnited States, Switzerland, Australia, Germany, Japan
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, United Kingdom, Spain, Italy, Brazil, Canada, Poland
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Chelsea TherapeuticsChiltern International Inc.CompletedA Clinical Study for Patients With Neurogenic Orthostatic Hypotension (NOH) Using Droxidopa (NOH301)Primary Autonomic Failure | Dopamine Beta Hydroxylase Deficiency | Symptomatic Neurogenic Orthostatic Hypotension (NOH) | Non-diabetic NeuropathyUnited States, Canada
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Chelsea TherapeuticsChiltern International Inc.CompletedPrimary Autonomic Failure | Dopamine Beta Hydroxylase Deficiency | Symptomatic Neurogenic Orthostatic Hypotension (NOH) | Non-diabetic NeuropathyUnited States, Australia, Canada, New Zealand
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Chelsea TherapeuticsCompletedMultiple System Atrophy | Neurogenic Orthostatic Hypotension | Dopamine Beta Hydroxylase Deficiency | Non-Diabetic Autonomic NeuropathyUnited States, Australia, Canada, New Zealand
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Novartis PharmaceuticalsRecruitingAcute Myeloid Leukemia | Primary Myelofibrosis | Polycythemia Vera | Thalassemia | Graft Versus Host DiseaseKorea, Republic of, Italy, Belgium, Japan, Germany, Australia, Bulgaria, Chile, China, Denmark, Greece, Hungary, Israel, Lebanon, Poland, Portugal, Russian Federation, Slovakia, South Africa, Spain, Sweden, Thailand, India, Mexico, Turkey, Fran...
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Genzyme, a Sanofi CompanyRecruitingGaucher Disease | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency DiseaseHungary, Croatia, United States, Australia, Belgium, Brazil, Bulgaria, Canada, Denmark, Germany, Greece, Hong Kong, India, Indonesia, Italy, Jordan, Korea, Republic of, Kuwait, Lebanon, Malaysia, Pakistan, Philippines, Poland, Saudi Arabia and more
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Fog Pharmaceuticals, Inc.RecruitingCancer | Gastric Cancer | Colorectal Cancer | Solid Tumor | Metastatic Cancer | Adenomatous Polyposis Coli | Non-small Cell Lung Cancer | Non-small Cell Lung Cancer Metastatic | Non-small Cell Carcinoma | Locally Advanced Solid Tumor | Non-small Cell Lung Cancer Stage IIIB | Gastroesophageal-junction Cancer | Non-Small... and other conditionsUnited States
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Novartis PharmaceuticalsCompletedMyelofibrosis | Sickle Cell Disease | Thalassemia | Diamond Blackfan AnemiaUnited States, Netherlands, Taiwan, Thailand, Italy, Germany, Spain, Canada, Belgium, Greece, Turkey, United Kingdom
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American Thrombosis and Hemostasis NetworkSanofi; Pfizer; Genentech, Inc.; CSL Behring; Hemophilia of Georgia, Inc.; Hemab TherapeuticsRecruitingHemophilia | Thrombosis | Thrombophilia | Sickle Cell Disease | Thalassemia | Bleeding Disorder | Von Willebrand Diseases | Factor IX Deficiency | Connective Tissue Disorder | Factor VIII Deficiency | Hematologic Disorder | Rare Bleeding Disorder | Platelet DisorderUnited States